Literature DB >> 27364325

Neurostatus e-Scoring improves consistency of Expanded Disability Status Scale assessments: A proof of concept study.

Marcus D'Souza1, Özgür Yaldizli1, Roland John2, Deborah R Vogt3, Athina Papadopoulou1, Elisabeth Lucassen1, Milena Menegola1, Michaela Andelova1, Frank Dahlke4, Franz Schnyder2, Ludwig Kappos1.   

Abstract

BACKGROUND: To improve the consistency of standardized Expanded Disability Status Scale (EDSS) assessments, an electronic data capture tool and analysis tool was developed, Neurostatus e-Scoring (NESC). This tool allows real-time feedback by comparing entries with established scoring rules.
OBJECTIVE: To test whether using NESC reduces inconsistencies as compared to the paper-and-pencil version of the Expanded Disability Status Scale (pEDSS).
METHODS: In all, 100 multiple sclerosis (MS) patients were assessed in random order on the same day by pairs of neurologists, one using pEDSS and one NESC. We compared inter-rater reliability and frequency of inconsistencies in Neurostatus subscores, functional system (FS) scores, ambulation and EDSS steps.
RESULTS: Inconsistencies of any type were more likely to occur when using pEDSS (mean odds ratio (95% confidence interval (CI)) = 2.93 (1.62; 5.29)). This was also the case for FS score inconsistencies (2.54 (1.40; 4.61)) and more likely for patients in the lower EDSS range (⩽3.5 vs >3.5) (5.32 (1.19; 23.77)). Overall, inter-rater agreement for the assessed Neurostatus subscores was high (median and inter-quartile range = 0.84 (0.73, 0.81)).
CONCLUSION: Our data provide class II evidence that the use of NESC increases consistency of standardized EDSS assessments, and may thus have the potential to decrease noise and increase power of MS clinical trials.

Entities:  

Keywords:  EDSS; Multiple sclerosis; clinical trial; disability; neurostatus

Mesh:

Year:  2016        PMID: 27364325     DOI: 10.1177/1352458516657439

Source DB:  PubMed          Journal:  Mult Scler        ISSN: 1352-4585            Impact factor:   6.312


  19 in total

1.  Retinal Tissue Perfusion in Patients with Multiple Sclerosis.

Authors:  Yi Liu; Silvia Delgado; Hong Jiang; Ying Lin; Jeffrey Hernandez; Yuqing Deng; Giovana Rosa Gameiro; Jianhua Wang
Journal:  Curr Eye Res       Date:  2019-05-15       Impact factor: 2.424

2.  Comparison of the EDSS, Timed 25-Foot Walk, and the 9-Hole Peg Test as Clinical Trial Outcomes in Relapsing-Remitting Multiple Sclerosis.

Authors:  Marcus W Koch; Jop P Mostert; Jerry S Wolinsky; Fred D Lublin; Bernard Uitdehaag; Gary R Cutter
Journal:  Neurology       Date:  2021-08-25       Impact factor: 11.800

3.  Postural Body Sway as Surrogate Outcome for Myelopathy in Adrenoleukodystrophy.

Authors:  Wouter J C van Ballegoij; Stephanie I W van de Stadt; Irene C Huffnagel; Stephan Kemp; Marjo S van der Knaap; Marc Engelen
Journal:  Front Physiol       Date:  2020-07-17       Impact factor: 4.566

4.  Association of Inflammation and Disability Accrual in Patients With Progressive-Onset Multiple Sclerosis.

Authors:  Jordana Hughes; Vilija Jokubaitis; Alessandra Lugaresi; Raymond Hupperts; Guillermo Izquierdo; Alexandre Prat; Marc Girard; Pierre Duquette; Francois Grand'Maison; Pierre Grammond; Patrizia Sola; Diana Ferraro; Cristina Ramo-Tello; Maria Trojano; Mark Slee; Vahid Shaygannejad; Cavit Boz; Jeanette Lechner-Scott; Vincent Van Pesch; Eugenio Pucci; Claudio Solaro; Freek Verheul; Murat Terzi; Franco Granella; Daniele Spitaleri; Raed Alroughani; Jae-Kwan Jun; Adam Fambiatos; Anneke Van der Walt; Helmut Butzkueven; Tomas Kalincik
Journal:  JAMA Neurol       Date:  2018-11-01       Impact factor: 18.302

Review 5.  Standardization and digitization of clinical data in multiple sclerosis.

