| Literature DB >> 26899947 |
Tobias Kühl1, Markus Mezger2, Ingrid Hausser3, Lin T Guey4, Rupert Handgretinger2, Leena Bruckner-Tuderman1, Alexander Nyström5.
Abstract
The tissue half-life of proteins largely determines treatment frequency of non-gene-editing-based therapies targeting the cause of genodermatoses. Surprisingly, such knowledge is missing for a vast number of proteins involved in pathologies. The dermal-epidermal junction zone is believed to be a rather static structure, but to our knowledge no detailed analysis of the stability of proteins within this zone has been performed. Here, we addressed the in vivo half-life of collagen type VII using genetic ablation of its expression and therapeutic introduction of exogenous collagen VII in a preclinical model. A similar in vivo stability of collagen VII was observed in the skin, tongue, and esophagus, with a half-life of about 1 month. Collagen VII expressed by intradermally injected mesenchymal stromal cells also exhibited a similar half-life. Our study provides key information needed for the development of protein replacement or cell-based therapies for dystrophic epidermolysis bullosa caused by genetic deficiency of collagen VII. Moreover, by showing what we define as an intermediate half-life of collagen VII, our study challenges the view of the dermal-epidermal junction zone as a static structure with very slow turnover.Entities:
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Year: 2016 PMID: 26899947 DOI: 10.1016/j.jid.2016.02.002
Source DB: PubMed Journal: J Invest Dermatol ISSN: 0022-202X Impact factor: 8.551