Literature DB >> 30363394

Genetic Dystonia-ataxia Syndromes: Clinical Spectrum, Diagnostic Approach, and Treatment Options.

Malco Rossi1, Bettina Balint2,3,4, Patricio Millar Vernetti1, Kailash P Bhatia2, Marcelo Merello1,5.   

Abstract

BACKGROUND: Dystonia and ataxia are manifestations of numerous disorders, and indeed, an ever-expanding spectrum of genes causing diseases that encompass dystonia and ataxia are discovered with the advances of genetic techniques. In recent years, a pathophysiological link between both clinical features and the role of the cerebellum in the genesis of dystonia, in some cases, has been proposed. In clinical practice, the genetic diagnosis of dystonia-ataxia syndromes is a major issue for genetic counseling, prognosis and, occasionally, specific treatment.
METHODS: For this pragmatic and educational review, we conducted a comprehensive and structured literature search in Pubmed, OMIM, and GeneReviews using the key words "dystonia" and "ataxia" to identify those genetic diseases that may combine dystonia with ataxia.
RESULTS: There are a plethora of genetic diseases causing dystonia and ataxia. We propose a series of clinico-radiological algorithms to guide their differential diagnosis depending on the age of onset, additional neurological or systemic features, and imaging findings. We suggest a sequential diagnostic approach to dystonia-ataxia syndromes. We briefly highlight the pathophysiological links between dystonia and ataxia and conclude with a review of specific treatment implications.
CONCLUSIONS: The clinical approach presented in this review is intended to improve the diagnostic success of clinicians when faced with patients with dystonia-ataxia syndromes.

Entities:  

Keywords:  ataxia; diagnosis; dystonia; genetics; movement disorders

Year:  2018        PMID: 30363394      PMCID: PMC6174447          DOI: 10.1002/mdc3.12635

Source DB:  PubMed          Journal:  Mov Disord Clin Pract        ISSN: 2330-1619


  77 in total

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3.  Deep brain stimulation in a dentatorubral-pallidoluyisian atrophy patient with myoclonic dystonia.

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4.  Childhood-onset ATP1A3-related conditions: Report of two new cases of phenotypic spectrum.

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Authors:  Keisuke Wakusawa; Kazuhiro Haginoya; Taro Kitamura; Noriko Togashi; Mamiko Ishitobi; Hiroyuki Yokoyama; Shuichi Higano; Akira Onuma; Takahiro Nara; Kazuie Iinuma
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6.  The role of cerebellum in patients with late onset cervical/segmental dystonia?--evidence from the clinic.

Authors:  A Batla; M C Sánchez; R Erro; C Ganos; M Stamelou; B Balint; F Brugger; E Antelmi; K P Bhatia
Journal:  Parkinsonism Relat Disord       Date:  2015-09-05       Impact factor: 4.891

7.  Long-term benefit to pallidal deep brain stimulation in a case of dystonia secondary to pantothenate kinase-associated neurodegeneration.

Authors:  Martin Krause; Wolfgang Fogel; Volker Tronnier; Sabine Pohle; Konstanze Hörtnagel; Ute Thyen; Jens Volkmann
Journal:  Mov Disord       Date:  2006-12       Impact factor: 10.338

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9.  Deep brain stimulation for tremor associated with underlying ataxia syndromes: a case series and discussion of issues.

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Journal:  Tremor Other Hyperkinet Mov (N Y)       Date:  2014-07-09

10.  IP3R1 deficiency in the cerebellum/brainstem causes basal ganglia-independent dystonia by triggering tonic Purkinje cell firings in mice.

Authors:  Chihiro Hisatsune; Hiroyuki Miyamoto; Moritoshi Hirono; Naohide Yamaguchi; Takeyuki Sugawara; Naoko Ogawa; Etsuko Ebisui; Toshio Ohshima; Masahisa Yamada; Takao K Hensch; Mitsuharu Hattori; Katsuhiko Mikoshiba
Journal:  Front Neural Circuits       Date:  2013-10-04       Impact factor: 3.492

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2.  Extending the Phenotypic Spectrum Associated with STUB1 Mutations: A Case of Dystonia.

Authors:  Diana A Olszewska; Justin A Kinsella
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Review 3.  Myoclonus-Ataxia Syndromes: A Diagnostic Approach.

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Journal:  Mov Disord Clin Pract       Date:  2020-11-03

4.  Functionally Relevant Maculopathy and Optic Atrophy in Spinocerebellar Ataxia Type 1.

Authors:  Frederike Cosima Oertel; Oliver Zeitz; Maria Rönnefarth; Charlotte Bereuter; Seyedamirhosein Motamedi; Hanna G Zimmermann; Joseph Kuchling; Anne Sophie Grosch; Sarah Doss; Andrew Browne; Friedemann Paul; Tanja Schmitz-Hübsch; Alexander U Brandt
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Review 6.  Challenges in Clinicogenetic Correlations: One Phenotype - Many Genes.

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Review 7.  Metals and Metal-Nanoparticles in Human Pathologies: From Exposure to Therapy.

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Review 8.  Emerging cellular themes in leukodystrophies.

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