Literature DB >> 3037739

Successful therapy of Niemann-Pick disease by implantation of human amniotic membrane.

B Scaggiante, A Pineschi, M Sustersich, M Andolina, E Agosti, D Romeo.   

Abstract

In a patient with a lysosomal storage disorder, not involving the CNS, repeated implantations of human amniotic sheets have proved to provide a successful approach to enzyme replacement therapy. Implantation of pure epithelial cells, separated from the other cell types of the amnion, might markedly improve the procedure, avoiding some risks of host-versus-graft rejection.

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Year:  1987        PMID： 3037739     DOI： 10.1097/00007890-198707000-00014

Source DB:  PubMed          Journal:  Transplantation        ISSN： 0041-1337            Impact factor:   4.939


  22 in total

Review 1.  Enzyme-replacement therapy: problems and prospects.

Authors:  B Rademaker; J Raber
Journal:  Pharm Weekbl Sci       Date:  1989-10-20

Review 2.  Amnion-derived pluripotent/multipotent stem cells.

Authors:  Toshio Miki; Stephen C Strom
Journal:  Stem Cell Rev       Date:  2006       Impact factor: 5.739

3.  Placenta-derived stem cells: new hope for cell therapy?

Authors:  Marco Evangelista; Maddalena Soncini; Ornella Parolini
Journal:  Cytotechnology       Date:  2008-09-28       Impact factor: 2.058

4.  Retroviral-mediated transfer of the human acid sphingomyelinase cDNA: correction of the metabolic defect in cultured Niemann-Pick disease cells.

Authors:  M Suchi; T Dinur; R J Desnick; S Gatt; L Pereira; E Gilboa; E H Schuchman
Journal:  Proc Natl Acad Sci U S A       Date:  1992-04-15       Impact factor: 11.205

Review 5.  Types A and B Niemann-Pick disease.

Authors:  Edward H Schuchman; Robert J Desnick
Journal:  Mol Genet Metab       Date:  2016-12-16       Impact factor: 4.797

6.  miR-410 Inhibition Induces RPE Differentiation of Amniotic Epithelial Stem Cells via Overexpression of OTX2 and RPE65.

Authors:  Soon Won Choi; Jae-Jun Kim; Min-Soo Seo; Sang-Bum Park; Tae-Wook Kang; Jin Young Lee; Byung-Chul Lee; Insung Kang; Tae-Hoon Shin; Hyung-Sik Kim; Kyung-Rok Yu; Kyung-Sun Kang
Journal:  Stem Cell Rev Rep       Date:  2015-06       Impact factor: 5.739

Review 7.  Gene Therapy for the Treatment of Neurological Disorders: Metabolic Disorders.

Authors:  Dominic J Gessler; Guangping Gao
Journal:  Methods Mol Biol       Date:  2016

8.  Attempted enzyme replacement using human amnion membrane implantations in mucopolysaccharidoses.

Authors:  J Muenzer; E F Neufeld; G Constantopoulos; R C Caruso; M I Kaiser-Kupfer; A Pikus; J Danoff; R R Berry; H D McDonald; J N Thompson
Journal:  J Inherit Metab Dis       Date:  1992       Impact factor: 4.982

Review 9.  A Rational Strategy for the Use of Amniotic Epithelial Stem Cell Therapy for Liver Diseases.

Authors:  Toshio Miki
Journal:  Stem Cells Transl Med       Date:  2016-03-03       Impact factor: 6.940

10.  Placental stem cell correction of murine intermediate maple syrup urine disease.

Authors:  Kristen J Skvorak; Kenneth Dorko; Fabio Marongiu; Veysel Tahan; Marc C Hansel; Roberto Gramignoli; K Michael Gibson; Stephen C Strom
Journal:  Hepatology       Date:  2013-02-15       Impact factor: 17.425
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