Literature DB >> 29052639

FDA advisers back gene therapy for rare form of blindness.

Heidi Ledford.   

Abstract

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Year:  2017        PMID： 29052639     DOI： 10.1038/nature.2017.22819

Source DB:  PubMed          Journal:  Nature        ISSN： 0028-0836            Impact factor:   49.962


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  8 in total

1.  Adeno-associated virus characterization for cargo discrimination through nanopore responsiveness.

Authors:  Buddini Iroshika Karawdeniya; Y M Nuwan D Y Bandara; Aminul Islam Khan; Wei Tong Chen; Hoang-Anh Vu; Adnan Morshed; Junghae Suh; Prashanta Dutta; Min Jun Kim
Journal:  Nanoscale       Date:  2020-12-08       Impact factor: 7.790

Review 2.  From the Sea for the Sight: Marine Derived Products for Human Vision.

Authors:  Simona Brillante; Christian Galasso; Chiara Lauritano; Sabrina Carrella
Journal:  Front Aging Neurosci       Date:  2022-05-09       Impact factor: 5.702

3.  A Drug-Tunable Gene Therapy for Broad-Spectrum Protection against Retinal Degeneration.

Authors:  Clayton P Santiago; Casey J Keuthan; Sanford L Boye; Shannon E Boye; Aisha A Imam; John D Ash
Journal:  Mol Ther       Date:  2018-07-19       Impact factor: 11.454

4.  Human iPSC Modeling Reveals Mutation-Specific Responses to Gene Therapy in a Genotypically Diverse Dominant Maculopathy.

Authors:  Divya Sinha; Benjamin Steyer; Pawan K Shahi; Katherine P Mueller; Rasa Valiauga; Kimberly L Edwards; Cole Bacig; Stephanie S Steltzer; Sandhya Srinivasan; Amr Abdeen; Evan Cory; Viswesh Periyasamy; Alireza Fotuhi Siahpirani; Edwin M Stone; Budd A Tucker; Sushmita Roy; Bikash R Pattnaik; Krishanu Saha; David M Gamm
Journal:  Am J Hum Genet       Date:  2020-07-23       Impact factor: 11.025

Review 5.  Neuronal Reprogramming for Tissue Repair and Neuroregeneration.

Authors:  Roxanne Hsiang-Chi Liou; Thomas L Edwards; Keith R Martin; Raymond Ching-Bong Wong
Journal:  Int J Mol Sci       Date:  2020-06-16       Impact factor: 5.923

6.  Overloaded Adeno-Associated Virus as a Novel Gene Therapeutic Tool for Otoferlin-Related Deafness.

Authors:  Vladan Rankovic; Christian Vogl; Nele M Dörje; Iman Bahader; Carlos J Duque-Afonso; Anupriya Thirumalai; Thomas Weber; Kathrin Kusch; Nicola Strenzke; Tobias Moser
Journal:  Front Mol Neurosci       Date:  2021-01-07       Impact factor: 5.639

7.  AAV-miR-204 Protects from Retinal Degeneration by Attenuation of Microglia Activation and Photoreceptor Cell Death.

Authors:  Marianthi Karali; Irene Guadagnino; Elena Marrocco; Rossella De Cegli; Annamaria Carissimo; Mariateresa Pizzo; Simona Casarosa; Ivan Conte; Enrico Maria Surace; Sandro Banfi
Journal:  Mol Ther Nucleic Acids       Date:  2019-11-18       Impact factor: 8.886

8.  A qualitative study among patients with an inherited retinal disease on the meaning of genomic unsolicited findings.

Authors:  Ignaas Devisch; Elfride De Baere; Marlies Saelaert; Heidi Mertes; Tania Moerenhout; Caroline Van Cauwenbergh; Bart P Leroy
Journal:  Sci Rep       Date:  2021-08-04       Impact factor: 4.379
  8 in total

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