Margherita Paschini1,2, Carla F Kim1,2,3. 1. Stem Cell Program and Divisions of Hematology/Oncology and Pulmonary & Respiratory Diseases, Boston Children's Hospital, Boston, MA, USA. 2. Department of Genetics, Harvard Medical School, Boston, MA, USA. 3. Harvard Stem Cell Institute, Cambridge, MA, USA.
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