| Literature DB >> 28776279 |
Neerja Gupta1, Vishal Vishnu Tewari2, Manoj Kumar3, Nitika Langeh4, Aditi Gupta4, Pallavi Mishra4, Punit Kaur3, Vedam Ramprasad5, Sakthivel Murugan5, Reema Kumar2, Manisha Jana5, Madhulika Kabra4.
Abstract
Asparagine synthetase deficiency is a rare inborn error of metabolism caused by a defect in ASNS, a gene encoding asparagine synthetase. It manifests with a severe neurological phenotype manifesting as severe developmental delay, congenital microcephaly, spasticity and refractory seizures. To date, nineteen patients from twelve unrelated families have been identified. Majority of the mutations are missense and nonsense mutations in homozygous or compound heterozygous state. We add another case from India which harbored a novel homozygous missense variation in exon 11 and compare the current case with previously reported cases.Entities:
Keywords: Asparagine Synthetase (ASNS) gene; Asparagine synthetase deficiency; Encephalopathy; Exome sequencing; Microcephaly
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Year: 2017 PMID: 28776279 DOI: 10.1007/s11011-017-0073-6
Source DB: PubMed Journal: Metab Brain Dis ISSN: 0885-7490 Impact factor: 3.584