Literature DB >> 29723417

Discontinuation of tyrosine kinase inhibitors in chronic myeloid leukemia: Recommendations for clinical practice from the French Chronic Myeloid Leukemia Study Group.

Delphine Rea1, Shanti Ame1, Marc Berger1, Jean-Michel Cayuela1, Aude Charbonnier1, Valérie Coiteux1, Pascale Cony-Makhoul1, Viviane Dubruille1, Stéphanie Dulucq1, Gabriel Etienne1, Laurence Legros1, Franck Nicolini1, Catherine Roche-Lestienne1, Martine Escoffre-Barbe1, Martine Gardembas1, Agnès Guerci-Bresler1, Hyacinthe Johnson-Ansah1, Françoise Rigal-Huguet1, Philippe Rousselot1, François-Xavier Mahon1.   

Abstract

BACKGROUND: The ultimate goal of chronic myeloid leukemia management in the tyrosine kinase inhibitor (TKI) era for patients who obtain deep molecular responses is maintaining a durable off-treatment response after treatment discontinuation; this situation is called treatment-free remission (TFR). Knowledge accumulated during the last 10 years justifies moving TFR strategies from research to clinical practice.
METHODS: Twenty experts from the French Chronic Myeloid Leukemia Study Group (France Intergroupe des Leucémies Myéloïdes Chroniques), including 17 hematologists, 2 molecular biologists, and 1 cytogeneticist, critically reviewed published data with the goal of developing evidence-based recommendations for TKI discontinuation in clinical practice.
RESULTS: Clinically relevant questions were addressed, including the selection of candidate patients (with known prognostic factors for outcomes taken into account), detailed monitoring procedures during the treatment-free phase, a definition of relapse requiring therapy resumption, and monitoring after treatment reintroduction.
CONCLUSIONS: This work presents consensus statements with the aim of guiding physicians and biologists by means of pragmatic recommendations for safe TKI discontinuation in daily practice. Cancer 2018;124:2956-63.
© 2018 American Cancer Society. © 2018 American Cancer Society.

Entities:  

Keywords:  chronic myeloid leukemia; clinical practice; recommendations; treatment discontinuation; tyrosine kinase inhibitors

Mesh:

Substances:

Year:  2018        PMID: 29723417     DOI: 10.1002/cncr.31411

Source DB:  PubMed          Journal:  Cancer        ISSN: 0008-543X            Impact factor:   6.860


  22 in total

1.  Health state utility and quality of life measures in patients with chronic myeloid leukemia in France.

Authors:  Foulon S; Cony-Makhoul P; Guerci-Bresler A; Daban M; Kapso R; Tubert-Bitter P; Bonastre J
Journal:  Qual Life Res       Date:  2021-03-02       Impact factor: 4.147

2.  TKI discontinuation in CML: how do we make more patients eligible? How do we increase the chances of a successful treatment-free remission?

Authors:  Andreas Hochhaus; Thomas Ernst
Journal:  Hematology Am Soc Hematol Educ Program       Date:  2021-12-10

3.  Impact of the treatment of chronic myeloid leukaemia by tyrosine-kinase inhibitors on sick leaves refund: a nationwide cohort study.

Authors:  Cécile Conte; Flora Vayr; Marie-Christelle Pajiep; Fabien Despas; Françoise Huguet; Maryse Lapeyre Mestre; Martin Gauthier; Fabrice Herin
Journal:  Support Care Cancer       Date:  2022-03-18       Impact factor: 3.603

4.  Real-world therapeutic response and tyrosine kinase inhibitor discontinuation in chronic phase-chronic myeloid leukemia: data from the French observatory.

Authors:  Sandrine Saugues; Céline Lambert; Elisabeth Daguenet; Hyacinthe Johnson Ansah; Ali Turhan; Françoise Huguet; Agnès Guerci-Bresler; Andreï Tchirkov; Dalil Hamroun; Eric Hermet; Bruno Pereira; Marc G Berger
Journal:  Ann Hematol       Date:  2022-08-30       Impact factor: 4.030

Review 5.  Pharmacology of tyrosine kinase inhibitors in chronic myeloid leukemia; a clinician's perspective.

