Literature DB >> 29855125

The Jamaican Haemophilia Registry: Describing the burden of disease.

G Wharfe1, L Buchner-Daley1, T Gibson1, P Hilliard2, K Usuba3,4, A Abad3, L Boma-Fischer5, V Bouskill6, G Floros5, D Lillicrap7, Y Lowe1, D Lowe1, N Palmer-Mitchell1, M L Rand8,9,10, J Teitel5, A Tuttle7, A Watson1, R White1, N L Young3,4, V S Blanchette3,10,11.   

Abstract

INTRODUCTION: Jamaica has an estimated 200 persons with haemophilia (PWH), who face significant constraints in access to specialized haemophilia care, including access to clotting factor concentrates. AIM: The aim of this paper is to establish the current burden of disease in PWH in Jamaica.
METHODS: PWH were enrolled through the University Hospital of the West Indies, Jamaica. The impact of haemophilia was assessed using a comprehensive battery of heath outcome measures that included the following: laboratory, clinical information and validated outcome measures of joint structure and function, activity, and health-related quality of life (HRQoL) to provide a health profile of the Jamaican haemophilia population.
RESULTS: In all, 45 PWH were registered (mean age: 29, range: 0.17-69 years), including 13 children (<18 years of age) and 32 adults. In this sample, 41 had haemophilia A (30 severe) and 4 had haemophilia B (3 severe); 10 patients with haemophilia A were inhibitor positive. The results indicate that adults with haemophilia in Jamaica have significant joint damage: mean Haemophilia Joint Health Score (HJHS) = 42.1 (SD = 17.3); moderate activity levels - mean Haemophilia Activities List (HAL) score = 64.8 (SD = 17.8); and low HRQoL scores - mean Haemo-QoL-A score = 62.3 (SD = 19.4). Results for children are also reported but should be interpreted with caution due to the small sample size.
CONCLUSIONS: There is a very high burden of disease in PWH in Jamaica. The health profiles reported in this paper are an essential first step in advocating for a multidisciplinary Comprehensive Care Program for assessment and care of PWH in Jamaica.
© 2018 John Wiley & Sons Ltd.

Entities:  

Keywords:  Jamaica; burden of disease; haemophilia; health assessment; outcome measures; registry

Mesh:

Year:  2018        PMID: 29855125     DOI: 10.1111/hae.13517

Source DB:  PubMed          Journal:  Haemophilia        ISSN: 1351-8216            Impact factor:   4.287


  5 in total

1.  Psychometric Validation of the Haemo-QOL-A in Participants with Hemophilia A Treated with Gene Therapy.

Authors:  Jennifer Quinn; Kathleen A Delaney; Wing Yen Wong; Wolfgang Miesbach; Monika Bullinger
Journal:  Patient Relat Outcome Meas       Date:  2022-07-18

2.  Persistence of haemostatic response following gene therapy with valoctocogene roxaparvovec in severe haemophilia A.

Authors:  K John Pasi; Michael Laffan; Savita Rangarajan; Tara M Robinson; Nina Mitchell; Will Lester; Emily Symington; Bella Madan; Xinqun Yang; Benjamin Kim; Glenn F Pierce; Wing Yen Wong
Journal:  Haemophilia       Date:  2021-08-11       Impact factor: 4.263

3.  Patient-relevant health outcomes for hemophilia care: Development of an international standard outcomes set.

Authors:  Erna C van Balen; Brian O'Mahony; Marjon H Cnossen; Gerard Dolan; Victor S Blanchette; Kathelijn Fischer; Deborah Gue; Jamie O'Hara; Alfonso Iorio; Shannon Jackson; Barbara A Konkle; Diane J Nugent; Donna Coffin; Mark W Skinner; Cees Smit; Alok Srivastava; Fred van Eenennaam; Johanna G van der Bom; Samantha C Gouw
Journal:  Res Pract Thromb Haemost       Date:  2021-03-06

4.  Impact of prophylaxis on health-related quality of life of boys with hemophilia: An analysis of pooled data from 9 countries.

Authors:  Koyo Usuba; Victoria E Price; Victor Blanchette; Audrey Abad; Carmen Altisent; Loretta Buchner-Daley; Jorge D A Carneiro; Brian M Feldman; Kathelijn Fischer; John Grainger; Susanne Holzhauer; Koon-Hung Luke; Sandrine Meunier; Margareth Ozelo; Ling Tang; Sandra V Antunes; Paula Villaça; Cindy Wakefield; Gilian Wharfe; Runhui Wu; Nancy L Young
Journal:  Res Pract Thromb Haemost       Date:  2019-04-23

5.  Shortening the Haemophilia Activities List (HAL) from 42 items to 18 items.

Authors:  Isolde A R Kuijlaars; Janjaap van der Net; Tyler W Buckner; Christine L Kempton; Roger E G Schutgens; Kathelijn Fischer
Journal:  Haemophilia       Date:  2021-09-08       Impact factor: 4.263

  5 in total

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