Literature DB >> 28927986

Unfounded Claims of Improved Functional Outcomes Attributed to Follistatin Gene Therapy in Inclusion Body Myositis.

Steven A Greenberg1.   

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Year:  2017        PMID: 28927986      PMCID: PMC5628928          DOI: 10.1016/j.ymthe.2017.09.002

Source DB:  PubMed          Journal:  Mol Ther        ISSN: 1525-0016            Impact factor:   11.454


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  14 in total

1.  Anti-T-lymphocyte globulin treatment in inclusion body myositis: a randomized pilot study.

Authors:  C Lindberg; E Trysberg; A Tarkowski; A Oldfors
Journal:  Neurology       Date:  2003-07-22       Impact factor: 9.910

2.  Changes to registration elements and results in a cohort of Clinicaltrials.gov trials were not reflected in published articles.

Authors:  Shelly Pranić; Ana Marušić
Journal:  J Clin Epidemiol       Date:  2015-07-29       Impact factor: 6.437

3.  Selective reporting in clinical trials: analysis of trial protocols accepted by The Lancet.

Authors:  Sanaa Al-Marzouki; Ian Roberts; Stephen Evans; Tom Marshall
Journal:  Lancet       Date:  2008-07-19       Impact factor: 79.321

4.  Comparison of registered and published primary outcomes in randomized controlled trials.

Authors:  Sylvain Mathieu; Isabelle Boutron; David Moher; Douglas G Altman; Philippe Ravaud
Journal:  JAMA       Date:  2009-09-02       Impact factor: 56.272

5.  Clinical Trials Registration and Results Information Submission. Final rule.

Authors: 
Journal:  Fed Regist       Date:  2016-09-21

6.  Follistatin Gene Therapy for Sporadic Inclusion Body Myositis Improves Functional Outcomes.

Authors:  Jerry R Mendell; Zarife Sahenk; Samiah Al-Zaidy; Louise R Rodino-Klapac; Linda P Lowes; Lindsay N Alfano; Katherine Berry; Natalie Miller; Mehmet Yalvac; Igor Dvorchik; Melissa Moore-Clingenpeel; Kevin M Flanigan; Kathleen Church; Kim Shontz; Choumpree Curry; Sarah Lewis; Markus McColly; Mark J Hogan; Brian K Kaspar
Journal:  Mol Ther       Date:  2017-03-06       Impact factor: 11.454

7.  Treatment of sporadic inclusion body myositis with bimagrumab.

Authors:  Anthony A Amato; Kumaraswamy Sivakumar; Namita Goyal; William S David; Mohammad Salajegheh; Jens Praestgaard; Estelle Lach-Trifilieff; Anne-Ulrike Trendelenburg; Didier Laurent; David J Glass; Ronenn Roubenoff; Brian S Tseng; Steven A Greenberg
Journal:  Neurology       Date:  2014-11-07       Impact factor: 9.910

8.  A phase 1/2a follistatin gene therapy trial for becker muscular dystrophy.

Authors:  Jerry R Mendell; Zarife Sahenk; Vinod Malik; Ana M Gomez; Kevin M Flanigan; Linda P Lowes; Lindsay N Alfano; Katherine Berry; Eric Meadows; Sarah Lewis; Lyndsey Braun; Kim Shontz; Maria Rouhana; Kelly Reed Clark; Xiomara Q Rosales; Samiah Al-Zaidy; Alessandra Govoni; Louise R Rodino-Klapac; Mark J Hogan; Brian K Kaspar
Journal:  Mol Ther       Date:  2014-10-17       Impact factor: 11.454

9.  Targeting protein homeostasis in sporadic inclusion body myositis.

Authors:  Mhoriam Ahmed; Pedro M Machado; Adrian Miller; Charlotte Spicer; Laura Herbelin; Jianghua He; Janelle Noel; Yunxia Wang; April L McVey; Mamatha Pasnoor; Philip Gallagher; Jeffrey Statland; Ching-Hua Lu; Bernadett Kalmar; Stefen Brady; Huma Sethi; George Samandouras; Matt Parton; Janice L Holton; Anne Weston; Lucy Collinson; J Paul Taylor; Giampietro Schiavo; Michael G Hanna; Richard J Barohn; Mazen M Dimachkie; Linda Greensmith
Journal:  Sci Transl Med       Date:  2016-03-23       Impact factor: 17.956

Review 10.  Comparison of registered and published outcomes in randomized controlled trials: a systematic review.

Authors:  Christopher W Jones; Lukas G Keil; Wesley C Holland; Melissa C Caughey; Timothy F Platts-Mills
Journal:  BMC Med       Date:  2015-11-18       Impact factor: 8.775

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  3 in total

Review 1.  Inclusion Body Myositis: Update on Pathogenesis and Treatment.

Authors:  Elie Naddaf; Richard J Barohn; Mazen M Dimachkie
Journal:  Neurotherapeutics       Date:  2018-10       Impact factor: 7.620

Review 2.  New Developments in the Genetics of Inclusion Body Myositis.

Authors:  Kyla A Britson; Stephanie Y Yang; Thomas E Lloyd
Journal:  Curr Rheumatol Rep       Date:  2018-04-02       Impact factor: 4.592

Review 3.  Myostatin/Activin Receptor Ligands in Muscle and the Development Status of Attenuating Drugs.

Authors:  Buel D Rodgers; Christopher W Ward
Journal:  Endocr Rev       Date:  2022-03-09       Impact factor: 25.261

  3 in total

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