Literature DB >> 30078822

Clinical Manifestations and Long-Term Mortality in Lamin A/C Mutation Carriers From a Japanese Multicenter Registry.

Kenzaburo Nakajima1,2, Takeshi Aiba1,3, Takeru Makiyama4, Suguru Nishiuchi4, Seiko Ohno5, Koichi Kato5, Yuta Yamamoto4, Takahiro Doi4, Satoshi Shizuta4, Kenji Onoue6, Nobue Yagihara7, Taisuke Ishikawa8, Ichiro Watanabe9, Hiroshi Kawakami10, Yasushi Oginosawa11, Nobuyuki Murakoshi12, Akihiko Nogami12, Kazutaka Aonuma12, Yoshihiko Saito6, Takeshi Kimura4, Satoshi Yasuda1,2, Naomasa Makita8, Wataru Shimizu13, Minoru Horie5, Kengo Kusano1,2.   

Abstract

BACKGROUND: Mutation in the lamin A/C gene (LMNA) is associated with several cardiac phenotypes, such as cardiac conduction disorders (CCD), atrial arrhythmia (AA), malignant ventricular arrhythmia (MVA) and left ventricular dysfunction (LVD), leading to sudden cardiac death (SCD) and/or end-stage heart failure. We investigated how these phenotypes are associated with each other and which of them are most important for total mortality. Methods and 
Results: A multicenter registry included 110 LMNA mutation carriers (age, 43±15 years, male: 62%) from 60 families. After genetic diagnosis of LMNA mutation (missense: 27%, non-missense: 73%), patients or subjects were followed to evaluate the manifestations of their phenotypes and the risk of total mortality; 90 patients could be followed (median: 5 [0-35] years). Prevalence of the 4 clinical phenotypes was significantly increased during follow-up. Among these phenotypes, AA was significantly associated with MVA. CCD was significantly associated with LVD. LVD, meanwhile, was significantly associated with CCD and MVA. Male sex was significantly associated with MVA. Furthermore, during follow-up, 17 patients died: 12 end-stage heart failure, 4 SCD and 1 stroke. LVD was the only independent predictor for all-cause death (OR: 41.7, 95% CI: 4.1-422.3; P=0.0016).
CONCLUSIONS: Several cardiac phenotypes were age-dependently increased in LMNA mutation carriers, suggesting that ICD or CRT-D could suppress SCD after middle age; however, LVD leading to end-stage heart failure was the only independent predictor for total mortality.

Entities:  

Keywords:  Arrhythmias; Heart failure; Lamin A/C; Phenotypes; Prognosis

Mesh:

Substances:

Year:  2018        PMID: 30078822     DOI: 10.1253/circj.CJ-18-0339

Source DB:  PubMed          Journal:  Circ J        ISSN: 1346-9843            Impact factor:   2.993


  8 in total

1.  European Heart Rhythm Association (EHRA)/Heart Rhythm Society (HRS)/Asia Pacific Heart Rhythm Society (APHRS)/Latin American Heart Rhythm Society (LAHRS) Expert Consensus Statement on the state of genetic testing for cardiac diseases.

Authors:  Arthur A M Wilde; Christopher Semsarian; Manlio F Márquez; Alireza Sepehri Shamloo; Michael J Ackerman; Euan A Ashley; Back Sternick Eduardo; Héctor Barajas-Martinez; Elijah R Behr; Connie R Bezzina; Jeroen Breckpot; Philippe Charron; Priya Chockalingam; Lia Crotti; Michael H Gollob; Steven Lubitz; Naomasa Makita; Seiko Ohno; Martín Ortiz-Genga; Luciana Sacilotto; Eric Schulze-Bahr; Wataru Shimizu; Nona Sotoodehnia; Rafik Tadros; James S Ware; David S Winlaw; Elizabeth S Kaufman; Takeshi Aiba; Andreas Bollmann; Jong-Il Choi; Aarti Dalal; Francisco Darrieux; John Giudicessi; Mariana Guerchicoff; Kui Hong; Andrew D Krahn; Ciorsti Mac Intyre; Judith A Mackall; Lluís Mont; Carlo Napolitano; Pablo Ochoa Juan; Petr Peichl; Alexandre C Pereira; Peter J Schwartz; Jon Skinner; Christoph Stellbrink; Jacob Tfelt-Hansen; Thomas Deneke
Journal:  J Arrhythm       Date:  2022-05-31

2.  European Heart Rhythm Association (EHRA)/Heart Rhythm Society (HRS)/Asia Pacific Heart Rhythm Society (APHRS)/Latin American Heart Rhythm Society (LAHRS) Expert Consensus Statement on the state of genetic testing for cardiac diseases.

