Meredith Wadman. Show Affiliations »
Abstract
Entities: Disease
Mesh: See more » Biomedical Research/trendsBrain Diseases/geneticsBrain Diseases/therapyChild, PreschoolClinical Trials, Phase II as TopicHumansMuscular Atrophy, Spinal/geneticsMuscular Atrophy, Spinal/therapyOligonucleotides/therapeutic useRNA, Antisense/therapeutic useSurvival of Motor Neuron 1 Protein/geneticsSurvival of Motor Neuron 2 Protein/genetics
Substances: See more » OligonucleotidesRNA, AntisenseSMN1 protein, humanSMN2 protein, humanSurvival of Motor Neuron 1 ProteinSurvival of Motor Neuron 2 Proteinnusinersen
Year: 2016 PMID: 27980162 DOI: 10.1126/science.354.6318.1359
Source DB: PubMed Journal: Science ISSN: 0036-8075 Impact factor: 47.728