Literature DB >> 26876592

Complete response to gemtuzumab ozogamicin in a patient with refractory mast cell leukemia.

I Alvarez-Twose1, P Martínez-Barranco2, J Gotlib3, A García-Montero4, J M Morgado1, M Jara-Acevedo4, J D Merker5, F J Peñalver2, A Matito1, Y Hou5, L Sánchez-Muñoz1, A Mayado4, M Mollejo6, L Escribano4, A Orfao4.   

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Year:  2016        PMID: 26876592     DOI: 10.1038/leu.2016.30

Source DB:  PubMed          Journal:  Leukemia        ISSN: 0887-6924            Impact factor:   11.528


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  12 in total

1.  Randomized trial of two schedules of low-dose gemtuzumab ozogamicin as induction monotherapy for newly diagnosed acute myeloid leukaemia in older patients not considered candidates for intensive chemotherapy. A phase II study of the EORTC and GIMEMA leukaemia groups (AML-19).

Authors:  Sergio Amadori; Stefan Suciu; Dominik Selleslag; Roberto Stasi; Giuliana Alimena; Liliana Baila; Vittorio Rizzoli; Erika Borlenghi; Gianluca Gaidano; Domenico Magro; Giuseppe Torelli; Petra Muus; Adriano Venditti; Emma Cacciola; Francesco Lauria; Marco Vignetti; Theo de Witte
Journal:  Br J Haematol       Date:  2010-03-08       Impact factor: 6.998

2.  Hematopoietic stem-cell transplantation for advanced systemic mastocytosis.

Authors:  Celalettin Ustun; Andreas Reiter; Bart L Scott; Ryotaro Nakamura; Gandhi Damaj; Sebastian Kreil; Ryan Shanley; William J Hogan; Miguel-Angel Perales; Tsiporah Shore; Herrad Baurmann; Robert Stuart; Bernd Gruhn; Michael Doubek; Jack W Hsu; Eleni Tholouli; Tanja Gromke; Lucy A Godley; Livio Pagano; Andrew Gilman; Eva Maria Wagner; Tor Shwayder; Martin Bornhäuser; Esperanza B Papadopoulos; Alexandra Böhm; Gregory Vercellotti; Maria Teresa Van Lint; Christoph Schmid; Werner Rabitsch; Vinod Pullarkat; Faezeh Legrand; Ibrahim Yakoub-Agha; Wael Saber; John Barrett; Olivier Hermine; Hans Hagglund; Wolfgang R Sperr; Uday Popat; Edwin P Alyea; Steven Devine; H Joachim Deeg; Daniel Weisdorf; Cem Akin; Peter Valent
Journal:  J Clin Oncol       Date:  2014-08-25       Impact factor: 44.544

Review 3.  Aggressive systemic mastocytosis and related mast cell disorders: current treatment options and proposed response criteria.

Authors:  Peter Valent; Cem Akin; Wolfgang R Sperr; Luis Escribano; Michel Arock; Hans-Peter Horny; John M Bennett; Dean D Metcalfe
Journal:  Leuk Res       Date:  2003-07       Impact factor: 3.156

4.  Effects of the CD33-targeted drug gemtuzumab ozogamicin (Mylotarg) on growth and mediator secretion in human mast cells and blood basophils.

Authors:  Maria-Theresa Krauth; Alexandra Böhm; Hermine Agis; Karoline Sonneck; Puchit Samorapoompichit; Stefan Florian; Karl Sotlar; Peter Valent
Journal:  Exp Hematol       Date:  2007-01       Impact factor: 3.084

Review 5.  Diagnostic criteria and classification of mastocytosis: a consensus proposal.

Authors:  P Valent; H P Horny; L Escribano; B J Longley; C Y Li; L B Schwartz; G Marone; R Nuñez; C Akin; K Sotlar; W R Sperr; K Wolff; R D Brunning; R M Parwaresch; K F Austen; K Lennert; D D Metcalfe; J W Vardiman; J M Bennett
Journal:  Leuk Res       Date:  2001-07       Impact factor: 3.156

6.  A case of mast cell leukaemia with exon 9 KIT mutation and good response to imatinib.

Authors:  Andrzej Mital; Anna Piskorz; Krzysztof Lewandowski; Bartosz Wasąg; Janusz Limon; Andrzej Hellmann
Journal:  Eur J Haematol       Date:  2011-04-07       Impact factor: 2.997

Review 7.  Refined diagnostic criteria and classification of mast cell leukemia (MCL) and myelomastocytic leukemia (MML): a consensus proposal.