Authors:  Marcus D'Souza; Athina Papadopoulou; Christophe Girardey; Ludwig Kappos
Journal:  Nat Rev Neurol       Date:  2021-01-15       Impact factor: 42.937

6.  Effect of Disease-Modifying Therapy on Disability in Relapsing-Remitting Multiple Sclerosis Over 15 Years.

Authors:  Tomas Kalincik; Ibrahima Diouf; Sifat Sharmin; Charles Malpas; Tim Spelman; Dana Horakova; Eva Kubala Havrdova; Maria Trojano; Guillermo Izquierdo; Alessandra Lugaresi; Alexandre Prat; Marc Girard; Pierre Duquette; Pierre Grammond; Vilija Jokubaitis; Anneke van der Walt; Francois Grand'Maison; Patrizia Sola; Diana Ferraro; Vahid Shaygannejad; Raed Alroughani; Raymond Hupperts; Murat Terzi; Cavit Boz; Jeannette Lechner-Scott; Eugenio Pucci; Vincent Van Pesch; Franco Granella; Roberto Bergamaschi; Daniele Spitaleri; Mark Slee; Steve Vucic; Radek Ampapa; Pamela McCombe; Cristina Ramo-Tello; Julie Prevost; Javier Olascoaga; Edgardo Cristiano; Michael Barnett; Maria Laura Saladino; Jose Luis Sanchez-Menoyo; Suzanne Hodgkinson; Csilla Rozsa; Stella Hughes; Fraser Moore; Cameron Shaw; Ernest Butler; Olga Skibina; Orla Gray; Allan Kermode; Tunde Csepany; Bhim Singhal; Neil Shuey; Imre Piroska; Bruce Taylor; Magdolna Simo; Carmen-Adella Sirbu; Attila Sas; Helmut Butzkueven
Journal:  Neurology       Date:  2020-12-28       Impact factor: 9.910

7.  Data Collection in Multiple Sclerosis: The MSDS Approach.

Authors:  Tjalf Ziemssen; Raimar Kern; Isabel Voigt; Rocco Haase
Journal:  Front Neurol       Date:  2020-06-16       Impact factor: 4.003

8.  Reference videos reduce variability of motor dysfunction assessments in multiple sclerosis.

Authors:  Marcus D'Souza; Saskia Steinheimer; Jonas Dorn; Cecily Morrison; Jacques Boisvert; Kristina Kravalis; Jessica Burggraaff; Caspar Ep van Munster; Manuela Diederich; Abigail Sellen; Christian P Kamm; Frank Dahlke; Bernard Mj Uitdehaag; Ludwig Kappos
Journal:  Mult Scler J Exp Transl Clin       Date:  2018-08-09

9.  Disease progression in women with X-linked adrenoleukodystrophy is slow.

Authors:  Irene C Huffnagel; Marcel G W Dijkgraaf; Georges E Janssens; Michel van Weeghel; Björn M van Geel; Bwee Tien Poll-The; Stephan Kemp; Marc Engelen
Journal:  Orphanet J Rare Dis       Date:  2019-02-07       Impact factor: 4.123

10.  Optical coherence tomography shows neuroretinal thinning in myelopathy of adrenoleukodystrophy.

Authors:  Wouter J C van Ballegoij; Sander C Kuijpers; Irene C Huffnagel; Henry C Weinstein; Bwee Tien Poll-The; Marc Engelen; Carlien A M Bennebroek; Frank D Verbraak
Journal:  J Neurol       Date:  2019-11-12       Impact factor: 4.849

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