Literature DB >> 28389197

[Haematopoietic stem cell transplantation in pyruvate kinase deficiency: When is it indicated?]

Paula Pérez-Albert1, María Guillen2, Marta Prudencio2, Marta Gonzalez-Vicent2, Julián Sevilla2.   

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Year:  2017        PMID: 28389197     DOI: 10.1016/j.anpedi.2017.02.016

Source DB:  PubMed          Journal:  An Pediatr (Engl Ed)        ISSN: 2341-2879


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  2 in total

1.  Allogeneic hematopoietic stem cell transplantation in a 3-year-old boy with congenital pyruvate kinase deficiency: A case report.

Authors:  Zhong-Yang Ma; Xue Yang
Journal:  World J Clin Cases       Date:  2021-04-26       Impact factor: 1.337

2.  Appraisal of patient-reported outcome measures in analogous diseases and recommendations for use in phase II and III clinical trials of pyruvate kinase deficiency.

Authors:  M S Salek; T Ionova; J R Johns; E N Oliva
Journal:  Qual Life Res       Date:  2018-11-19       Impact factor: 4.147

  2 in total

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