Literature DB >> 29426586

Safety of rAAV2/2-ND4 Gene Therapy for Leber Hereditary Optic Neuropathy.

Catherine Vignal1, Scott Uretsky2, Serge Fitoussi2, Anne Galy2, Laure Blouin2, Jean-François Girmens3, Samuel Bidot1, Nitza Thomasson2, Céline Bouquet2, Sonia Valero2, Sandrine Meunier2, Jean-Philippe Combal2, Bernard Gilly2, Barrett Katz4, José-Alain Sahel5.   

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Year:  2018        PMID： 29426586     DOI： 10.1016/j.ophtha.2017.12.036

Source DB:  PubMed          Journal:  Ophthalmology        ISSN： 0161-6420            Impact factor:   12.079


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  29 in total

1.  Immune Response and Intraocular Inflammation in Patients With Leber Hereditary Optic Neuropathy Treated With Intravitreal Injection of Recombinant Adeno-Associated Virus 2 Carrying the ND4 Gene: A Secondary Analysis of a Phase 1/2 Clinical Trial.

Authors:  Céline Bouquet; Catherine Vignal Clermont; Anne Galy; Serge Fitoussi; Laure Blouin; Marion R Munk; Sonia Valero; Sandrine Meunier; Barrett Katz; José Alain Sahel; Nitza Thomasson
Journal:  JAMA Ophthalmol       Date:  2019-04-01       Impact factor: 7.389

2.  Retinal gene therapy: an eye-opener of the 21st century.

Authors:  Anne Louise Askou; Thomas Stax Jakobsen; Thomas J Corydon
Journal:  Gene Ther       Date:  2020-06-19       Impact factor: 5.250

Review 3.  Mesenchymal stem cells (MSCs) in Leber's hereditary optic neuropathy (LHON): a potential therapeutic approach for future.

Authors:  Mohana Devi Subramaniam; Ruth Bright Chirayath; Mahalaxmi Iyer; Aswathy P Nair; Balachandar Vellingiri
Journal:  Int Ophthalmol       Date:  2022-03-31       Impact factor: 2.029

Review 4.  Pathophysiology of Conversion to Symptomatic Leber Hereditary Optic Neuropathy and Therapeutic Implications: a Review.

Authors:  Alvaro J Mejia-Vergara; Nicolas Seleme; Alfredo A Sadun; Rustum Karanjia
Journal:  Curr Neurol Neurosci Rep       Date:  2020-04-15       Impact factor: 5.081

Review 5.  AAV Vector Immunogenicity in Humans: A Long Journey to Successful Gene Transfer.

Authors:  Helena Costa Verdera; Klaudia Kuranda; Federico Mingozzi
Journal:  Mol Ther       Date:  2020-01-10       Impact factor: 11.454

6.  Clinical utility gene card for: inherited optic neuropathies including next-generation sequencing-based approaches.

Authors:  Neringa Jurkute; Anna Majander; Richard Bowman; Marcela Votruba; Stephen Abbs; James Acheson; Guy Lenaers; Patrizia Amati-Bonneau; Mariya Moosajee; Gavin Arno; Patrick Yu-Wai-Man
Journal:  Eur J Hum Genet       Date:  2018-08-24       Impact factor: 4.246

7.  Intravitreal Gene Therapy vs. Natural History in Patients With Leber Hereditary Optic Neuropathy Carrying the m.11778G>A ND4 Mutation: Systematic Review and Indirect Comparison.

Authors:  Nancy J Newman; Patrick Yu-Wai-Man; Valerio Carelli; Valerie Biousse; Mark L Moster; Catherine Vignal-Clermont; Robert C Sergott; Thomas Klopstock; Alfredo A Sadun; Jean-François Girmens; Chiara La Morgia; Adam A DeBusk; Neringa Jurkute; Claudia Priglinger; Rustum Karanjia; Constant Josse; Julie Salzmann; François Montestruc; Michel Roux; Magali Taiel; José-Alain Sahel
Journal:  Front Neurol       Date:  2021-05-24       Impact factor: 4.003

Review 8.  Bioengineering strategies for restoring vision.

Authors:  Jasmina Cehajic-Kapetanovic; Mandeep S Singh; Eberhart Zrenner; Robert E MacLaren
Journal:  Nat Biomed Eng       Date:  2022-01-31       Impact factor: 25.671

Review 9.  Current and Emerging Clinical Treatment in Mitochondrial Disease.

Authors:  Rory J Tinker; Albert Z Lim; Renae J Stefanetti; Robert McFarland
Journal:  Mol Diagn Ther       Date:  2021-03-01       Impact factor: 4.074

10.  Leber Hereditary Optic Neuropathy Gene Therapy: Adverse Events and Visual Acuity Results of All Patient Groups.

Authors:  Byron L Lam; William J Feuer; Janet L Davis; Vittorio Porciatti; Hong Yu; Robert B Levy; Elizabeth Vanner; John Guy
Journal:  Am J Ophthalmol       Date:  2022-03-07       Impact factor: 5.488
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