Literature DB >> 31202634

ERT Degrades Gene Therapy for Storage Disorder.

David Michael Markusic1.   

Abstract

Entities:  

Mesh：

Year:  2019        PMID： 31202634      PMCID： PMC6612798          DOI： 10.1016/j.ymthe.2019.06.002

Source DB:  PubMed          Journal:  Mol Ther        ISSN： 1525-0016            Impact factor:   11.454


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  5 in total

Review 1.  Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications.

Authors:  Alessandra Biffi
Journal:  Mol Ther       Date:  2017-04-04       Impact factor: 11.454

Review 2.  Platelet-Targeted Gene Therapy for Hemophilia.

Authors:  Qizhen Shi
Journal:  Mol Ther Methods Clin Dev       Date:  2018-02-07       Impact factor: 6.698

3.  Targeting a Pre-existing Anti-transgene T Cell Response for Effective Gene Therapy of MPS-I in the Mouse Model of the Disease.

Authors:  Giorgia Squeri; Laura Passerini; Francesca Ferro; Cecilia Laudisa; Daniela Tomasoni; Federica Deodato; Maria Alice Donati; Serena Gasperini; Alessandro Aiuti; Maria Ester Bernardo; Bernhard Gentner; Luigi Naldini; Andrea Annoni; Alessandra Biffi; Silvia Gregori
Journal:  Mol Ther       Date:  2019-04-19       Impact factor: 11.454

4.  Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy.

Authors:  Alessandra Biffi; Eugenio Montini; Laura Lorioli; Martina Cesani; Francesca Fumagalli; Tiziana Plati; Cristina Baldoli; Sabata Martino; Andrea Calabria; Sabrina Canale; Fabrizio Benedicenti; Giuliana Vallanti; Luca Biasco; Simone Leo; Nabil Kabbara; Gianluigi Zanetti; William B Rizzo; Nalini A L Mehta; Maria Pia Cicalese; Miriam Casiraghi; Jaap J Boelens; Ubaldo Del Carro; David J Dow; Manfred Schmidt; Andrea Assanelli; Victor Neduva; Clelia Di Serio; Elia Stupka; Jason Gardner; Christof von Kalle; Claudio Bordignon; Fabio Ciceri; Attilio Rovelli; Maria Grazia Roncarolo; Alessandro Aiuti; Maria Sessa; Luigi Naldini
Journal:  Science       Date:  2013-07-11       Impact factor: 47.728

Review 5.  Gene therapy for lysosomal storage disorders: recent advances for metachromatic leukodystrophy and mucopolysaccaridosis I.

Authors:  Rachele Penati; Francesca Fumagalli; Valeria Calbi; Maria Ester Bernardo; Alessandro Aiuti
Journal:  J Inherit Metab Dis       Date:  2017-05-30       Impact factor: 4.982
  5 in total
  1 in total

Review 1.  Immune Responses to Viral Gene Therapy Vectors.

Authors:  Jamie L Shirley; Ype P de Jong; Cox Terhorst; Roland W Herzog
Journal:  Mol Ther       Date:  2020-01-10       Impact factor: 11.454
  1 in total

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