Literature DB >> 27404882

Safer conditioning for blood stem cell transplants.

Alessandro Aiuti1, Luigi Naldini1.   

Abstract

Mesh:

Year:  2016        PMID: 27404882     DOI: 10.1038/nbt.3629

Source DB:  PubMed          Journal:  Nat Biotechnol        ISSN: 1087-0156            Impact factor:   54.908


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  11 in total

1.  Antibody targeting KIT as pretransplantation conditioning in immunocompetent mice.

Authors:  Xingkui Xue; Nancy K Pech; W Christopher Shelley; Edward F Srour; Mervin C Yoder; Mary C Dinauer
Journal:  Blood       Date:  2010-09-02       Impact factor: 22.113

2.  Non-genotoxic conditioning for hematopoietic stem cell transplantation using a hematopoietic-cell-specific internalizing immunotoxin.

Authors:  Rahul Palchaudhuri; Borja Saez; Jonathan Hoggatt; Amir Schajnovitz; David B Sykes; Tiffany A Tate; Agnieszka Czechowicz; Youmna Kfoury; Fnu Ruchika; Derrick J Rossi; Gregory L Verdine; Michael K Mansour; David T Scadden
Journal:  Nat Biotechnol       Date:  2016-06-06       Impact factor: 54.908

Review 3.  Eliminating SCID row: new approaches to SCID.

Authors:  Donald B Kohn
Journal:  Hematology Am Soc Hematol Educ Program       Date:  2014-11-18

4.  Efficient transplantation via antibody-based clearance of hematopoietic stem cell niches.

Authors:  Agnieszka Czechowicz; Daniel Kraft; Irving L Weissman; Deepta Bhattacharya
Journal:  Science       Date:  2007-11-23       Impact factor: 47.728

5.  Defining the intensity of conditioning regimens: working definitions.

Authors:  Andrea Bacigalupo; Karen Ballen; Doug Rizzo; Sergio Giralt; Hillard Lazarus; Vincent Ho; Jane Apperley; Shimon Slavin; Marcelo Pasquini; Brenda M Sandmaier; John Barrett; Didier Blaise; Robert Lowski; Mary Horowitz
Journal:  Biol Blood Marrow Transplant       Date:  2009-09-01       Impact factor: 5.742

6.  Distinct routes of lineage development reshape the human blood hierarchy across ontogeny.

Authors:  Faiyaz Notta; Sasan Zandi; Naoya Takayama; Stephanie Dobson; Olga I Gan; Gavin Wilson; Kerstin B Kaufmann; Jessica McLeod; Elisa Laurenti; Cyrille F Dunant; John D McPherson; Lincoln D Stein; Yigal Dror; John E Dick
Journal:  Science       Date:  2015-11-05       Impact factor: 47.728

7.  Haemopoietic stem-cell transplantation with antibody-based minimal-intensity conditioning: a phase 1/2 study.

Authors:  Karin C Straathof; Kanchan Rao; Matthias Eyrich; Geoff Hale; Prudence Bird; Eleanor Berrie; Lucinda Brown; Stuart Adams; Paul G Schlegel; Nicholas Goulden; H Bobby Gaspar; Andrew R Gennery; Paul Landais; E G Davies; Malcolm K Brenner; Paul A Veys; Persis Jal Amrolia
Journal:  Lancet       Date:  2009-09-02       Impact factor: 79.321

8.  Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning.

Authors:  Alessandro Aiuti; Shimon Slavin; Memet Aker; Francesca Ficara; Sara Deola; Alessandra Mortellaro; Shoshana Morecki; Grazia Andolfi; Antonella Tabucchi; Filippo Carlucci; Enrico Marinello; Federica Cattaneo; Sergio Vai; Paolo Servida; Roberto Miniero; Maria Grazia Roncarolo; Claudio Bordignon
Journal:  Science       Date:  2002-06-28       Impact factor: 47.728

9.  Pre-Clinical Development of a Humanized Anti-CD47 Antibody with Anti-Cancer Therapeutic Potential.

Authors:  Jie Liu; Lijuan Wang; Feifei Zhao; Serena Tseng; Cyndhavi Narayanan; Lei Shura; Stephen Willingham; Maureen Howard; Susan Prohaska; Jens Volkmer; Mark Chao; Irving L Weissman; Ravindra Majeti
Journal:  PLoS One       Date:  2015-09-21       Impact factor: 3.240

10.  Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy.

