Literature DB >> 30952673

Two decades of excellent transplant survival for chronic granulomatous disease: a supraregional immunology transplant center report.

Su Han Lum1, Terence Flood1, Sophie Hambleton1,2, Peter McNaughton1, Helen Watson3, Mario Abinun1,2, Stephen Owens1, Nevenka Cigrovski1, Andrew Cant1, Andrew R Gennery1,2, Mary Slatter1,2.   

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Year:  2019        PMID: 30952673     DOI: 10.1182/blood.2019000021

Source DB:  PubMed          Journal:  Blood        ISSN: 0006-4971            Impact factor:   22.113


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  7 in total

Review 1.  Long Term Outcome and Immune Function After Hematopoietic Stem Cell Transplantation for Primary Immunodeficiency.

Authors:  Andrew R Gennery; Arjan Lankester
Journal:  Front Pediatr       Date:  2019-09-24       Impact factor: 3.418

2.  T-replete HLA-matched grafts vs T-depleted HLA-mismatched grafts in inborn errors of immunity.

Authors:  Su Han Lum; Sinéad Greener; Inigo Perez-Heras; Daniel Drozdov; Rebecca P Payne; Helen Watson; Kay Carruthers; Robert January; Zohreh Nademi; Stephen Owens; Eleri Williams; Sheila Waugh; Shirelle Burton-Fanning; Timmothy Ronan Leahy; Andrew Cant; Mario Abinun; Terry Flood; Sophie Hambleton; Andrew R Gennery; Mary Slatter
Journal:  Blood Adv       Date:  2022-02-22

Review 3.  Update on Clinical Ex Vivo Hematopoietic Stem Cell Gene Therapy for Inherited Monogenic Diseases.

Authors:  Francesca Tucci; Samantha Scaramuzza; Alessandro Aiuti; Alessandra Mortellaro
Journal:  Mol Ther       Date:  2020-11-20       Impact factor: 11.454

Review 4.  Treosulfan-based conditioning for inborn errors of immunity.

Authors:  Mary A Slatter; Andrew R Gennery
Journal:  Ther Adv Hematol       Date:  2021-05-20

5.  Urogenital Abnormalities in Adenosine Deaminase Deficiency.

Authors:  Roberta Pajno; Lucia Pacillo; Salvatore Recupero; Maria P Cicalese; Francesca Ferrua; Federica Barzaghi; Silvia Ricci; Antonio Marzollo; Silvia Pecorelli; Chiara Azzari; Andrea Finocchi; Caterina Cancrini; Gigliola Di Matteo; Gianni Russo; Massimo Alfano; Arianna Lesma; Andrea Salonia; Stuart Adams; Claire Booth; Alessandro Aiuti
Journal:  J Clin Immunol       Date:  2020-04-19       Impact factor: 8.317

6.  Preclinical Optimization and Safety Studies of a New Lentiviral Gene Therapy for p47phox-Deficient Chronic Granulomatous Disease.

Authors:  Andrea Schejtman; Winston Vetharoy; Uimook Choi; Christine Rivat; Narda Theobald; Giuseppa Piras; Diego Leon-Rico; Karen Buckland; Elena Armenteros-Monterroso; Sara Benedetti; Michael T Ashworth; Michael Rothe; Axel Schambach; Hubert Bobby Gaspar; Elizabeth M Kang; Harry L Malech; Adrian J Thrasher; Giorgia Santilli
Journal:  Hum Gene Ther       Date:  2021-05-06       Impact factor: 5.695

7.  Hematopoietic Tumors in a Mouse Model of X-linked Chronic Granulomatous Disease after Lentiviral Vector-Mediated Gene Therapy.

Authors:  Raisa Jofra Hernández; Andrea Calabria; Francesca Sanvito; Fabiola De Mattia; Giada Farinelli; Serena Scala; Ilaria Visigalli; Nicola Carriglio; Maura De Simone; Michela Vezzoli; Francesca Cecere; Maddalena Migliavacca; Luca Basso-Ricci; Maryam Omrani; Fabrizio Benedicenti; Rossana Norata; Paola Maria Vittoria Rancoita; Clelia Di Serio; Paola Albertini; Patrizia Cristofori; Luigi Naldini; Bernhard Gentner; Eugenio Montini; Alessandro Aiuti; Alessandra Mortellaro
Journal:  Mol Ther       Date:  2020-09-23       Impact factor: 11.454

  7 in total

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