Literature DB >> 26898712

Toward the identification of neuroprotective agents: g-scale synthesis, pharmacokinetic evaluation and CNS distribution of (R)-RC-33, a promising SIGMA1 receptor agonist.

Annamaria Marra1, Daniela Rossi1, Luca Pignataro2, Chiara Bigogno3, Annalisa Canta4, Norberto Oggioni4, Alessio Malacrida4, Massimo Corbo5, Guido Cavaletti4, Marco Peviani6, Daniela Curti6, Giulio Dondio3, Simona Collina1.   

Abstract

AIM: Nowadays, there is a great interest in the therapeutic potential of sigma1 receptor ligands for treating different CNS pathologies. Our previous investigations led to identify (R)-RC-33 as a potent and selective S1R agonist.
RESULTS: Herein, we report the gram-scale synthesis, pharmacokinetic profile and CNS distribution of (R)-RC-33 in the mouse to determine the most suitable dosage schedule for in vivo administration. For comparative purposes, the same experiments were also performed with PRE-084, the most widely used S1R agonist commonly in pharmacological experiments. DISCUSSION: (R)-RC-33 shows a similar pharmacokinetic profile and a better CNS distribution when compared with PRE-084.
CONCLUSION: (R)-RC-33 may be a promising candidate for in vivo studies in animal models of neurodegenerative diseases.

Entities:  

Keywords:  CNS distribution; Parkinson's disease; S1R agonist; amyotrophic lateral sclerosis; multiple sclerosis; neurological disorders; pharmacokinetic profile

Mesh:

Substances:

Year:  2016        PMID: 26898712     DOI: 10.4155/fmc.15.191

Source DB:  PubMed          Journal:  Future Med Chem        ISSN: 1756-8919            Impact factor:   3.808


  7 in total

Review 1.  PRE-084 as a tool to uncover potential therapeutic applications for selective sigma-1 receptor activation.

Authors:  Zeinab Y Motawe; Salma S Abdelmaboud; Javier Cuevas; Jerome W Breslin
Journal:  Int J Biochem Cell Biol       Date:  2020-07-12       Impact factor: 5.085

2.  BOPC1 Enantiomers Preparation and HuR Interaction Study. From Molecular Modeling to a Curious DEEP-STD NMR Application.

Authors:  Serena Della Volpe; Roberta Listro; Michela Parafioriti; Marcello Di Giacomo; Daniela Rossi; Francesca Alessandra Ambrosio; Giosuè Costa; Stefano Alcaro; Francesco Ortuso; Anna K H Hirsch; Francesca Vasile; Simona Collina
Journal:  ACS Med Chem Lett       Date:  2020-01-28       Impact factor: 4.345

3.  Discovery of N-cyclobutylaminoethoxyisoxazole derivatives as novel sigma-1 receptor ligands with neurite outgrowth efficacy in cells.

Authors:  Hao Sun; Yun-Jie Wang; Wen-Wen Shi; Fan Yang; Jie Tang; Tao Pang; Li-Fang Yu
Journal:  RSC Adv       Date:  2018-02-14       Impact factor: 4.036

4.  PEG 400/Cerium Ammonium Nitrate Combined with Microwave-Assisted Synthesis for Rapid Access to Beta-Amino Ketones. An Easy-to-Use Protocol for Discovering New Hit Compounds.

Authors:  Giacomo Rossino; Maria Valeria Raimondi; Marta Rui; Marcello Di Giacomo; Daniela Rossi; Simona Collina
Journal:  Molecules       Date:  2018-03-28       Impact factor: 4.411

5.  Anti-Inflammatory, Antioxidant and Crystallographic Studies of N-Palmitoyl-ethanol Amine (PEA) Derivatives.

Authors:  Carmela Saturnino; Ada Popolo; Anna Ramunno; Simona Adesso; Michela Pecoraro; Maria Rosaria Plutino; Silvia Rizzato; Alberto Albinati; Stefania Marzocco; Marina Sala; Domenico Iacopetta; Maria Stefania Sinicropi
Journal:  Molecules       Date:  2017-04-11       Impact factor: 4.411

6.  Repurposing the Antiplatelet Agent Ticlopidine to Counteract the Acute Phase of ER Stress Condition: An Opportunity for Fighting Coronavirus Infections and Cancer.

Authors:  Anna Tesei; Michela Cortesi; Martina Bedeschi; Noemi Marino; Giacomo Rossino; Roberta Listro; Daniela Rossi; Pasquale Linciano; Simona Collina
Journal:  Molecules       Date:  2022-07-06       Impact factor: 4.927

7.  Safe and Efficient Sigma1 Ligand: A Potential Drug Candidate for Multiple Sclerosis.

Authors:  Bénédicte Oxombre; Fahima Madouri; Anne-Sophie Journé; Séverine Ravez; Eloise Woitrain; Pascal Odou; Nathalie Duhal; Sandro Ninni; David Montaigne; Nadira Delhem; Patrick Vermersch; Patricia Melnyk
Journal:  Int J Mol Sci       Date:  2022-10-06       Impact factor: 6.208

  7 in total

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