Authors:  Arthur A M Wilde; Christopher Semsarian; Manlio F Márquez; Alireza Sepehri Shamloo; Michael J Ackerman; Euan A Ashley; Eduardo Back Sternick; Héctor Barajas-Martinez; Elijah R Behr; Connie R Bezzina; Jeroen Breckpot; Philippe Charron; Priya Chockalingam; Lia Crotti; Michael H Gollob; Steven Lubitz; Naomasa Makita; Seiko Ohno; Martín Ortiz-Genga; Luciana Sacilotto; Eric Schulze-Bahr; Wataru Shimizu; Nona Sotoodehnia; Rafik Tadros; James S Ware; David S Winlaw; Elizabeth S Kaufman; Takeshi Aiba; Andreas Bollmann; Jong Il Choi; Aarti Dalal; Francisco Darrieux; John Giudicessi; Mariana Guerchicoff; Kui Hong; Andrew D Krahn; Ciorsti MacIntyre; Judith A Mackall; Lluís Mont; Carlo Napolitano; Juan Pablo Ochoa; Petr Peichl; Alexandre C Pereira; Peter J Schwartz; Jon Skinner; Christoph Stellbrink; Jacob Tfelt-Hansen; Thomas Deneke
Journal:  Europace       Date:  2022-09-01       Impact factor: 5.486

3.  Refractory Right Ventricular Failure in a Patient with Emery-Dreifuss Muscular Dystrophy.

Authors:  Yasuyuki Chiba; Arata Fukushima; Motoki Nakao; Yuta Kobayashi; Takahiro Ishigaki; Taro Tenma; Kiwamu Kamiya; Yasushige Shingu; Tomonori Ooka; Yoshiro Matsui; Toshihisa Anzai
Journal:  Intern Med       Date:  2020-02-19       Impact factor: 1.271

4.  Can Circulating Cardiac Biomarkers Be Helpful in the Assessment of LMNA Mutation Carriers?

Authors:  Przemyslaw Chmielewski; Ewa Michalak; Ilona Kowalik; Maria Franaszczyk; Malgorzata Sobieszczanska-Malek; Grazyna Truszkowska; Malgorzata Stepien-Wojno; Elzbieta Katarzyna Biernacka; Bogna Foss-Nieradko; Michal Lewandowski; Artur Oreziak; Maria Bilinska; Mariusz Kusmierczyk; Frédérique Tesson; Jacek Grzybowski; Tomasz Zielinski; Rafal Ploski; Zofia T Bilinska
Journal:  J Clin Med       Date:  2020-05-12       Impact factor: 4.241

5.  Case reports of a c.475G>T, p.E159* lamin A/C mutation with a family history of conduction disorder, dilated cardiomyopathy and sudden cardiac death.

Authors:  Tetsuro Yokokawa; Shohei Ichimura; Naoko Hijioka; Takashi Kaneshiro; Akiomi Yoshihisa; Hiroyuki Kunii; Kazuhiko Nakazato; Takafumi Ishida; Osamu Suzuki; Seiko Ohno; Takeshi Aiba; Hiroshi Ohtani; Yasuchika Takeishi
Journal:  BMC Cardiovasc Disord       Date:  2019-12-17       Impact factor: 2.298

Review 6.  Clinical Profile, Arrhythmias, and Adverse Cardiac Outcomes in Emery-Dreifuss Muscular Dystrophies: A Systematic Review of the Literature.

Authors:  Anna Chiara Valenti; Alessandro Albini; Jacopo Francesco Imberti; Marco Vitolo; Niccolò Bonini; Giovanna Lattanzi; Renate B Schnabel; Giuseppe Boriani
Journal:  Biology (Basel)       Date:  2022-03-30

7.  Looking at New Unexpected Disease Targets in LMNA-Linked Lipodystrophies in the Light of Complex Cardiovascular Phenotypes: Implications for Clinical Practice.

Authors:  Héléna Mosbah; Camille Vatier; Franck Boccara; Isabelle Jéru; Olivier Lascols; Marie-Christine Vantyghem; Bruno Fève; Bruno Donadille; Elisabeth Sarrazin; Sophie Benabbou; Jocelyn Inamo; Stéphane Ederhy; Ariel Cohen; Barbara Neraud; Pascale Richard; Fabien Picard; Sophie Christin-Maitre; Alban Redheuil; Karim Wahbi; Corinne Vigouroux
Journal:  Cells       Date:  2020-03-20       Impact factor: 6.600

8.  Titin-Related Dilated Cardiomyopathy: The Clinical Trajectory and the Role of Circulating Biomarkers in the Clinical Assessment.

Authors:  Przemysław Chmielewski; Grażyna Truszkowska; Ilona Kowalik; Małgorzata Rydzanicz; Ewa Michalak; Małgorzata Sobieszczańska-Małek; Maria Franaszczyk; Piotr Stawiński; Małgorzata Stępień-Wojno; Artur Oręziak; Michał Lewandowski; Przemysław Leszek; Maria Bilińska; Tomasz Zieliński; Rafał Płoski; Zofia T Bilińska
Journal:  Diagnostics (Basel)       Date:  2021-12-22
  8 in total

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