. Show Affiliations »
Abstract
Entities: Species
Mesh: See more » ChildControlled Clinical Trials as TopicDrug ApprovalDystrophin/biosynthesisDystrophin/geneticsDystrophin/metabolismEvidence-Based MedicineHealth Services Needs and DemandHumansMaleMorpholinosMuscular Dystrophy, Duchenne/drug therapyMuscular Dystrophy, Duchenne/metabolismMuscular Dystrophy, Duchenne/physiopathologyOligonucleotides/therapeutic useUnited StatesUnited States Food and Drug Administration
Substances: See more » DystrophinMorpholinosOligonucleotideseteplirsen
Year: 2016 PMID: 27707475 DOI: 10.1016/S0140-6736(16)31765-2
Source DB: PubMed Journal: Lancet ISSN: 0140-6736 Impact factor: 79.321