Literature DB >> 30264190

[Biliary atresia and congenital cholestatic syndromes : Characteristics before, after and during transition].

N Junge1, J Dingemann2, C Petersen2, M P Manns3, N Richter4, J Klempnauer4, U Baumann5, A Schneider3.   

Abstract

BACKGROUND: A growing number of patients with biliary atresia and congenital cholestatic syndromes are reaching adulthood. These patients often have a number of typical medical features, including specific characteristics of liver transplantation medicine.
OBJECTIVE: What are the special features in the care of adults suffering from liver diseases with manifestation in childhood and adolescence, both before and after liver transplantation (LTX). How does the progression of individual diseases differ depending on age at manifestation? What are specific aspects following pediatric LTX? PATIENTS AND METHODS: Evaluation and discussion of existing guidelines and recommendations of the individual disciplines and professional societies as well as the current literature. Joint discussion of the recommendations between disciplines (gastroenterology, pediatric gastroenterology, surgery). Inclusion of center-specific experiences with transition from existing transition outpatient departments and training.
RESULTS: The recommendations are presented specifically for each disease. Special features in individual diseases after LTX are also discussed. Diagnosis-independent general treatment concepts for cholestasis and chronic liver disease are presented.
CONCLUSION: Patients with biliary atresia and congenital cholestatic syndromes have a life-long chronic liver disease with and without LTX and require specific medical care. The patients benefit from the pooling of expertise in the individual disciplines.

Entities:  

Keywords:  Alagille syndrome; Cholestasis, progressive familial intrahepatic; Cystic fibrosis; Liver transplantation; Transition to adult care

Mesh:

Year:  2018        PMID: 30264190     DOI: 10.1007/s00108-018-0506-2

Source DB:  PubMed          Journal:  Internist (Berl)        ISSN: 0020-9554            Impact factor:   0.743


  30 in total

1.  Differences in presentation and progression between severe FIC1 and BSEP deficiencies.

Authors:  Ludmila Pawlikowska; Sandra Strautnieks; Irena Jankowska; Piotr Czubkowski; Karan Emerick; Anthony Antoniou; Catherine Wanty; Bjorn Fischler; Emmanuel Jacquemin; Sami Wali; Samra Blanchard; Inge-Merete Nielsen; Billy Bourke; Shirley McQuaid; Florence Lacaille; Jane A Byrne; Albertien M van Eerde; Kaija-Leena Kolho; Leo Klomp; Roderick Houwen; Peter Bacchetti; Steven Lobritto; Vera Hupertz; Patricia McClean; Giorgina Mieli-Vergani; Benjamin Shneider; Antal Nemeth; Etienne Sokal; Nelson B Freimer; A S Knisely; Philip Rosenthal; Peter F Whitington; Joanna Pawlowska; Richard J Thompson; Laura N Bull
Journal:  J Hepatol       Date:  2010-04-13       Impact factor: 25.083

2.  Chronic cholestasis and dyslipidemia: what is the cardiovascular risk?

Authors:  Dennis D Black
Journal:  J Pediatr       Date:  2005-03       Impact factor: 4.406

3.  Evaluation of risk for atherosclerosis in Alagille syndrome and progressive familial intrahepatic cholestasis: two congenital cholestatic diseases with different lipoprotein metabolisms.

Authors:  Hironori Nagasaka; Tohru Yorifuji; Hiroto Egawa; Hidekatsu Yanai; Tomoo Fujisawa; Kiyotaka Kosugiyama; Akira Matsui; Makoto Hasegawa; Tomoo Okada; Masaki Takayanagi; Hitoshi Chiba; Kunihiko Kobayashi
Journal:  J Pediatr       Date:  2005-03       Impact factor: 4.406

4.  Recovery of graft steatosis and protein-losing enteropathy after biliary diversion in a PFIC 1 liver transplanted child.

Authors:  Emanuele Nicastro; Xavier Stephenne; Françoise Smets; Fabio Fusaro; Catherine de Magnée; Raymond Reding; Etienne M Sokal
Journal:  Pediatr Transplant       Date:  2011-06-15

5.  Mutations in TJP2 cause progressive cholestatic liver disease.

Authors:  Melissa Sambrotta; Sandra Strautnieks; Efterpi Papouli; Peter Rushton; Barnaby E Clark; David A Parry; Clare V Logan; Lucy J Newbury; Binita M Kamath; Simon Ling; Tassos Grammatikopoulos; Bart E Wagner; John C Magee; Ronald J Sokol; Giorgina Mieli-Vergani; Joshua D Smith; Colin A Johnson; Patricia McClean; Michael A Simpson; A S Knisely; Laura N Bull; Richard J Thompson
Journal:  Nat Genet       Date:  2014-03-09       Impact factor: 38.330

6.  MYO5B mutations cause cholestasis with normal serum gamma-glutamyl transferase activity in children without microvillous inclusion disease.

Authors:  Emmanuel Gonzales; Sarah A Taylor; Anne Davit-Spraul; Alice Thébaut; Nadège Thomassin; Catherine Guettier; Peter F Whitington; Emmanuel Jacquemin
Journal:  Hepatology       Date:  2016-10-05       Impact factor: 17.425

7.  Current status of 21 patients who have survived more than 20 years since undergoing surgery for biliary atresia.

Authors:  M Nio; R Ohi; Y Hayashi; N Endo; M Ibrahim; D Iwami
Journal:  J Pediatr Surg       Date:  1996-03       Impact factor: 2.545

8.  Management of cholestatic pruritus in paediatric patients with alagille syndrome: the King's College Hospital experience.

Authors:  Victoria Kronsten; Emer Fitzpatrick; Alastair Baker
Journal:  J Pediatr Gastroenterol Nutr       Date:  2013-08       Impact factor: 2.839

9.  Russell Strong and the history of reduced-size liver transplantation.

Authors:  Guiseppe Garcea; Hajir Nabi; Guy J Maddern
Journal:  World J Surg       Date:  2009-08       Impact factor: 3.352

10.  Mutations in the nuclear bile acid receptor FXR cause progressive familial intrahepatic cholestasis.

Authors:  Natalia Gomez-Ospina; Carol J Potter; Rui Xiao; Kandamurugu Manickam; Mi-Sun Kim; Kang Ho Kim; Benjamin L Shneider; Jennifer L Picarsic; Theodora A Jacobson; Jing Zhang; Weimin He; Pengfei Liu; A S Knisely; Milton J Finegold; Donna M Muzny; Eric Boerwinkle; James R Lupski; Sharon E Plon; Richard A Gibbs; Christine M Eng; Yaping Yang; Gabriel C Washington; Matthew H Porteus; William E Berquist; Neeraja Kambham; Ravinder J Singh; Fan Xia; Gregory M Enns; David D Moore
Journal:  Nat Commun       Date:  2016-02-18       Impact factor: 14.919

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  1 in total

Review 1.  Need for transition medicine in pediatric surgery - health related quality of life in adolescents and young adults with congenital malformations.

Authors:  Marie Uecker; Benno Ure; Julia Hannah Quitmann; Jens Dingemann
Journal:  Innov Surg Sci       Date:  2022-01-07
  1 in total

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