Literature DB >> 29511948

Current Information and Recommendations on the Discontinuation of TKI Inhibitors in Chronic Myeloid Leukemia.

Massimo Breccia1, Robin Foà2.   

Abstract

PURPOSE OF REVIEW: Discontinuation of tyrosine kinase inhibitors (TKIs) in chronic phase chronic myeloid leukemia (CP-CML) patients has become a reality. Treatment-free remission (TFR) is the term that identifies success after discontinuation. RECENT
FINDINGS: Several trials have demonstrated that with imatinib about 40% of patients discontinuing treatment in deep and stable molecular response remain disease-free. Second-generation TKIs have improved the rate of deep molecular responses and allowed to increase the percentage of patients attempting treatment discontinuation. We hereby review the current information based on the available published data and discuss the current suggestions on how to move TFR into the clinical practice.

Entities:  

Keywords:  Chronic myeloid leukemia; Discontinuation; Treatment-free remission; Tyrosine kinase inhibitors

Mesh:

Substances:

Year:  2018        PMID: 29511948     DOI: 10.1007/s11912-018-0669-y

Source DB:  PubMed          Journal:  Curr Oncol Rep        ISSN: 1523-3790            Impact factor:   5.075


  28 in total

1.  Discontinuation of dasatinib in patients with chronic myeloid leukaemia who have maintained deep molecular response for longer than 1 year (DADI trial): a multicentre phase 2 trial.

Authors:  Jun Imagawa; Hideo Tanaka; Masaya Okada; Hirohisa Nakamae; Masayuki Hino; Kazunori Murai; Yoji Ishida; Takashi Kumagai; Seiichi Sato; Kazuteru Ohashi; Hisashi Sakamaki; Hisashi Wakita; Nobuhiko Uoshima; Yasunori Nakagawa; Yosuke Minami; Masahiro Ogasawara; Tomoharu Takeoka; Hiroshi Akasaka; Takahiko Utsumi; Naokuni Uike; Tsutomu Sato; Sachiko Ando; Kensuke Usuki; Satoshi Morita; Junichi Sakamoto; Shinya Kimura
Journal:  Lancet Haematol       Date:  2015-11-10       Impact factor: 18.959

2.  E14a2 BCR-ABL1 transcript is associated with a higher rate of treatment-free remission in individuals with chronic myeloid leukemia after stopping tyrosine kinase inhibitor therapy.

Authors:  Simone Claudiani; Jane F Apperley; Robert Peter Gale; Richard Clark; Richard Szydlo; Simona Deplano; Renuka Palanicawandar; Jamshid Khorashad; Letizia Foroni; Dragana Milojkovic
Journal:  Haematologica       Date:  2017-05-11       Impact factor: 9.941

3.  Expression of the CTLA-4 ligand CD86 on plasmacytoid dendritic cells (pDC) predicts risk of disease recurrence after treatment discontinuation in CML.

Authors:  C Schütz; S Inselmann; S Saussele; C T Dietz; M C Mu Ller; E Eigendorff; C A Brendel; S K Metzelder; T H Bru Mmendorf; C Waller; J Dengler; M E Goebeler; R Herbst; G Freunek; S Hanzel; T Illmer; Y Wang; T Lange; F Finkernagel; R Hehlmann; M Huber; A Neubauer; A Hochhaus; J Guilhot; F Xavier Mahon; M Pfirrmann; A Burchert
Journal:  Leukemia       Date:  2017-01-11       Impact factor: 11.528

4.  Long-Term Follow-Up of the French Stop Imatinib (STIM1) Study in Patients With Chronic Myeloid Leukemia.

Authors:  Gabriel Etienne; Joëlle Guilhot; Delphine Rea; Françoise Rigal-Huguet; Franck Nicolini; Aude Charbonnier; Agnès Guerci-Bresler; Laurence Legros; Bruno Varet; Martine Gardembas; Viviane Dubruille; Michel Tulliez; Marie-Pierre Noel; Jean-Christophe Ianotto; Bruno Villemagne; Martin Carré; François Guilhot; Philippe Rousselot; François-Xavier Mahon
Journal:  J Clin Oncol       Date:  2016-10-31       Impact factor: 44.544

5.  Long-Term Outcomes of Imatinib Treatment for Chronic Myeloid Leukemia.

Authors:  Andreas Hochhaus; Richard A Larson; François Guilhot; Jerald P Radich; Susan Branford; Timothy P Hughes; Michele Baccarani; Michael W Deininger; Francisco Cervantes; Satoko Fujihara; Christine-Elke Ortmann; Hans D Menssen; Hagop Kantarjian; Stephen G O'Brien; Brian J Druker
Journal:  N Engl J Med       Date:  2017-03-09       Impact factor: 91.245

6.  Chronic myeloid leukaemia: ESMO Clinical Practice Guidelines for diagnosis, treatment and follow-up.

Authors:  A Hochhaus; S Saussele; G Rosti; F-X Mahon; J J W M Janssen; H Hjorth-Hansen; J Richter; C Buske
Journal:  Ann Oncol       Date:  2017-07-01       Impact factor: 32.976

Review 7.  Standardized definitions of molecular response in chronic myeloid leukemia.

