Literature DB >> 31184581

Physical activity improved by adherence to prophylaxis in an Italian population of children, adolescents and adults with severe haemophilia A: the SHAPE Study.

Ezio Zanon1, Annarita Tagliaferri2, Samantha Pasca1, Cosimo P Ettorre3, Lucia D Notarangelo4, Chiara Biasioli5, Anna B Aru6, Marta Milan1, Silvia Linari7, Angiola Rocino8, Fabio Gagliano9, Giovanni Di Minno10, Gabriella Gamba11, Rita C Santoro12, Piercarla Schinco13, Marco Marietta14, Axel Seuser15, Sylvia von Mackensen16.   

Abstract

BACKGROUND: Physical activity in people with haemophilia (PWH) reduces the development of severe arthropathy, but it must be performed after regular, proper prophylaxis. Strict adherence to treatment is crucial to achieving effectiveness and established outcomes. The primary aim of this study was to collect prospective data on adherence to prophylaxis for over 36 months. A secondary aim was to verify whether adherence correlates with physical activity.
MATERIALS AND METHODS: Italian patients with severe haemophilia A treated on prophylaxis with octocog alfa were included in the study. Physical findings were assessed by the Haemophilia and Exercise Project (HEP)-Test-Q and the Early Prophylaxis Immunologic Challenge (EPIC)-Norfolk Physical Activity Questionnaire; orthopaedic status was assessed by the Hemophilia Joint Health Score (HJHS). Adherence was measured as percentage of empty vials returned with respect to the prescribed amount.
RESULTS: Forty-two PWH were enrolled: 31% children, 21.4% adolescents, and 47.6% adults. Type, frequency and impact of physical activities differed among the three groups. The HEP-Test-Q showed the highest impairments in the domains "endurance" and "strength/co-ordination". Eight percent of patients were classified as adherent to prophylaxis. Among them, 50% had at least one bleeding episode in the year before enrolment; this percentage dropped during the three years of the study. While remaining stable in the "non-adherent" group, the HJHS score decreased in the "adherent" patients. The mean number of school/work days lost was lower in adherent patients (from 3.4±6.8 to 0.2±0.9) than in non-adherent ones. DISCUSSION: PWH with better orthopaedic scores reported better physical performance. Adherence to long-term prophylaxis proved to be high and correlated with a reduction in bleeds, target joints, school/work days lost, and with a performance improvement in endurance sports activities over time.

Entities:  

Year:  2019        PMID: 31184581      PMCID: PMC7141936          DOI: 10.2450/2019.0040-19

Source DB:  PubMed          Journal:  Blood Transfus        ISSN: 1723-2007            Impact factor:   3.443


  26 in total

1.  Barriers to compliance with prophylaxis therapy in haemophilia.

Authors:  M R Hacker; S Geraghty; M Manco-Johnson
Journal:  Haemophilia       Date:  2001-07       Impact factor: 4.287

2.  Secondary prophylaxis vs. on-demand treatment to improve quality of life in severe adult haemophilia A patients: a prospective study in a single centre.

Authors:  J A Aznar; M García-Dasí; S Pérez-Alenda; A Marco; M Jaca; A Moret; F Querol
Journal:  Vox Sang       Date:  2013-06-27       Impact factor: 2.144

3.  Prophylaxis: musculoskeletal evaluation.

Authors:  M S Gilbert
Journal:  Semin Hematol       Date:  1993-07       Impact factor: 3.851

4.  A randomized clinical trial of prophylaxis in children with hemophilia A (the ESPRIT Study).

Authors:  A Gringeri; B Lundin; S von Mackensen; L Mantovani; P M Mannucci
Journal:  J Thromb Haemost       Date:  2011-04       Impact factor: 5.824

5.  Use of implantable venous access devices in children with severe hemophilia: benefits and burden.

Authors:  Karin Van Dijk; Johanna G Van Der Bom; Klaas N M A Bax; David C Van Der Zee; Marijke H Van Den Berg
Journal:  Haematologica       Date:  2004-02       Impact factor: 9.941

6.  Adherence to prophylaxis and bleeding outcome in haemophilia: a multicentre study.

Authors:  LieSbeth H Schrijvers; Marlene Beijlevelt-van der Zande; Marjolein Peters; Janske Lock; Marjon H Cnossen; Marieke J Schuurmans; Kathelijn Fischer
Journal:  Br J Haematol       Date:  2016-04-21       Impact factor: 6.998

7.  Development and validation of a new questionnaire for the assessment of subjective physical performance in adult patients with haemophilia--the HEP-Test-Q.

Authors:  S von Mackensen; D Czepa; M Herbsleb; T Hilberg
Journal:  Haemophilia       Date:  2009-10-21       Impact factor: 4.287

8.  Effects of secondary prophylaxis started in adolescent and adult haemophiliacs.

Authors:  A Tagliaferri; M Franchini; A Coppola; G F Rivolta; C Santoro; G Rossetti; G Feola; E Zanon; A Dragani; P Iannaccaro; P Radossi; P M Mannucci
Journal:  Haemophilia       Date:  2008-06-05       Impact factor: 4.287

9.  Better adherence to prescribed treatment regimen is related to less chronic pain among adolescents and young adults with moderate or severe haemophilia.

Authors:  J M McLaughlin; M L Witkop; A Lambing; T L Anderson; J Munn; B Tortella
Journal:  Haemophilia       Date:  2014-02-11       Impact factor: 4.287

Review 10.  Treatment adherence in hemophilia.

Authors:  Courtney D Thornburg; Natalie A Duncan
Journal:  Patient Prefer Adherence       Date:  2017-09-27       Impact factor: 2.711

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  3 in total

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Authors:  Ionut Hotea; Melen Brinza; Cristina Blag; Alina-Andreea Zimta; Noemi Dirzu; Corina Burzo; Ioana Rus; Dragos Apostu; Horea Benea; Mirela Marian; Alexandru Mester; Sergiu Pasca; Sabina Iluta; Patric Teodorescu; Ciprian Jitaru; Mihnea Zdrenghea; Anca Bojan; Tunde Torok-Vistai; Radu Niculescu; Cristina Tarniceriu; Delia Dima; Cristina Truica; Margit Serban; Ciprian Tomuleasa; Daniel Coriu
Journal:  Ann Transl Med       Date:  2021-07

2.  A Delphi Consensus Approach for Difficult-to-Treat Patients with Severe Hemophilia A without Inhibitors.

Authors:  Sreenivas P Veeranki; Priti Pednekar; Marlon Graf; Rifat Tuly; Michael Recht; Katharine Batt
Journal:  J Blood Med       Date:  2021-10-21

Review 3.  Factor VIII replacement prophylaxis in patients with hemophilia A transitioning to adults: a systematic literature review.

Authors:  Jing Sun; Xuan Zhou; Nan Hu
Journal:  Orphanet J Rare Dis       Date:  2021-06-26       Impact factor: 4.123

  3 in total

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