Literature DB >> 31168457

SF3B1 mutation predicts unfavorable treatment-free survival in Chinese chronic lymphocytic leukemia patients.

Yi Miao1,2,3, Yi-Xin Zou1,2,3, Dan-Ling Gu1,2,3, Hong-Cheng Zhu4, Hua-Yuan Zhu1,2,3, Li Wang1,2,3, Jin-Hua Liang1,2,3, Yi Xia1,2,3, Jia-Zhu Wu1,2,3, Chun-Lin Shao5, Lei Fan1,2,3, Zhen Zhang4, Wei Xu1,2,3, Jian-Yong Li1,2,3.   

Abstract

BACKGROUND: Splicing factor 3b subunit 1 (SF3B1), a splicing factor modulating RNA alternative splicing, is frequently mutated in multiple hematological malignancies including myelodysplastic syndromes and chronic lymphocytic leukemia (CLL). The clinical impact of SF3B1 mutation on CLL remains controversial especially for patients of Asian descent.
METHODS: We retrospectively analyzed the frequency of SF3B1 mutation by Sanger sequencing in 399 newly diagnosed Chinese CLL patients.
RESULTS: SF3B1 mutation was detected in 5.5% (22/399) of the studied cohort with 59.1% of them being c.A2098G (p.K700E). SF3B1 mutation was common in patients with unmutated immunoglobulin heavy chain variable region gene, positive CD38 and positive ZAP-70. Survival analysis showed that SF3B1 mutation was associated with short treatment-free survival (TFS), but not overall survival (OS). We then developed 2 new risk models, named CLL-IPI-S and CLL-PI, according to the SF3B1 mutation status and CLL-international prognostic index (CLL-IPI); CLL-PI showed greater power to predict TFS than CLL-IPI in Chinese CLL patients.
CONCLUSIONS: Our data suggest a low incidence and adverse clinical significance of SF3B1 mutation in newly diagnosed Chinese CLL patients.

Entities:  

Keywords:  Splicing factor 3b subunit 1 mutation (SF3B1 mutation); chronic lymphocytic leukemia (CLL); prognosis; risk models

Year:  2019        PMID: 31168457      PMCID: PMC6526254          DOI: 10.21037/atm.2019.03.63

Source DB:  PubMed          Journal:  Ann Transl Med        ISSN: 2305-5839


  21 in total

1.  Mutations of the SF3B1 splicing factor in chronic lymphocytic leukemia: association with progression and fludarabine-refractoriness.

Authors:  Davide Rossi; Alessio Bruscaggin; Valeria Spina; Silvia Rasi; Hossein Khiabanian; Monica Messina; Marco Fangazio; Tiziana Vaisitti; Sara Monti; Sabina Chiaretti; Anna Guarini; Ilaria Del Giudice; Michaela Cerri; Stefania Cresta; Clara Deambrogi; Ernesto Gargiulo; Valter Gattei; Francesco Forconi; Francesco Bertoni; Silvia Deaglio; Raul Rabadan; Laura Pasqualucci; Robin Foà; Riccardo Dalla-Favera; Gianluca Gaidano
Journal:  Blood       Date:  2011-10-28       Impact factor: 22.113

2.  Clinical impact of small subclones harboring NOTCH1, SF3B1 or BIRC3 mutations in chronic lymphocytic leukemia.

Authors:  Silvia Rasi; Hossein Khiabanian; Carmela Ciardullo; Lodovico Terzi-di-Bergamo; Sara Monti; Valeria Spina; Alessio Bruscaggin; Michaela Cerri; Clara Deambrogi; Lavinia Martuscelli; Alessandra Biasi; Elisa Spaccarotella; Lorenzo De Paoli; Valter Gattei; Robin Foà; Raul Rabadan; Gianluca Gaidano; Davide Rossi
Journal:  Haematologica       Date:  2016-01-27       Impact factor: 9.941

3.  Impact of trisomy 12, del(13q), del(17p), and del(11q) on the immunophenotype, DNA ploidy status, and proliferative rate of leukemic B-cells in chronic lymphocytic leukemia.

Authors:  Sandra Quijano; Antonio López; Ana Rasillo; José María Sayagués; Susana Barrena; Maria Luz Sánchez; Cristina Teodosio; Pilar Giraldo; Manuel Giralt; M Carmen Pérez; Mercedes Romero; Luis Perdiguer; Alberto Orfao
Journal:  Cytometry B Clin Cytom       Date:  2008-05       Impact factor: 3.058

4.  SF3B1 mutations correlated to cytogenetics and mutations in NOTCH1, FBXW7, MYD88, XPO1 and TP53 in 1160 untreated CLL patients.

Authors:  S Jeromin; S Weissmann; C Haferlach; F Dicker; K Bayer; V Grossmann; T Alpermann; A Roller; A Kohlmann; T Haferlach; W Kern; S Schnittger
Journal:  Leukemia       Date:  2013-09-12       Impact factor: 11.528

5.  Distinct patterns of novel gene mutations in poor-prognostic stereotyped subsets of chronic lymphocytic leukemia: the case of SF3B1 and subset #2.

