Literature DB >> 27687132

A Cure For Hemophilia: the Promise Becomes a Reality.

Roland W Herzog.   

Abstract

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Year:  2016        PMID： 27687132      PMCID： PMC5113114          DOI： 10.1038/mt.2016.169

Source DB:  PubMed          Journal:  Mol Ther        ISSN： 1525-0016            Impact factor:   11.454


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  1 in total

1.  Superior In vivo Transduction of Human Hepatocytes Using Engineered AAV3 Capsid.

Authors:  Koen Vercauteren; Brad E Hoffman; Irene Zolotukhin; Geoffrey D Keeler; Jing W Xiao; Etiena Basner-Tschakarjan; Katherine A High; Hildegund Cj Ertl; Charles M Rice; Arun Srivastava; Ype P de Jong; Roland W Herzog
Journal:  Mol Ther       Date:  2016-03-29       Impact factor: 11.454
  1 in total
  8 in total

Review 1.  Next Generation of Adeno-Associated Virus Vectors for Gene Therapy for Human Liver Diseases.

Authors:  Kenneth I Berns; Arun Srivastava
Journal:  Gastroenterol Clin North Am       Date:  2019-04-01       Impact factor: 3.806

Review 2.  Gene Therapy for Hemophilia.

Authors:  Arthur W Nienhuis; Amit C Nathwani; Andrew M Davidoff
Journal:  Mol Ther       Date:  2017-04-11       Impact factor: 11.454

Review 3.  Complexity of immune responses to AAV transgene products - Example of factor IX.

Authors:  Roland W Herzog
Journal:  Cell Immunol       Date:  2017-05-29       Impact factor: 4.868

4.  Direct Head-to-Head Evaluation of Recombinant Adeno-associated Viral Vectors Manufactured in Human versus Insect Cells.

Authors:  Oleksandr Kondratov; Damien Marsic; Sean M Crosson; Hector R Mendez-Gomez; Oleksandr Moskalenko; Mario Mietzsch; Regine Heilbronn; Jonathan R Allison; Kari B Green; Mavis Agbandje-McKenna; Sergei Zolotukhin
Journal:  Mol Ther       Date:  2017-08-10       Impact factor: 11.454

5.  Evaluation of engineered AAV capsids for hepatic factor IX gene transfer in murine and canine models.

Authors:  David M Markusic; Timothy C Nichols; Elizabeth P Merricks; Brett Palaschak; Irene Zolotukhin; Damien Marsic; Sergei Zolotukhin; Arun Srivastava; Roland W Herzog
Journal:  J Transl Med       Date:  2017-05-01       Impact factor: 5.531

6.  Illness perceptions and their relation to physical activity in children and adolescents with hemophilia.

Authors:  Sarah Bérubé; Claudine Amesse; Serge Sultan
Journal:  Health Psychol Behav Med       Date:  2020-10-04

Review 7.  Gene Therapy With Regulatory T Cells: A Beneficial Alliance.

Authors:  Moanaro Biswas; Sandeep R P Kumar; Cox Terhorst; Roland W Herzog
Journal:  Front Immunol       Date:  2018-03-19       Impact factor: 7.561

8.  An Observational Study from Long-Term AAV Re-administration in Two Hemophilia Dogs.

Authors:  Junjiang Sun; Wenwei Shao; Xiaojing Chen; Elizabeth P Merricks; Lauren Wimsey; Yasmina L Abajas; Glenn P Niemeyer; Clinton D Lothrop; Paul E Monahan; R Jude Samulski; Timothy C Nichols; Chengwen Li
Journal:  Mol Ther Methods Clin Dev       Date:  2018-08-04       Impact factor: 6.698
  8 in total

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