Literature DB >> 31443790

Sustained Rescue of Rod Function and Probable Non-Cell-Autonomous Rescue of Cones after Gene Therapy.

Karen Sophia Park, Jose Ronaldo Lima de Carvalho, Stephen H Tsang.   

Abstract

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Mesh：

Year:  2019        PMID： 31443790      PMCID： PMC9121307          DOI： 10.1016/j.ophtha.2019.03.007

Source DB:  PubMed          Journal:  Ophthalmology        ISSN： 0161-6420            Impact factor:   14.277


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  5 in total

1.  Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial.

Authors:  Stephen Russell; Jean Bennett; Jennifer A Wellman; Daniel C Chung; Zi-Fan Yu; Amy Tillman; Janet Wittes; Julie Pappas; Okan Elci; Sarah McCague; Dominique Cross; Kathleen A Marshall; Jean Walshire; Taylor L Kehoe; Hannah Reichert; Maria Davis; Leslie Raffini; Lindsey A George; F Parker Hudson; Laura Dingfield; Xiaosong Zhu; Julia A Haller; Elliott H Sohn; Vinit B Mahajan; Wanda Pfeifer; Michelle Weckmann; Chris Johnson; Dina Gewaily; Arlene Drack; Edwin Stone; Katie Wachtel; Francesca Simonelli; Bart P Leroy; J Fraser Wright; Katherine A High; Albert M Maguire
Journal:  Lancet       Date:  2017-07-14       Impact factor: 79.321

2.  Efficacy, Safety, and Durability of Voretigene Neparvovec-rzyl in RPE65 Mutation-Associated Inherited Retinal Dystrophy: Results of Phase 1 and 3 Trials.

Authors:  Albert M Maguire; Stephen Russell; Jennifer A Wellman; Daniel C Chung; Zi-Fan Yu; Amy Tillman; Janet Wittes; Julie Pappas; Okan Elci; Kathleen A Marshall; Sarah McCague; Hannah Reichert; Maria Davis; Francesca Simonelli; Bart P Leroy; J Fraser Wright; Katherine A High; Jean Bennett
Journal:  Ophthalmology       Date:  2019-06-22       Impact factor: 12.079

3.  Reprogramming metabolism by targeting sirtuin 6 attenuates retinal degeneration.

Authors:  Lijuan Zhang; Jianhai Du; Sally Justus; Chun-Wei Hsu; Luis Bonet-Ponce; Wen-Hsuan Wu; Yi-Ting Tsai; Wei-Pu Wu; Yading Jia; Jimmy K Duong; Vinit B Mahajan; Chyuan-Sheng Lin; Shuang Wang; James B Hurley; Stephen H Tsang
Journal:  J Clin Invest       Date:  2016-11-14       Impact factor: 14.808

4.  Cone outer segment morphology and cone function in the Rpe65-/- Nrl-/- mouse retina are amenable to retinoid replacement.

Authors:  Kannan Kunchithapautham; Beth Coughlin; Rosalie K Crouch; Bärbel Rohrer
Journal:  Invest Ophthalmol Vis Sci       Date:  2009-04-30       Impact factor: 4.799

5.  Halting progressive neurodegeneration in advanced retinitis pigmentosa.

Authors:  Susanne F Koch; Yi-Ting Tsai; Jimmy K Duong; Wen-Hsuan Wu; Chun-Wei Hsu; Wei-Pu Wu; Luis Bonet-Ponce; Chyuan-Sheng Lin; Stephen H Tsang
Journal:  J Clin Invest       Date:  2015-08-24       Impact factor: 14.808
  5 in total
  1 in total

1.  Quantitative Autofluorescence Following Gene Therapy With Voretigene Neparvovec.

Authors:  Sarah R Levi; Jin Kyun Oh; Jose Ronaldo Lima de Carvalho; Vinit B Mahajan; Stephen H Tsang; Janet R Sparrow
Journal:  JAMA Ophthalmol       Date:  2020-08-01       Impact factor: 8.253
  1 in total

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