Literature DB >> 30374182

Rare diseases: Repurposing ciclopirox.

Sarah Crunkhorn.   

Abstract

Entities:  

Year:  2018        PMID: 30374182     DOI: 10.1038/nrd.2018.189

Source DB:  PubMed          Journal:  Nat Rev Drug Discov        ISSN: 1474-1776            Impact factor:   84.694


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  1 in total

1.  Repurposing ciclopirox as a pharmacological chaperone in a model of congenital erythropoietic porphyria.

Authors:  Pedro Urquiza; Ana Laín; Arantza Sanz-Parra; Jorge Moreno; Ganeko Bernardo-Seisdedos; Pierre Dubus; Esperanza González; Virginia Gutiérrez-de-Juan; Sandra García; Hasier Eraña; Itxaso San Juan; Iratxe Macías; Fredj Ben Bdira; Paula Pluta; Gabriel Ortega; Julen Oyarzábal; Rosario González-Muñiz; Juan Rodríguez-Cuesta; Juan Anguita; Emilio Díez; Jean-Marc Blouin; Hubert de Verneuil; José M Mato; Emmanuel Richard; Juan M Falcón-Pérez; Joaquín Castilla; Oscar Millet
Journal:  Sci Transl Med       Date:  2018-09-19       Impact factor: 17.956

  1 in total

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