Authors:  P Valent; K Sotlar; W R Sperr; L Escribano; S Yavuz; A Reiter; T I George; H C Kluin-Nelemans; O Hermine; J H Butterfield; H Hägglund; C Ustun; J L Hornick; M Triggiani; D Radia; C Akin; K Hartmann; J Gotlib; L B Schwartz; S Verstovsek; A Orfao; D D Metcalfe; M Arock; H-P Horny
Journal:  Ann Oncol       Date:  2014-03-27       Impact factor: 32.976

8.  International Working Group-Myeloproliferative Neoplasms Research and Treatment (IWG-MRT) & European Competence Network on Mastocytosis (ECNM) consensus response criteria in advanced systemic mastocytosis.

Authors:  Jason Gotlib; Animesh Pardanani; Cem Akin; Andreas Reiter; Tracy George; Olivier Hermine; Hanneke Kluin-Nelemans; Karin Hartmann; Wolfgang R Sperr; Knut Brockow; Lawrence B Schwartz; Alberto Orfao; Daniel J Deangelo; Michel Arock; Karl Sotlar; Hans-Peter Horny; Dean D Metcalfe; Luis Escribano; Srdan Verstovsek; Ayalew Tefferi; Peter Valent
Journal:  Blood       Date:  2013-01-16       Impact factor: 22.113

Review 9.  Standards and standardization in mastocytosis: consensus statements on diagnostics, treatment recommendations and response criteria.

Authors:  P Valent; C Akin; L Escribano; M Födinger; K Hartmann; K Brockow; M Castells; W R Sperr; H C Kluin-Nelemans; N A T Hamdy; O Lortholary; J Robyn; J van Doormaal; K Sotlar; A W Hauswirth; M Arock; O Hermine; A Hellmann; M Triggiani; M Niedoszytko; L B Schwartz; A Orfao; H-P Horny; D D Metcalfe
Journal:  Eur J Clin Invest       Date:  2007-06       Impact factor: 4.686

10.  Genomic and epigenomic landscapes of adult de novo acute myeloid leukemia.

Authors:  Timothy J Ley; Christopher Miller; Li Ding; Benjamin J Raphael; Andrew J Mungall; A Gordon Robertson; Katherine Hoadley; Timothy J Triche; Peter W Laird; Jack D Baty; Lucinda L Fulton; Robert Fulton; Sharon E Heath; Joelle Kalicki-Veizer; Cyriac Kandoth; Jeffery M Klco; Daniel C Koboldt; Krishna-Latha Kanchi; Shashikant Kulkarni; Tamara L Lamprecht; David E Larson; Ling Lin; Charles Lu; Michael D McLellan; Joshua F McMichael; Jacqueline Payton; Heather Schmidt; David H Spencer; Michael H Tomasson; John W Wallis; Lukas D Wartman; Mark A Watson; John Welch; Michael C Wendl; Adrian Ally; Miruna Balasundaram; Inanc Birol; Yaron Butterfield; Readman Chiu; Andy Chu; Eric Chuah; Hye-Jung Chun; Richard Corbett; Noreen Dhalla; Ranabir Guin; An He; Carrie Hirst; Martin Hirst; Robert A Holt; Steven Jones; Aly Karsan; Darlene Lee; Haiyan I Li; Marco A Marra; Michael Mayo; Richard A Moore; Karen Mungall; Jeremy Parker; Erin Pleasance; Patrick Plettner; Jacquie Schein; Dominik Stoll; Lucas Swanson; Angela Tam; Nina Thiessen; Richard Varhol; Natasja Wye; Yongjun Zhao; Stacey Gabriel; Gad Getz; Carrie Sougnez; Lihua Zou; Mark D M Leiserson; Fabio Vandin; Hsin-Ta Wu; Frederick Applebaum; Stephen B Baylin; Rehan Akbani; Bradley M Broom; Ken Chen; Thomas C Motter; Khanh Nguyen; John N Weinstein; Nianziang Zhang; Martin L Ferguson; Christopher Adams; Aaron Black; Jay Bowen; Julie Gastier-Foster; Thomas Grossman; Tara Lichtenberg; Lisa Wise; Tanja Davidsen; John A Demchok; Kenna R Mills Shaw; Margi Sheth; Heidi J Sofia; Liming Yang; James R Downing; Greg Eley
Journal:  N Engl J Med       Date:  2013-05-01       Impact factor: 91.245

