Qiushi Liang1, Merel Stok2, Yvette van Helsdingen1, Guus van der Velden1, Ed Jacobs3, Dirk Duncker4, Arnold Reuser2, Ans van der Ploeg2, Arnold Vulto5, Niek P van Til1, Gerard Wagemaker6. 1. Department of Hematology, Erasmus MC University Medical Center, Rotterdam, Netherlands. 2. Center for Lysosomal and Metabolic Diseases & Department of Clinical Genetics, Erasmus MC University Medical Center, Rotterdam, Netherlands. 3. Department of Genetics, Erasmus MC University Medical Center, Rotterdam, Netherlands. 4. Department of Experimental Cardiology, Erasmus MC University Medical Center, Rotterdam, Netherlands. 5. Hospital Pharmacy, Erasmus MC University Medical Center, Rotterdam, Netherlands. 6. Hacettepe University, Stem Cell Research and Development Center, Ankara, Turkey.
Authors: Merel Stok; Helen de Boer; Marshall W Huston; Edwin H Jacobs; Onno Roovers; Trudi P Visser; Holger Jahr; Dirk J Duncker; Elza D van Deel; Arnold J J Reuser; Niek P van Til; Gerard Wagemaker Journal: Mol Ther Methods Clin Dev Date: 2020-05-04 Impact factor: 6.698