Literature DB >> 28625571

Micromanaging Tolerance in Hemophilia A Gene Therapy.

Jennielle Jobson1, Brian D Brown2.   

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Year:  2017        PMID： 28625571      PMCID： PMC5542799          DOI： 10.1016/j.ymthe.2017.06.001

Source DB:  PubMed          Journal:  Mol Ther        ISSN： 1525-0016            Impact factor:   11.454


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  10 in total

1.  Induction and role of regulatory CD4+CD25+ T cells in tolerance to the transgene product following hepatic in vivo gene transfer.

Authors:  Ou Cao; Eric Dobrzynski; Lixin Wang; Sushrusha Nayak; Bethany Mingle; Cox Terhorst; Roland W Herzog
Journal:  Blood       Date:  2007-04-16       Impact factor: 22.113

2.  Eradication of neutralizing antibodies to factor VIII in canine hemophilia A after liver gene therapy.

Authors:  Jonathan D Finn; Margareth C Ozelo; Denise E Sabatino; Helen W G Franck; Elizabeth P Merricks; Julie M Crudele; Shangzhen Zhou; Haig H Kazazian; David Lillicrap; Timothy C Nichols; Valder R Arruda
Journal:  Blood       Date:  2010-09-28       Impact factor: 22.113

3.  Endogenous microRNA can be broadly exploited to regulate transgene expression according to tissue, lineage and differentiation state.

Authors:  Brian D Brown; Bernhard Gentner; Alessio Cantore; Silvia Colleoni; Mario Amendola; Anna Zingale; Alessia Baccarini; Giovanna Lazzari; Cesare Galli; Luigi Naldini
Journal:  Nat Biotechnol       Date:  2007-11-16       Impact factor: 54.908

Review 4.  Alloantibodies to therapeutic factor VIII in hemophilia A: the role of von Willebrand factor in regulating factor VIII immunogenicity.

Authors:  Johannes Oldenburg; Sébastien Lacroix-Desmazes; David Lillicrap
Journal:  Haematologica       Date:  2015-02       Impact factor: 9.941

Review 5.  Gene Therapy for Hemophilia.

Authors:  Arthur W Nienhuis; Amit C Nathwani; Andrew M Davidoff
Journal:  Mol Ther       Date:  2017-04-11       Impact factor: 11.454

Review 6.  Gene therapy for immune tolerance induction in hemophilia with inhibitors.

Authors:  V R Arruda; B J Samelson-Jones
Journal:  J Thromb Haemost       Date:  2016-05-14       Impact factor: 5.824

7.  A Novel Platform for Immune Tolerance Induction in Hemophilia A Mice.

Authors:  Simone Merlin; Elvira Stefania Cannizzo; Ester Borroni; Valentina Bruscaggin; Piercarla Schinco; Warut Tulalamba; Marinee K Chuah; Valder R Arruda; Thierry VandenDriessche; Maria Prat; Guido Valente; Antonia Follenzi
Journal:  Mol Ther       Date:  2017-05-26       Impact factor: 11.454

8.  Liver-directed lentiviral gene therapy in a dog model of hemophilia B.

Authors:  Alessio Cantore; Marco Ranzani; Cynthia C Bartholomae; Monica Volpin; Patrizia Della Valle; Francesca Sanvito; Lucia Sergi Sergi; Pierangela Gallina; Fabrizio Benedicenti; Dwight Bellinger; Robin Raymer; Elizabeth Merricks; Francesca Bellintani; Samia Martin; Claudio Doglioni; Armando D'Angelo; Thierry VandenDriessche; Marinee K Chuah; Manfred Schmidt; Timothy Nichols; Eugenio Montini; Luigi Naldini
Journal:  Sci Transl Med       Date:  2015-03-04       Impact factor: 17.956

9.  Adenovirus-associated virus vector-mediated gene transfer in hemophilia B.

Authors:  Amit C Nathwani; Edward G D Tuddenham; Savita Rangarajan; Cecilia Rosales; Jenny McIntosh; David C Linch; Pratima Chowdary; Anne Riddell; Arnulfo Jaquilmac Pie; Chris Harrington; James O'Beirne; Keith Smith; John Pasi; Bertil Glader; Pradip Rustagi; Catherine Y C Ng; Mark A Kay; Junfang Zhou; Yunyu Spence; Christopher L Morton; James Allay; John Coleman; Susan Sleep; John M Cunningham; Deokumar Srivastava; Etiena Basner-Tschakarjan; Federico Mingozzi; Katherine A High; John T Gray; Ulrike M Reiss; Arthur W Nienhuis; Andrew M Davidoff
Journal:  N Engl J Med       Date:  2011-12-10       Impact factor: 176.079

10.  The miR-126-VEGFR2 axis controls the innate response to pathogen-associated nucleic acids.

Authors:  Judith Agudo; Albert Ruzo; Navpreet Tung; Hélène Salmon; Marylène Leboeuf; Daigo Hashimoto; Christian Becker; Lee-Ann Garrett-Sinha; Alessia Baccarini; Miriam Merad; Brian D Brown
Journal:  Nat Immunol       Date:  2013-11-24       Impact factor: 25.606
  10 in total
  2 in total

Review 1.  Innovative Approaches for Immune Tolerance to Factor VIII in the Treatment of Hemophilia A.

Authors:  Alexandra Sherman; Moanaro Biswas; Roland W Herzog
Journal:  Front Immunol       Date:  2017-11-24       Impact factor: 7.561

Review 2.  Escape or Fight: Inhibitors in Hemophilia A.

Authors:  Simone Merlin; Antonia Follenzi
Journal:  Front Immunol       Date:  2020-03-24       Impact factor: 7.561
  2 in total

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