Literature DB >> 29544888

Clinical phenotype of hereditary spastic paraplegia due to KIF1C gene mutations across life span.

Didem Yücel-Yılmaz1, Emrah Yücesan2, Dilek Yalnızoğlu3, Kader Karlı Oğuz4, Mahmut Şamil Sağıroğlu5, Uğur Özbek2, Esra Serdaroğlu3, Başar Bilgiç6, Sevim Erdem7, Sibel Aylin Uğur İşeri2, Haşmet Hanağası6, Hakan Gürvit6, Rıza Köksal Özgül1, Ali Dursun8.   

Abstract

Hereditary spastic paraplegias (HSPs) are a group of genetic disorders resulting in pyramidal tract impairment, predominantly in lower limbs. KIF1C gene has recently been identified as one of the genetic causes of HSP and associated with pure or complicated HSP. We present three patients with complicated HSP from two unrelated families, who had early onset progressive cerebellar signs and developed pyramidal tract signs during follow-up. Whole exome sequencing in these patients followed by segregation analysis identified novel truncating KIF1C mutations (c.463C> T; p.R155∗ and c.2478delA; p.Ala828Argfs∗13). Neuroimaging findings showed cerebral and upper cervical spinal atrophy, bilateral symmetrical pyramidal tract involvement, and focal cerebral white matter lesions. Patients with KIF1C mutations may present with cerebellar signs and pyramidal findings may emerge later, therefore complicated HSP should be considered in the differential diagnosis of unidentified cases with cerebellar dysfunction.
Copyright © 2018 The Japanese Society of Child Neurology. Published by Elsevier B.V. All rights reserved.

Entities:  

Keywords:  Ataxia; Hereditary spastic paraplegia; KIF1C; Kinesin

Mesh:

Substances:

Year:  2018        PMID: 29544888     DOI: 10.1016/j.braindev.2018.02.013

Source DB:  PubMed          Journal:  Brain Dev        ISSN: 0387-7604            Impact factor:   1.961


  4 in total

1.  Progressive ataxia of Charolais cattle highlights a role of KIF1C in sustainable myelination.

Authors:  Amandine Duchesne; Anne Vaiman; Magali Frah; Sandrine Floriot; Sabrina Legoueix-Rodriguez; Anne Desmazières; Sébastien Fritz; Christian Beauvallet; Olivier Albaric; Eric Venot; Maud Bertaud; Romain Saintilan; Raphaël Guatteo; Diane Esquerré; Julien Branchu; Anaïs Fleming; Alexis Brice; Frédéric Darios; Jean-Luc Vilotte; Giovanni Stevanin; Didier Boichard; Khalid Hamid El Hachimi
Journal:  PLoS Genet       Date:  2018-08-01       Impact factor: 5.917

2.  KIF1C Variants Are Associated with Hypomyelination, Ataxia, Tremor, and Dystonia in Fraternal Twins.

Authors:  Enrica Marchionni; Aurélie Méneret; Boris Keren; Judith Melki; Christian Denier; Alexandra Durr; Emmanuelle Apartis; Odile Boespflug-Tanguy; Fanny Mochel
Journal:  Tremor Other Hyperkinet Mov (N Y)       Date:  2019-07-17

Review 3.  Going Too Far Is the Same as Falling Short: Kinesin-3 Family Members in Hereditary Spastic Paraplegia.

Authors:  Dominik R Gabrych; Victor Z Lau; Shinsuke Niwa; Michael A Silverman
Journal:  Front Cell Neurosci       Date:  2019-09-26       Impact factor: 5.505

Review 4.  The Classification of Autosomal Recessive Cerebellar Ataxias: a Consensus Statement from the Society for Research on the Cerebellum and Ataxias Task Force.

Authors:  Marie Beaudin; Antoni Matilla-Dueñas; Bing-Weng Soong; Jose Luiz Pedroso; Orlando G Barsottini; Hiroshi Mitoma; Shoji Tsuji; Jeremy D Schmahmann; Mario Manto; Guy A Rouleau; Christopher Klein; Nicolas Dupre
Journal:  Cerebellum       Date:  2019-12       Impact factor: 3.847

  4 in total

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