Nancy S Jecker1. Show Affiliations » 1. a University of Washington.
Abstract
Entities: Disease Species
Mesh: See more » Compassionate Use Trials/ethicsEthics, MedicalHealth Care Rationing/ethicsHumansInfantOligonucleotides/therapeutic usePatient Selection/ethicsSpinal Muscular Atrophies of Childhood/drug therapyTherapies, Investigational/ethicsUnited States
Substances: See more » Oligonucleotidesnusinersen
Year: 2017 PMID: 29020544 DOI: 10.1080/15265161.2017.1365196
Source DB: PubMed Journal: Am J Bioeth ISSN: 1526-5161 Impact factor: 11.229