Literature DB >> 30158561

A potential biomarker strategy to monitor treatment response in spinal muscular atrophy.

Heather Wood1.   

Abstract

Entities:  

Year:  2018        PMID： 30158561     DOI： 10.1038/s41582-018-0068-x

Source DB:  PubMed          Journal:  Nat Rev Neurol        ISSN： 1759-4758            Impact factor:   42.937


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  3 in total

1.  Systemic nanoparticle delivery of CRISPR-Cas9 ribonucleoproteins for effective tissue specific genome editing.

Authors:  Tuo Wei; Qiang Cheng; Yi-Li Min; Eric N Olson; Daniel J Siegwart
Journal:  Nat Commun       Date:  2020-06-26       Impact factor: 14.919

Review 2.  Therapeutic siRNA: State-of-the-Art and Future Perspectives.

Authors:  Maik Friedrich; Achim Aigner
Journal:  BioDrugs       Date:  2022-08-23       Impact factor: 7.744

3.  Naturally-occurring cholesterol analogues in lipid nanoparticles induce polymorphic shape and enhance intracellular delivery of mRNA.

Authors:  Siddharth Patel; N Ashwanikumar; Ema Robinson; Yan Xia; Cosmin Mihai; Joseph P Griffith; Shangguo Hou; Adam A Esposito; Tatiana Ketova; Kevin Welsher; John L Joyal; Örn Almarsson; Gaurav Sahay
Journal:  Nat Commun       Date:  2020-02-20       Impact factor: 14.919
  3 in total

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