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Literature DB >> 29319697

FDA approves hereditary blindness gene therapy.

Abstract

Entities: Disease

Mesh：

Year: 2018 PMID： 29319697 DOI： 10.1038/nbt0118-6a

Source DB: PubMed Journal: Nat Biotechnol ISSN： 1087-0156 Impact factor: 54.908

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1 in total

1. First AAV gene therapy poised for landmark approval.

Authors: Eric Smalley
Journal: Nat Biotechnol Date: 2017-11-09 Impact factor: 54.908

1 in total

18 in total

1. To win at gene therapy, companies pick viruses with production credentials.

Authors: Cormac Sheridan
Journal: Nat Biotechnol Date: 2019-01-03 Impact factor: 54.908

2. Rollout of high-priced cell and gene therapies forces payer rethink.

Authors: Melanie Senior
Journal: Nat Biotechnol Date: 2018-04-05 Impact factor: 54.908

3. A Common Outer Retinal Change in Retinal Degeneration by Optical Coherence Tomography Can Be Used to Assess Outcomes of Gene Therapy.

Authors: Myung Kuk Joe; Wenbo Li; Suja Hiriyanna; Wenhan Yu; Shreya A Shah; Mones Abu-Asab; Haohua Qian; Zhijian Wu
Journal: Hum Gene Ther Date: 2019-12-04 Impact factor: 5.695

4. Intein-mediated protein trans-splicing expands adeno-associated virus transfer capacity in the retina.

Authors: Patrizia Tornabene; Ivana Trapani; Renato Minopoli; Miriam Centrulo; Mariangela Lupo; Sonia de Simone; Paola Tiberi; Fabio Dell'Aquila; Elena Marrocco; Carolina Iodice; Antonella Iuliano; Carlo Gesualdo; Settimio Rossi; Laura Giaquinto; Silvia Albert; Carel B Hoyng; Elena Polishchuk; Frans P M Cremers; Enrico M Surace; Francesca Simonelli; Maria A De Matteis; Roman Polishchuk; Alberto Auricchio
Journal: Sci Transl Med Date: 2019-05-15 Impact factor: 19.319

Review 5. Development of New Strategies Using Extracellular Vesicles Loaded with Exogenous Nucleic Acid.

Authors: Nicola Salvatore Orefice
Journal: Pharmaceutics Date: 2020-07-26 Impact factor: 6.321

6. Argininosuccinic aciduria fosters neuronal nitrosative stress reversed by Asl gene transfer.

Authors: Julien Baruteau; Dany P Perocheau; Joanna Hanley; Maëlle Lorvellec; Eridan Rocha-Ferreira; Rajvinder Karda; Joanne Ng; Natalie Suff; Juan Antinao Diaz; Ahad A Rahim; Michael P Hughes; Blerida Banushi; Helen Prunty; Mariya Hristova; Deborah A Ridout; Alex Virasami; Simon Heales; Stewen J Howe; Suzanne M K Buckley; Philippa B Mills; Paul Gissen; Simon N Waddington
Journal: Nat Commun Date: 2018-08-29 Impact factor: 14.919

7. Codon-Optimization of Wild-Type Adeno-Associated Virus Capsid Sequences Enhances DNA Family Shuffling while Conserving Functionality.

Authors: Marti Cabanes-Creus; Samantha L Ginn; Anais K Amaya; Sophia H Y Liao; Adrian Westhaus; Claus V Hallwirth; Patrick Wilmott; Jason Ward; Kimberley L Dilworth; Giorgia Santilli; Arkadiusz Rybicki; Hiroyuki Nakai; Adrian J Thrasher; Adrian C Filip; Ian E Alexander; Leszek Lisowski
Journal: Mol Ther Methods Clin Dev Date: 2018-11-01 Impact factor: 6.698