Literature DB >> 31028669

Targeting BTK in CLL: Beyond Ibrutinib.

David A Bond1, Jennifer A Woyach2.   

Abstract

PURPOSE OF REVIEW: While the Bruton's tyrosine kinase inhibitor (BTKi) ibrutinib has revolutionized the treatment of chronic lymphocytic leukemia (CLL), current limitations include off-target toxicities and the development of resistance. In this review, we summarize the emerging data for alternative BTKi. RECENT
FINDINGS: Second-generation BTKi include acalabrutinib, zanubrutinib, and tirabrutinib which offer greater BTK selectivity. While these agents may limit off-target toxicity, they do not overcome common mechanisms of ibrutinib resistance. Reversible BTKi including vecabrutinib and LOXO-305 inhibit BTK in the presence of C481S mutation, and non-selective reversible BTKi, including ARQ-531, may retain activity despite mutations within PLCG2. Early-phase studies are underway to establish the clinical efficacy and toxicity of these agents. A randomized trial of ibrutinib versus acalabrutinib is ongoing, and acalabrutinib may be an option for ibrutinib-intolerant patients. Results from ongoing trials of alternate BTKi will help to define their role in CLL therapy as single agents or in combination therapy.

Entities:  

Keywords:  Acalabrutinib; B cell receptor; Tirabrutinib; Zanubrutinib

Mesh:

Substances:

Year:  2019        PMID: 31028669     DOI: 10.1007/s11899-019-00512-0

Source DB:  PubMed          Journal:  Curr Hematol Malig Rep        ISSN: 1558-8211            Impact factor:   3.952


  61 in total

1.  Age at diagnosis and the utility of prognostic testing in patients with chronic lymphocytic leukemia.

Authors:  Tait D Shanafelt; Kari G Rabe; Neil E Kay; Clive S Zent; Diane F Jelinek; Megan S Reinalda; Susan M Schwager; Debbie A Bowen; Susan L Slager; Curtis A Hanson; Timothy G Call
Journal:  Cancer       Date:  2010-10-15       Impact factor: 6.860

2.  Chronic lymphocytic leukemia B cells contain anomalous Lyn tyrosine kinase, a putative contribution to defective apoptosis.

Authors:  Antonella Contri; Anna Maria Brunati; Livio Trentin; Anna Cabrelle; Marta Miorin; Luca Cesaro; Lorenzo A Pinna; Renato Zambello; Gianpietro Semenzato; Arianna Donella-Deana
Journal:  J Clin Invest       Date:  2005-02       Impact factor: 14.808

3.  Unmutated and mutated chronic lymphocytic leukemias derive from self-reactive B cell precursors despite expressing different antibody reactivity.

Authors:  Maxime Hervé; Kai Xu; Yen-Shing Ng; Hedda Wardemann; Emilia Albesiano; Bradley T Messmer; Nicholas Chiorazzi; Eric Meffre
Journal:  J Clin Invest       Date:  2005-05-02       Impact factor: 14.808

4.  Solid tumors after chronic lymphocytic leukemia.

Authors:  M Hisada; R J Biggar; M H Greene; J F Fraumeni; L B Travis
Journal:  Blood       Date:  2001-09-15       Impact factor: 22.113

5.  Tec regulates platelet activation by GPVI in the absence of Btk.

Authors:  Ben T Atkinson; Wilfried Ellmeier; Steve P Watson
Journal:  Blood       Date:  2003-07-03       Impact factor: 22.113

6.  Constitutive activation of distinct BCR-signaling pathways in a subset of CLL patients: a molecular signature of anergy.

Authors:  Marta Muzio; Benedetta Apollonio; Cristina Scielzo; Michela Frenquelli; Irene Vandoni; Vassiliki Boussiotis; Federico Caligaris-Cappio; Paolo Ghia
Journal:  Blood       Date:  2008-02-21       Impact factor: 22.113

7.  Guidelines for the diagnosis and treatment of chronic lymphocytic leukemia: a report from the International Workshop on Chronic Lymphocytic Leukemia updating the National Cancer Institute-Working Group 1996 guidelines.

Authors:  Michael Hallek; Bruce D Cheson; Daniel Catovsky; Federico Caligaris-Cappio; Guillaume Dighiero; Hartmut Döhner; Peter Hillmen; Michael J Keating; Emili Montserrat; Kanti R Rai; Thomas J Kipps
Journal:  Blood       Date:  2008-01-23       Impact factor: 22.113

8.  Second cancers in patients with chronic lymphocytic leukemia.

Authors:  L B Travis; R E Curtis; B F Hankey; J F Fraumeni
Journal:  J Natl Cancer Inst       Date:  1992-09-16       Impact factor: 13.506

9.  Other malignancies in chronic lymphocytic leukemia/small lymphocytic lymphoma.

Authors:  Apostolia-Maria Tsimberidou; Sijin Wen; Peter McLaughlin; Susan O'Brien; William G Wierda; Susan Lerner; Sara Strom; Emil J Freireich; L Jeffrey Medeiros; Hagop M Kantarjian; Michael J Keating
Journal:  J Clin Oncol       Date:  2008-12-29       Impact factor: 44.544

10.  Constitutively activated phosphatidylinositol-3 kinase (PI-3K) is involved in the defect of apoptosis in B-CLL: association with protein kinase Cdelta.

