Literature DB >> 31473366

One year of mepolizumab. Efficacy and safety in real-life in Italy.

Diego Bagnasco1, Marco Caminati2, Francesco Menzella3, Manlio Milanese4, Giovanni Rolla5, Carlo Lombardi6, Caterina Bucca7, Enrico Heffler8, Giovanni Paoletti8, Elisa Testino1, Andrea Manfredi1, Cristiano Caruso9, Giuseppe Guida10, Gianenrico Senna2, Marco Bonavia11, Anna Maria Riccio1, Giorgio Walter Canonica8, Giovanni Passalacqua12.   

Abstract

BACKGROUND: Severe asthma is a disease with a heavy socio-economic burden and a relevant impact on the life of patients. Mepolizumab (MEP) was recently introduced in practice. The previous data were favourable as efficacy and safety are concerned. Nowadays, we can report the clinical data after more than one year of use of MEP in the real-life setting.
OBJECTIVE: To evaluate the efficacy and safety of MEP in a real life framework, mainly concerning asthma exacerbations, steroid dependence, effects on respiratory function and adverse events.
METHODS: This retrospective analysis was performed on 138 patients, treated with MEP for at least 12 months, and referred to eleven severe asthma clinics in Italy. All patients met the criteria for severe uncontrolled asthma according to ATS/ERS guidelines and prescribing MEP conditions according to the Italian Drug Agency (AIFA).
RESULTS: We could observe 138 patients (78 female, age 58 ± 10 years). The average age of onset of asthma was 34 ± 16 years. The blood eosinophil count decreased from 822 ± 491/μL at baseline to 117 ± 96/μL (p < .0001) after 12 months of therapy. Exacerbations decreased from 3.8/year to 0.7/year (-81%; p < .0001). Steroid-dependent patients before MEP (80%) with a daily dose of 10.1 ± 9.4 mg prednisone decrease at 28% after 12 months with a mean of 2.0 ± 4.2 mg/day (p < .0001). The occurrence of adverse events was overall low. CONCLUSIONS & CLINICAL RELEVANCE: In this real-life setting, MEP confirmed its efficacy and safety profile, already shown in clinical trials. This was apparent concerning exacerbation rate, systemic steroids intake and safety.
Copyright © 2019 Elsevier Ltd. All rights reserved.

Entities:  

Keywords:  Asthma; Biologics; Eosinophils; Exacerbations; IL-5; Mepolizumab; OCS; Quality of life; Real life; Safety; Severe asthma

Year:  2019        PMID: 31473366     DOI: 10.1016/j.pupt.2019.101836

Source DB:  PubMed          Journal:  Pulm Pharmacol Ther        ISSN: 1094-5539            Impact factor:   3.410


  14 in total

1.  Real-life effectiveness of mepolizumab in patients with severe refractory eosinophilic asthma and multiple comorbidities.

Authors:  Claudia Crimi; Raffaele Campisi; Giulia Cacopardo; Rossella Intravaia; Santi Nolasco; Morena Porto; Corrado Pelaia; Nunzio Crimi
Journal:  World Allergy Organ J       Date:  2020-09-18       Impact factor: 4.084

2.  Upper and lower airway inflammation in severe asthmatics: a guide for a precision biologic treatment.

Authors:  Manuela Latorre; Elena Bacci; Veronica Seccia; Maria Laura Bartoli; Cristina Cardini; Silvana Cianchetti; Ludovica Cristofani; Antonella Di Franco; Mario Miccoli; Ilaria Puxeddu; Alessandro Celi; Pierluigi Paggiaro
Journal:  Ther Adv Respir Dis       Date:  2020 Jan-Dec       Impact factor: 4.031

Review 3.  Difficult and Severe Asthma in Children.

Authors:  Federica Porcaro; Nicola Ullmann; Annalisa Allegorico; Antonio Di Marco; Renato Cutrera
Journal:  Children (Basel)       Date:  2020-12-10

4.  Economic impact of mepolizumab in uncontrolled severe eosinophilic asthma, in real life.

Authors:  Diego Bagnasco; Massimiliano Povero; Lorenzo Pradelli; Luisa Brussino; Giovanni Rolla; Marco Caminati; Francesco Menzella; Enrico Heffler; Giorgio Walter Canonica; Pierluigi Paggiaro; Gianenrico Senna; Manlio Milanese; Carlo Lombardi; Caterina Bucca; Andrea Manfredi; Rikki Frank Canevari; Giovanni Passalacqua
Journal:  World Allergy Organ J       Date:  2021-01-27       Impact factor: 4.084

Review 5.  Specific Therapy for T2 Asthma.

Authors:  Diego Bagnasco; Elisa Testino; Stefania Nicola; Laura Melissari; Maria Russo; Rikki Frank Canevari; Luisa Brussino; Giovanni Passalacqua
Journal:  J Pers Med       Date:  2022-04-07

6.  Oral Corticosteroids Dependence and Biologic Drugs in Severe Asthma: Myths or Facts? A Systematic Review of Real-World Evidence.

Authors:  Luigino Calzetta; Marina Aiello; Annalisa Frizzelli; Giuseppina Bertorelli; Paola Rogliani; Alfredo Chetta
Journal:  Int J Mol Sci       Date:  2021-07-01       Impact factor: 5.923

7.  Real-life evidence of low-dose mepolizumab efficacy in EGPA: a case series.

Authors:  Aikaterini Detoraki; Eugenio Tremante; Remo Poto; Emanuela Morelli; Giuseppe Quaremba; Francescopaolo Granata; Antonio Romano; Ilaria Mormile; Francesca Wanda Rossi; Amato de Paulis; Giuseppe Spadaro
Journal:  Respir Res       Date:  2021-06-23

8.  Mepolizumab in a population with severe eosinophilic asthma and corticosteroid dependence: results from a French early access programme.

Authors:  Camille Taillé; Pascal Chanez; Gilles Devouassoux; Alain Didier; Christophe Pison; Gilles Garcia; Jeremy Charriot; Stéphane Bouée; Alina Gruber; Celine Pribil; Arnaud Bourdin; Marc Humbert
Journal:  Eur Respir J       Date:  2020-06-25       Impact factor: 16.671

9.  Real-world mepolizumab in the prospective severe asthma REALITI-A study: initial analysis.

Authors:  Tim Harrison; Giorgio Walter Canonica; Geoffrey Chupp; Jason Lee; Florence Schleich; Tobias Welte; Antonio Valero; Kim Gemzoe; Aoife Maxwell; Sandra Joksaite; Shibing Yang; Peter Howarth; Melissa K Van Dyke
Journal:  Eur Respir J       Date:  2020-10-15       Impact factor: 16.671

10.  REal worlD Effectiveness and Safety of Mepolizumab in a Multicentric Spanish Cohort of Asthma Patients Stratified by Eosinophils: The REDES Study.

Authors:  Christian Domingo Ribas; Teresa Carrillo Díaz; Marina Blanco Aparicio; Eva Martínez Moragón; David Banas Conejero; M Guadalupe Sánchez Herrero
Journal:  Drugs       Date:  2021-09-29       Impact factor: 9.546

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