Maria Rosa Lidonnici1,2, Annamaria Aprile1,3, Marta Claudia Frittoli4, Giacomo Mandelli1, Ylenia Paleari1,2, Antonello Spinelli5, Bernhard Gentner4, Matilde Zambelli6, Cristina Parisi6, Laura Bellio6, Elena Cassinerio7, Laura Zanaboni7, Maria Domenica Cappellini7, Fabio Ciceri4, Sarah Marktel4, Giuliana Ferrari8,2. 1. San Raffaele-Telethon Institute for Gene Therapy (SR-TIGET), Division of Regenerative Medicine, Stem Cells and Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy. 2. Vita-Salute San Raffaele University, Milan, Italy. 3. Università degli Studi di Roma "Tor Vergata", Italy. 4. Hematology and Bone Marrow Transplantation Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy. 5. Experimental Imaging Centre, San Raffaele Scientific Institute, Milan, Italy. 6. Immunohematology and Transfusion Medicine Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy. 7. Università di Milano, Ca Granda Foundation IRCCS, Italy. 8. San Raffaele-Telethon Institute for Gene Therapy (SR-TIGET), Division of Regenerative Medicine, Stem Cells and Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy ferrari.giuliana@hsr.it.
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