Authors:  Ingo Ringshausen; Folker Schneller; Christian Bogner; Susanne Hipp; Justus Duyster; Christian Peschel; Thomas Decker
Journal:  Blood       Date:  2002-07-12       Impact factor: 22.113

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  29 in total

1.  Overcoming resistance to targeted therapies in chronic lymphocytic leukemia.

Authors:  Sigrid S Skånland; Anthony R Mato
Journal:  Blood Adv       Date:  2021-01-12

Review 2.  Proteolysis-targeting chimaeras (PROTACs) as pharmacological tools and therapeutic agents: advances and future challenges.

Authors:  Chao Wang; Yujing Zhang; Tingting Zhang; Lingyu Shi; Zhongmin Geng; Dongming Xing
Journal:  J Enzyme Inhib Med Chem       Date:  2022-12       Impact factor: 5.756

3.  Cardiovascular adverse events in patients with chronic lymphocytic leukemia receiving acalabrutinib monotherapy: pooled analysis of 762 patients.

Authors:  Jennifer R Brown; John C Byrd; Paolo Ghia; Jeff P Sharman; Peter Hillmen; Deborah M Stephens; Clare Sun; Wojciech Jurczak; John M Pagel; Alessandra Ferrajoli; Priti Patel; Lin Tao; Nataliya Kuptsova-Clarkson; Javid Moslehi; Richard R Furman
Journal:  Haematologica       Date:  2022-06-01       Impact factor: 11.047

4.  Efficacy and Safety of Tirabrutinib and Idelalisib With or Without Obinutuzumab in Relapsed Chronic Lymphocytic Leukemia.

Authors:  Nadine Kutsch; Christian Pallasch; Thomas Decker; Holger Hebart; Kai Uwe Chow; Ullrich Graeven; Jens Kisro; Alexander Kroeber; Eugen Tausch; Kirsten Fischer; Anna-Maria Fink; Clemens-Martin Wendtner; Matthias Ritgen; Stephan Stilgenbauer; Danjie Zhang; Biao Li; Juliane M Jürgensmeier; Nishanthan Rajakumaraswamy; Pankaj Bhargava; Michael Hallek; Barbara Eichhorst
Journal:  Hemasphere       Date:  2022-05-25

5.  Noncatalytic Bruton's tyrosine kinase activates PLCγ2 variants mediating ibrutinib resistance in human chronic lymphocytic leukemia cells.

Authors:  Martin Wist; Laura Meier; Orit Gutman; Jennifer Haas; Sascha Endres; Yuan Zhou; Reinhild Rösler; Sebastian Wiese; Stephan Stilgenbauer; Elias Hobeika; Yoav I Henis; Peter Gierschik; Claudia Walliser
Journal:  J Biol Chem       Date:  2020-03-17       Impact factor: 5.157

Review 6.  The resistance mechanisms and treatment strategies of BTK inhibitors in B-cell lymphoma.

Authors:  Haoran Wang; Wentao Zhang; Jingyi Yang; Keshu Zhou
Journal:  Hematol Oncol       Date:  2021-10-15       Impact factor: 4.850

7.  Acalabrutinib Versus Ibrutinib in Previously Treated Chronic Lymphocytic Leukemia: Results of the First Randomized Phase III Trial.

Authors:  John C Byrd; Peter Hillmen; Paolo Ghia; Arnon P Kater; Asher Chanan-Khan; Richard R Furman; Susan O'Brien; Mustafa Nuri Yenerel; Arpad Illés; Neil Kay; Jose A Garcia-Marco; Anthony Mato; Javier Pinilla-Ibarz; John F Seymour; Stephane Lepretre; Stephan Stilgenbauer; Tadeusz Robak; Wayne Rothbaum; Raquel Izumi; Ahmed Hamdy; Priti Patel; Kara Higgins; Sophia Sohoni; Wojciech Jurczak
Journal:  J Clin Oncol       Date:  2021-07-26       Impact factor: 44.544

Review 8.  NK Cells in Chronic Lymphocytic Leukemia and Their Therapeutic Implications.

Authors:  Paolo Sportoletti; Filomena De Falco; Beatrice Del Papa; Stefano Baldoni; Valerio Guarente; Andrea Marra; Erica Dorillo; Chiara Rompietti; Francesco Maria Adamo; Loredana Ruggeri; Mauro Di Ianni; Emanuela Rosati
Journal:  Int J Mol Sci       Date:  2021-06-22       Impact factor: 5.923

9.  BTK inhibitors, irrespective of ITK inhibition, increase efficacy of a CD19/CD3-bispecific antibody in CLL.

Authors:  Maissa Mhibik; Erika M Gaglione; David Eik; Ellen K Kendall; Amy Blackburn; Keyvan Keyvanfar; Maria Joao Baptista; Inhye E Ahn; Clare Sun; Junpeng Qi; Christoph Rader; Adrian Wiestner
Journal:  Blood       Date:  2021-11-11       Impact factor: 22.113

Review 10.  Resistance to Bruton tyrosine kinase inhibitors: the Achilles heel of their success story in lymphoid malignancies.

Authors:  Deborah M Stephens; John C Byrd
Journal:  Blood       Date:  2021-09-30       Impact factor: 25.476

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