Literature DB >> 31248723

The Right Tools for the Right Job: CRISPR-pass Could Offer Safe Gene Correction for Many Disorders.

David J Segal1.   

Abstract

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Year:  2019        PMID: 31248723      PMCID: PMC6698281          DOI: 10.1016/j.ymthe.2019.06.008

Source DB:  PubMed          Journal:  Mol Ther        ISSN: 1525-0016            Impact factor:   11.454


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  13 in total

1.  Cytosine, but not adenine, base editors induce genome-wide off-target mutations in rice.

Authors:  Shuai Jin; Yuan Zong; Qiang Gao; Zixu Zhu; Yanpeng Wang; Peng Qin; Chengzhi Liang; Daowen Wang; Jin-Long Qiu; Feng Zhang; Caixia Gao
Journal:  Science       Date:  2019-02-28       Impact factor: 47.728

2.  Postnatal genome editing partially restores dystrophin expression in a mouse model of muscular dystrophy.

Authors:  Chengzu Long; Leonela Amoasii; Alex A Mireault; John R McAnally; Hui Li; Efrain Sanchez-Ortiz; Samadrita Bhattacharyya; John M Shelton; Rhonda Bassel-Duby; Eric N Olson
Journal:  Science       Date:  2015-12-31       Impact factor: 47.728

3.  In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy.

Authors:  Christopher E Nelson; Chady H Hakim; David G Ousterout; Pratiksha I Thakore; Eirik A Moreb; Ruth M Castellanos Rivera; Sarina Madhavan; Xiufang Pan; F Ann Ran; Winston X Yan; Aravind Asokan; Feng Zhang; Dongsheng Duan; Charles A Gersbach
Journal:  Science       Date:  2015-12-31       Impact factor: 47.728

4.  Cytosine base editor generates substantial off-target single-nucleotide variants in mouse embryos.

Authors:  Erwei Zuo; Yidi Sun; Wu Wei; Tanglong Yuan; Wenqin Ying; Hao Sun; Liyun Yuan; Lars M Steinmetz; Yixue Li; Hui Yang
Journal:  Science       Date:  2019-02-28       Impact factor: 47.728

5.  De novo gene disruptions in children on the autistic spectrum.

Authors:  Ivan Iossifov; Michael Ronemus; Dan Levy; Zihua Wang; Inessa Hakker; Julie Rosenbaum; Boris Yamrom; Yoon-Ha Lee; Giuseppe Narzisi; Anthony Leotta; Jude Kendall; Ewa Grabowska; Beicong Ma; Steven Marks; Linda Rodgers; Asya Stepansky; Jennifer Troge; Peter Andrews; Mitchell Bekritsky; Kith Pradhan; Elena Ghiban; Melissa Kramer; Jennifer Parla; Ryan Demeter; Lucinda L Fulton; Robert S Fulton; Vincent J Magrini; Kenny Ye; Jennifer C Darnell; Robert B Darnell; Elaine R Mardis; Richard K Wilson; Michael C Schatz; W Richard McCombie; Michael Wigler
Journal:  Neuron       Date:  2012-04-26       Impact factor: 17.173

6.  Gentamicin-induced readthrough of stop codons in Duchenne muscular dystrophy.

Authors:  Vinod Malik; Louise R Rodino-Klapac; Laurence Viollet; Cheryl Wall; Wendy King; Roula Al-Dahhak; Sarah Lewis; Christopher J Shilling; Janaiah Kota; Carmen Serrano-Munuera; John Hayes; John D Mahan; Katherine J Campbell; Brenda Banwell; Majed Dasouki; Victoria Watts; Kumaraswamy Sivakumar; Ricardo Bien-Willner; Kevin M Flanigan; Zarife Sahenk; Richard J Barohn; Christopher M Walker; Jerry R Mendell
Journal:  Ann Neurol       Date:  2010-06       Impact factor: 10.422

7.  Long-term evaluation of AAV-CRISPR genome editing for Duchenne muscular dystrophy.

Authors:  Christopher E Nelson; Yaoying Wu; Matthew P Gemberling; Matthew L Oliver; Matthew A Waller; Joel D Bohning; Jacqueline N Robinson-Hamm; Karen Bulaklak; Ruth M Castellanos Rivera; Joel H Collier; Aravind Asokan; Charles A Gersbach
Journal:  Nat Med       Date:  2019-02-18       Impact factor: 53.440

8.  CRISPR-Pass: Gene Rescue of Nonsense Mutations Using Adenine Base Editors.

Authors:  Choongil Lee; Dong Hyun Jo; Gue-Ho Hwang; Jihyeon Yu; Jin Hyoung Kim; Se-Eun Park; Jin-Soo Kim; Jeong Hun Kim; Sangsu Bae
Journal:  Mol Ther       Date:  2019-05-24       Impact factor: 11.454

9.  Evolved Cas9 variants with broad PAM compatibility and high DNA specificity.

Authors:  Johnny H Hu; Shannon M Miller; Maarten H Geurts; Weixin Tang; Liwei Chen; Ning Sun; Christina M Zeina; Xue Gao; Holly A Rees; Zhi Lin; David R Liu
Journal:  Nature       Date:  2018-02-28       Impact factor: 49.962

10.  Optimized base editors enable efficient editing in cells, organoids and mice.

Authors:  Maria Paz Zafra; Emma M Schatoff; Alyna Katti; Miguel Foronda; Marco Breinig; Anabel Y Schweitzer; Amber Simon; Teng Han; Sukanya Goswami; Emma Montgomery; Jordana Thibado; Edward R Kastenhuber; Francisco J Sánchez-Rivera; Junwei Shi; Christopher R Vakoc; Scott W Lowe; Darjus F Tschaharganeh; Lukas E Dow
Journal:  Nat Biotechnol       Date:  2018-07-03       Impact factor: 54.908

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