J Signorovitch1, R Ayyagari2, E Kakkis3. 1. Analysis Group, Inc., Boston, MA, USA. 2. Analysis Group Inc., Boston, MA, USA. 3. Ultragenyx Pharmaceutical Inc., Novato, CA, USA.
Authors: Andrew E Mulberg; Christina Bucci-Rechtweg; Joseph Giuliano; David Jacoby; Franklin K Johnson; Qing Liu; Deborah Marsden; Scott McGoohan; Robert Nelson; Nita Patel; Klaus Romero; Vikram Sinha; Sheela Sitaraman; John Spaltro; Vivian Kessler Journal: Orphanet J Rare Dis Date: 2019-02-08 Impact factor: 4.123