Literature DB >> 27058929

Imprecision Medicine: A One-Size-Fits-Many Approach for Muscle Dystrophy.

Astrid Breitbart1, Charles E Murry2.   

Abstract

There is still no curative treatment for Duchenne muscular dystrophy (DMD). In this issue of Cell Stem Cell, Young et al. (2016) demonstrate a genome editing approach applicable to 60% of DMD patients with CRISPR/Cas9 using one pair of guide RNAs.
Copyright © 2016 Elsevier Inc. All rights reserved.

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Year:  2016        PMID: 27058929     DOI: 10.1016/j.stem.2016.03.004

Source DB:  PubMed          Journal:  Cell Stem Cell        ISSN: 1875-9777            Impact factor:   24.633


  2 in total

1.  Effective regeneration of dystrophic muscle using autologous iPSC-derived progenitors with CRISPR-Cas9 mediated precise correction.

Authors:  Mackenzie Hagan; Muhammad Ashraf; Il-Man Kim; Neal L Weintraub; Yaoliang Tang
Journal:  Med Hypotheses       Date:  2017-11-23       Impact factor: 1.538

2.  Recent developments in Duchenne muscular dystrophy: facts and numbers.

Authors:  Maggie C Walter; Peter Reilich
Journal:  J Cachexia Sarcopenia Muscle       Date:  2017-10       Impact factor: 12.910

  2 in total

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