Authors:  J C Strefford; L-A Sutton; P Baliakas; A Agathangelidis; J Malčíková; K Plevova; L Scarfó; Z Davis; E Stalika; D Cortese; N Cahill; L B Pedersen; P F di Celle; T Tzenou; C Geisler; P Panagiotidis; A W Langerak; N Chiorazzi; S Pospisilova; D Oscier; F Davi; C Belessi; L Mansouri; P Ghia; K Stamatopoulos; R Rosenquist
Journal:  Leukemia       Date:  2013-04-05       Impact factor: 11.528

6.  Whole-genome sequencing identifies recurrent mutations in chronic lymphocytic leukaemia.

Authors:  Xose S Puente; Magda Pinyol; Víctor Quesada; Laura Conde; Gonzalo R Ordóñez; Neus Villamor; Georgia Escaramis; Pedro Jares; Sílvia Beà; Marcos González-Díaz; Laia Bassaganyas; Tycho Baumann; Manel Juan; Mónica López-Guerra; Dolors Colomer; José M C Tubío; Cristina López; Alba Navarro; Cristian Tornador; Marta Aymerich; María Rozman; Jesús M Hernández; Diana A Puente; José M P Freije; Gloria Velasco; Ana Gutiérrez-Fernández; Dolors Costa; Anna Carrió; Sara Guijarro; Anna Enjuanes; Lluís Hernández; Jordi Yagüe; Pilar Nicolás; Carlos M Romeo-Casabona; Heinz Himmelbauer; Ester Castillo; Juliane C Dohm; Silvia de Sanjosé; Miguel A Piris; Enrique de Alava; Jesús San Miguel; Romina Royo; Josep L Gelpí; David Torrents; Modesto Orozco; David G Pisano; Alfonso Valencia; Roderic Guigó; Mónica Bayés; Simon Heath; Marta Gut; Peter Klatt; John Marshall; Keiran Raine; Lucy A Stebbings; P Andrew Futreal; Michael R Stratton; Peter J Campbell; Ivo Gut; Armando López-Guillermo; Xavier Estivill; Emili Montserrat; Carlos López-Otín; Elías Campo
Journal:  Nature       Date:  2011-06-05       Impact factor: 49.962

7.  The impact of SF3B1 mutations in CLL on the DNA-damage response.

Authors:  G D Te Raa; I A M Derks; V Navrkalova; A Skowronska; P D Moerland; J van Laar; C Oldreive; H Monsuur; M Trbusek; J Malcikova; M Lodén; C H Geisler; J Hüllein; A Jethwa; T Zenz; S Pospisilova; T Stankovic; M H J van Oers; A P Kater; E Eldering
Journal:  Leukemia       Date:  2014-11-05       Impact factor: 11.528

8.  Clinical significance of SF3B1 mutations in myelodysplastic syndromes and myelodysplastic/myeloproliferative neoplasms.

Authors:  Luca Malcovati; Elli Papaemmanuil; David T Bowen; Jacqueline Boultwood; Matteo G Della Porta; Cristiana Pascutto; Erica Travaglino; Michael J Groves; Anna L Godfrey; Ilaria Ambaglio; Anna Gallì; Matteo C Da Vià; Simona Conte; Sudhir Tauro; Norene Keenan; Ann Hyslop; Jonathan Hinton; Laura J Mudie; James S Wainscoat; P Andrew Futreal; Michael R Stratton; Peter J Campbell; Eva Hellström-Lindberg; Mario Cazzola
Journal:  Blood       Date:  2011-10-12       Impact factor: 22.113

9.  Frequencies of SF3B1, NOTCH1, MYD88, BIRC3 and IGHV mutations and TP53 disruptions in Chinese with chronic lymphocytic leukemia: disparities with Europeans.

Authors:  Yi Xia; Lei Fan; Li Wang; Robert Peter Gale; Man Wang; Tian Tian; Wei Wu; Liang Yu; Yao-Yu Chen; Wei Xu; Jian-Yong Li
Journal:  Oncotarget       Date:  2015-03-10

10.  Comprehensive molecular portraits of human breast tumours.

Authors: 
Journal:  Nature       Date:  2012-09-23       Impact factor: 49.962

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  3 in total

1.  The potential differential diagnosis value and clinical significance of CD35 expression in B-chronic lymphoproliferative disorders.

Authors:  Yu Shi; Lu Liu; Hui Yang; Xiao Chen; Yan Wang; Sishu Zhao; Huimin Jin; Yujie Wu
Journal:  Ann Transl Med       Date:  2021-07

Review 2.  Roles and mechanisms of alternative splicing in cancer - implications for care.

Authors:  Sophie C Bonnal; Irene López-Oreja; Juan Valcárcel
Journal:  Nat Rev Clin Oncol       Date:  2020-04-17       Impact factor: 66.675

3.  Prognostic models for newly-diagnosed chronic lymphocytic leukaemia in adults: a systematic review and meta-analysis.

Authors:  Nina Kreuzberger; Johanna Aag Damen; Marialena Trivella; Lise J Estcourt; Angela Aldin; Lisa Umlauff; Maria Dla Vazquez-Montes; Robert Wolff; Karel Gm Moons; Ina Monsef; Farid Foroutan; Karl-Anton Kreuzer; Nicole Skoetz
Journal:  Cochrane Database Syst Rev       Date:  2020-07-31
  3 in total

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