Eduardo F Tizzano1. Show Affiliations » 1. Área de Genética Clínica y Molecular-Unidad Funcional de Enfermedades Raras, Grupo de Medicina Genética VHIR, CIBERER, Hospital Universitario Vall d'Hebron, Barcelona, España. Electronic address: etizzano@vhebron.net.
Abstract
Entities: Disease
Mesh: See more » ChildChild, PreschoolHumansInfantMuscular Atrophy, Spinal/drug therapyRare Diseases/drug therapy
Year: 2018 PMID: 29685310 DOI: 10.1016/j.medcli.2018.03.001
Source DB: PubMed Journal: Med Clin (Barc) ISSN: 0025-7753 Impact factor: 1.725