Literature DB >> 29673809

A 5-center experience with intrathecal administration of nusinersen in SMA1 in Italy letter to the editor of european journal of pediatric neurology regarding the manuscript "single-center experience with intrathecal administration of nusinersen in children with spinal muscular atrophy type 1" written by pechmann and colleagues".

V A Sansone1, M Pane2, S Messina3, C Bruno4, A D'Amico5, E Albamonte6, M Catteruccia5, M Sframeli3, M Pedemonte4, G Vita3, E Bertini5, E Mercuri2.   

Abstract

Entities:  

Mesh:

Substances:

Year:  2018        PMID: 29673809     DOI: 10.1016/j.ejpn.2018.02.004

Source DB:  PubMed          Journal:  Eur J Paediatr Neurol        ISSN: 1090-3798            Impact factor:   3.140


× No keyword cloud information.
  2 in total

1.  Intrathecal administration of Nusinersen in type 1 SMA: successful psychological program in a single Italian center.

Authors:  Stefania La Foresta; Cristina Faraone; Maria Sframeli; Gian Luca Vita; Massimo Russo; Claudia Profazio; Immacolata Rulli; Eloisa Gitto; Antonio Versaci; Sonia Messina; Giuseppe Vita
Journal:  Neurol Sci       Date:  2018-07-25       Impact factor: 3.307

2.  The Italian neuromuscular registry: a coordinated platform where patient organizations and clinicians collaborate for data collection and multiple usage.

Authors:  Anna Ambrosini; Daniela Calabrese; Francesco Maria Avato; Felice Catania; Guido Cavaletti; Maria Carmela Pera; Antonio Toscano; Giuseppe Vita; Lucia Monaco; Davide Pareyson
Journal:  Orphanet J Rare Dis       Date:  2018-10-04       Impact factor: 4.123

  2 in total

北京卡尤迪生物科技股份有限公司 © 2022-2023.