Authors:  Deepam Pushpam; Sameer Bakhshi
Journal:  Daru       Date:  2020-01-03       Impact factor: 3.117

6.  Managing chronic myeloid leukemia for treatment-free remission: a proposal from the GIMEMA CML WP.

Authors:  Michele Baccarani; Elisabetta Abruzzese; Vincenzo Accurso; Francesco Albano; Mario Annunziata; Sara Barulli; Germana Beltrami; Micaela Bergamaschi; Gianni Binotto; Monica Bocchia; Giovanni Caocci; Isabella Capodanno; Francesco Cavazzini; Michele Cedrone; Marco Cerrano; Monica Crugnola; Mariella D'Adda; Chiara Elena; Carmen Fava; Paola Fazi; Claudio Fozza; Sara Galimberti; Valentina Giai; Antonella Gozzini; Gabriele Gugliotta; Alessandra Iurlo; Gaetano La Barba; Luciano Levato; Alessandro Lucchesi; Luigia Luciano; Francesca Lunghi; Monia Lunghi; Michele Malagola; Roberto Marasca; Bruno Martino; Angela Melpignano; Maria Cristina Miggiano; Enrico Montefusco; Caterina Musolino; Fausto Palmieri; Patrizia Pregno; Davide Rapezzi; Giovanna Rege-Cambrin; Serena Rupoli; Marzia Salvucci; Rosaria Sancetta; Simona Sica; Raffaele Spadano; Fabio Stagno; Mario Tiribelli; Simona Tomassetti; Elena Trabacchi; Massimiliano Bonifacio; Massimo Breccia; Fausto Castagnetti; Fabrizio Pane; Domenico Russo; Giuseppe Saglio; Simona Soverini; Paolo Vigneri; Gianantonio Rosti
Journal:  Blood Adv       Date:  2019-12-23

7.  Comparison of the clinical outcomes of nilotinib and dasatinib therapies in newly diagnosed patients in the chronic phase of chronic myeloid leukemia: a retrospective analysis.

Authors:  Noriyoshi Iriyama; Kei-Ji Sugimoto; Eriko Sato; Tomoiku Takaku; Michihide Tokuhira; Tomonori Nakazato; Maho Ishikawa; Hiroyuki Fujita; Isao Fujioka; Yuta Kimura; Norio Asou; Masahiro Kizaki; Norio Komatsu; Yoshihiro Hatta; Tatsuya Kawaguchi
Journal:  Med Oncol       Date:  2018-09-07       Impact factor: 3.064

8.  Relevance of treatment-free remission recommendations in chronic phase chronic leukemia patients treated with frontline tyrosine kinase inhibitors.

Authors:  Gabriel Etienne; Carole Faberes; Fréderic Bauduer; Didier Adiko; François Lifermann; Corinne Dagada; Caroline Lenoir; Anna Schmitt; Emilie Klein; Marie-Pierre Fort; Fontanet Bijou; Beatrice Turcq; Fanny Robbesyn; Françoise Durrieu; Laura Versmée; Samia Madene; Marius Moldovan; Sandrine Katsahian; Anais Charles-Nelson; Axelle Lascaux; François-Xavier Mahon; Stéphanie Dulucq
Journal:  Cancer Med       Date:  2021-05-14       Impact factor: 4.452

9.  Discontinuation of tyrosine kinase inhibitor in chronic myeloid leukemia: a retrospective cohort in east occitania.

Authors:  J B Robin; A Theron; P Quittet; C Exbrayat; J B Gaillard; T Lavabre-Bertrand; S David; A Saad; E Jourdan; G Cartron
Journal:  Ann Hematol       Date:  2022-03-12       Impact factor: 3.673

10.  Accelerated Phase Chronic Myeloid Leukemia and Treatment Free Remission Maintained After Five Years of Nilotinib: A Case Report.

Authors:  Isabella Capodanno; Elisabetta Lugli; Katia Codeluppi; Mariapina Faruolo; Enrica Bellesia; Riccardo Valli; Francesco Merli
Journal:  Front Oncol       Date:  2021-06-11       Impact factor: 6.244

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