Authors:  Alessandra Biffi; Eugenio Montini; Laura Lorioli; Martina Cesani; Francesca Fumagalli; Tiziana Plati; Cristina Baldoli; Sabata Martino; Andrea Calabria; Sabrina Canale; Fabrizio Benedicenti; Giuliana Vallanti; Luca Biasco; Simone Leo; Nabil Kabbara; Gianluigi Zanetti; William B Rizzo; Nalini A L Mehta; Maria Pia Cicalese; Miriam Casiraghi; Jaap J Boelens; Ubaldo Del Carro; David J Dow; Manfred Schmidt; Andrea Assanelli; Victor Neduva; Clelia Di Serio; Elia Stupka; Jason Gardner; Christof von Kalle; Claudio Bordignon; Fabio Ciceri; Attilio Rovelli; Maria Grazia Roncarolo; Alessandro Aiuti; Maria Sessa; Luigi Naldini
Journal:  Science       Date:  2013-07-11       Impact factor: 47.728

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  6 in total

Review 1.  Mitochondrial Neurogastrointestinal Encephalomyopathy Caused by Thymidine Phosphorylase Enzyme Deficiency: From Pathogenesis to Emerging Therapeutic Options.

Authors:  Rana Yadak; Peter Sillevis Smitt; Marike W van Gisbergen; Niek P van Til; Irenaeus F M de Coo
Journal:  Front Cell Neurosci       Date:  2017-02-15       Impact factor: 5.505

Review 2.  Beta Thalassemia: New Therapeutic Options Beyond Transfusion and Iron Chelation.

Authors:  Irene Motta; Rayan Bou-Fakhredin; Ali T Taher; Maria Domenica Cappellini
Journal:  Drugs       Date:  2020-07       Impact factor: 9.546

Review 3.  Curing Hemoglobinopathies: Challenges and Advances of Conventional and New Gene Therapy Approaches.

Authors:  Irene Motta; Valentina Ghiaccio; Andrea Cosentino; Laura Breda
Journal:  Mediterr J Hematol Infect Dis       Date:  2019-11-01       Impact factor: 2.576

4.  A systematic review and meta-analysis of gene therapy with hematopoietic stem and progenitor cells for monogenic disorders.

Authors:  Francesca Tucci; Stefania Galimberti; Luigi Naldini; Maria Grazia Valsecchi; Alessandro Aiuti
Journal:  Nat Commun       Date:  2022-03-14       Impact factor: 14.919

Review 5.  What Animal Cancers teach us about Human Biology.

Authors:  Patricia Kattner; Katharina Zeiler; Verena J Herbener; Katia La Ferla-Brühl; Rebecca Kassubek; Michael Grunert; Timo Burster; Oliver Brühl; Anna Sarah Weber; Hannah Strobel; Georg Karpel-Massler; Sibylle Ott; Alexa Hagedorn; Daniel Tews; Ansgar Schulz; Vikas Prasad; Markus D Siegelin; Lisa Nonnenmacher; Pamela Fischer-Posovszky; Marc-Eric Halatsch; Klaus-Michael Debatin; Mike-Andrew Westhoff
Journal:  Theranostics       Date:  2021-05-03       Impact factor: 11.556

Review 6.  Bone Marrow-Derived Mesenchymal Stromal Cells: A Novel Target to Optimize Hematopoietic Stem Cell Transplantation Protocols in Hematological Malignancies and Rare Genetic Disorders.

Authors:  Stefania Crippa; Ludovica Santi; Roberto Bosotti; Giulia Porro; Maria Ester Bernardo
Journal:  J Clin Med       Date:  2019-12-18       Impact factor: 4.241

  6 in total

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