Authors:  N C P Cross; H E White; M C Müller; G Saglio; A Hochhaus
Journal:  Leukemia       Date:  2012-04-16       Impact factor: 11.528

8.  NCCN Guidelines Insights: Chronic Myeloid Leukemia, Version 1.2017.

Authors:  Arnel Pallera; Jessica K Altman; Ellin Berman; Camille N Abboud; Bhavana Bhatnagar; Peter Curtin; Daniel J DeAngelo; Jason Gotlib; R Tanner Hagelstrom; Gabriela Hobbs; Madan Jagasia; Hagop M Kantarjian; Patricia Kropf; Leland Metheny; Joseph O Moore; Evelena Ontiveros; Enkhtsetseg Purev; Albert Quiery; Vishnu V B Reddy; Michal G Rose; Neil P Shah; B Douglas Smith; David S Snyder; Kendra L Sweet; Raoul Tibes; David T Yang; Kristina Gregory; Hema Sundar; Michael Deininger; Jerald P Radich
Journal:  J Natl Compr Canc Netw       Date:  2016-12       Impact factor: 11.908

9.  Natural killer-cell counts are associated with molecular relapse-free survival after imatinib discontinuation in chronic myeloid leukemia: the IMMUNOSTIM study.

Authors:  Delphine Rea; Guylaine Henry; Zena Khaznadar; Gabriel Etienne; François Guilhot; Franck Nicolini; Joelle Guilhot; Philippe Rousselot; Françoise Huguet; Laurence Legros; Martine Gardembas; Viviane Dubruille; Agnès Guerci-Bresler; Aude Charbonnier; Frédéric Maloisel; Jean-Christophe Ianotto; Bruno Villemagne; François-Xavier Mahon; Hélène Moins-Teisserenc; Nicolas Dulphy; Antoine Toubert
Journal:  Haematologica       Date:  2017-05-18       Impact factor: 9.941

Review 10.  Deep molecular responses for treatment-free remission in chronic myeloid leukemia.

Authors:  Stéphanie Dulucq; Francois-Xavier Mahon
Journal:  Cancer Med       Date:  2016-07-01       Impact factor: 4.452

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  6 in total

Review 1.  Treatment and monitoring of Philadelphia chromosome-positive leukemia patients: recent advances and remaining challenges.

Authors:  Simona Soverini; Renato Bassan; Thomas Lion
Journal:  J Hematol Oncol       Date:  2019-04-23       Impact factor: 17.388

Review 2.  Next-generation sequencing for BCR-ABL1 kinase domain mutation testing in patients with chronic myeloid leukemia: a position paper.

Authors:  Simona Soverini; Elisabetta Abruzzese; Monica Bocchia; Massimiliano Bonifacio; Sara Galimberti; Antonella Gozzini; Alessandra Iurlo; Luigiana Luciano; Patrizia Pregno; Gianantonio Rosti; Giuseppe Saglio; Fabio Stagno; Mario Tiribelli; Paolo Vigneri; Giovanni Barosi; Massimo Breccia
Journal:  J Hematol Oncol       Date:  2019-12-05       Impact factor: 17.388

Review 3.  Monitoring of Minimal Residual Disease (MRD) in Chronic Myeloid Leukemia: Recent Advances.

Authors:  Cosimo Cumbo; Luisa Anelli; Giorgina Specchia; Francesco Albano
Journal:  Cancer Manag Res       Date:  2020-05-06       Impact factor: 3.989

Review 4.  Nuclear Receptors as Potential Therapeutic Targets for Myeloid Leukemia.

Authors:  Pan Pan; Xiao Chen
Journal:  Cells       Date:  2020-08-19       Impact factor: 6.600

Review 5.  Prospects for achieving treatment-free remission in chronic myeloid leukaemia.

Authors:  Giuseppe Saglio; Robert P Gale
Journal:  Br J Haematol       Date:  2020-02-14       Impact factor: 6.998

6.  Making Treatment-Free Remission (TFR) Easier in Chronic Myeloid Leukemia: Fact-Checking and Practical Management Tools.

Authors:  Fausto Castagnetti; Gianni Binotto; Isabella Capodanno; Atto Billio; Elisabetta Calistri; Francesco Cavazzini; Monica Crugnola; Antonella Gozzini; Gabriele Gugliotta; Mauro Krampera; Alessandro Lucchesi; Anna Merli; Maria Cristina Miggiano; Claudia Minotto; Monica Poggiaspalla; Marzia Salvucci; Barbara Scappini; Mario Tiribelli; Elena Trabacchi; Gianantonio Rosti; Sara Galimberti; Massimiliano Bonifacio
Journal:  Target Oncol       Date:  2021-10-18       Impact factor: 4.864

  6 in total

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