Literature DB >> 28848834

Editorial: Clinical Trial Design for Alpha-1 Antitrypsin Deficiency: A Model for Rare Diseases.

Michael R Jacobs1, Gerard J Criner1.   

Abstract

Entities:  

Keywords:  alpha-1 antitrypsin deficiency; clinical trial design; rare diseases: adaptive clinical trials; surrogate endpoints

Year:  2015        PMID: 28848834      PMCID: PMC5556963          DOI: 10.15326/jcopdf.2.2.2015.0140

Source DB:  PubMed          Journal:  Chronic Obstr Pulm Dis        ISSN: 2372-952X


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1.  An Official American Thoracic Society/European Respiratory Society Statement: Research questions in chronic obstructive pulmonary disease.

Authors:  Bartolome R Celli; Marc Decramer; Jadwiga A Wedzicha; Kevin C Wilson; Alvar Agustí; Gerard J Criner; William MacNee; Barry J Make; Stephen I Rennard; Robert A Stockley; Claus Vogelmeier; Antonio Anzueto; David H Au; Peter J Barnes; Pierre-Regis Burgel; Peter M Calverley; Ciro Casanova; Enrico M Clini; Christopher B Cooper; Harvey O Coxson; Daniel J Dusser; Leonardo M Fabbri; Bonnie Fahy; Gary T Ferguson; Andrew Fisher; Monica J Fletcher; Maurice Hayot; John R Hurst; Paul W Jones; Donald A Mahler; François Maltais; David M Mannino; Fernando J Martinez; Marc Miravitlles; Paula M Meek; Alberto Papi; Klaus F Rabe; Nicolas Roche; Frank C Sciurba; Sanjay Sethi; Nikos Siafakas; Don D Sin; Joan B Soriano; James K Stoller; Donald P Tashkin; Thierry Troosters; Geert M Verleden; Johny Verschakelen; Jorgen Vestbo; John W Walsh; George R Washko; Robert A Wise; Emiel F M Wouters; Richard L ZuWallack
Journal:  Am J Respir Crit Care Med       Date:  2015-04-01       Impact factor: 21.405

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