Literature DB >> 27980162

Antisense rescues babies from killer disease.

Meredith Wadman.   

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Year:  2016        PMID: 27980162     DOI: 10.1126/science.354.6318.1359

Source DB:  PubMed          Journal:  Science        ISSN: 0036-8075            Impact factor:   47.728


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  5 in total

1.  Efficient Gene Silencing in Brain Tumors with Hydrophobically Modified siRNAs.

Authors:  Maire F Osborn; Andrew H Coles; Diane Golebiowski; Dimas Echeverria; Michael P Moazami; Jonathan K Watts; Miguel Sena-Esteves; Anastasia Khvorova
Journal:  Mol Cancer Ther       Date:  2018-04-13       Impact factor: 6.261

2.  Comparison of the efficacy of MOE and PMO modifications of systemic antisense oligonucleotides in a severe SMA mouse model.

Authors:  Lei Sheng; Frank Rigo; C Frank Bennett; Adrian R Krainer; Yimin Hua
Journal:  Nucleic Acids Res       Date:  2020-04-06       Impact factor: 16.971

Review 3.  Oligonucleotide Therapeutics: From Discovery and Development to Patentability.

Authors:  Lara Moumné; Anne-Céline Marie; Nicolas Crouvezier
Journal:  Pharmaceutics       Date:  2022-01-22       Impact factor: 6.321

4.  Rescue of mis-splicing of a common SLC26A4 mutant associated with sensorineural hearing loss by antisense oligonucleotides.

Authors:  Pengchao Feng; Zhijiao Xu; Jialin Chen; Meizhen Liu; Yu Zhao; Daqi Wang; Lei Han; Li Wang; Bo Wan; Xingshun Xu; Dali Li; Yilai Shu; Yimin Hua
Journal:  Mol Ther Nucleic Acids       Date:  2022-03-19       Impact factor: 8.886

Review 5.  From Antisense RNA to RNA Modification: Therapeutic Potential of RNA-Based Technologies.

Authors:  Hironori Adachi; Martin Hengesbach; Yi-Tao Yu; Pedro Morais
Journal:  Biomedicines       Date:  2021-05-14
  5 in total

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