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  10 in total

1.  Trispecific killer engager CD16xIL15xCD33 potently induces NK cell activation and cytotoxicity against neoplastic mast cells.

Authors:  Hyun Don Yun; Martin Felices; Daniel A Vallera; Peter Hinderlie; Sarah Cooley; Michel Arock; Jason Gotlib; Celalettin Ustun; Jeffrey S Miller
Journal:  Blood Adv       Date:  2018-07-10

Review 2.  Clinical Validation of KIT Inhibition in Advanced Systemic Mastocytosis.

Authors:  John H Baird; Jason Gotlib
Journal:  Curr Hematol Malig Rep       Date:  2018-10       Impact factor: 3.952

Review 3.  Mastocytosis: 2016 updated WHO classification and novel emerging treatment concepts.

Authors:  Peter Valent; Cem Akin; Dean D Metcalfe
Journal:  Blood       Date:  2016-12-28       Impact factor: 22.113

Review 4.  Advances in the Classification and Treatment of Mastocytosis: Current Status and Outlook toward the Future.

Authors:  Peter Valent; Cem Akin; Karin Hartmann; Gunnar Nilsson; Andreas Reiter; Olivier Hermine; Karl Sotlar; Wolfgang R Sperr; Luis Escribano; Tracy I George; Hanneke C Kluin-Nelemans; Celalettin Ustun; Massimo Triggiani; Knut Brockow; Jason Gotlib; Alberto Orfao; Lawrence B Schwartz; Sigurd Broesby-Olsen; Carsten Bindslev-Jensen; Petri T Kovanen; Stephen J Galli; K Frank Austen; Daniel A Arber; Hans-Peter Horny; Michel Arock; Dean D Metcalfe
Journal:  Cancer Res       Date:  2017-03-02       Impact factor: 12.701

5.  The clinical and molecular diversity of mast cell leukemia with or without associated hematologic neoplasm.

Authors:  Mohamad Jawhar; Juliana Schwaab; Manja Meggendorfer; Nicole Naumann; Hans-Peter Horny; Karl Sotlar; Torsten Haferlach; Karla Schmitt; Alice Fabarius; Peter Valent; Wolf-Karsten Hofmann; Nicholas C P Cross; Georgia Metzgeroth; Andreas Reiter
Journal:  Haematologica       Date:  2017-03-02       Impact factor: 9.941

Review 6.  Preclinical human models and emerging therapeutics for advanced systemic mastocytosis.

Authors:  Michel Arock; Ghaith Wedeh; Gregor Hoermann; Siham Bibi; Cem Akin; Barbara Peter; Karoline V Gleixner; Karin Hartmann; Joseph H Butterfield; Dean D Metcalfe; Peter Valent
Journal:  Haematologica       Date:  2018-07-05       Impact factor: 9.941

7.  Bone Marrow Mast Cell Antibody-Targetable Cell Surface Protein Expression Profiles in Systemic Mastocytosis.

Authors:  Noelia Dasilva-Freire; Andrea Mayado; Cristina Teodosio; María Jara-Acevedo; Iván Álvarez-Twose; Almudena Matito; Laura Sánchez-Muñoz; Carolina Caldas; Ana Henriques; Javier I Muñoz-González; Andrés C García-Montero; J Ignacio Sánchez-Gallego; Luis Escribano; Alberto Orfao
Journal:  Int J Mol Sci       Date:  2019-01-28       Impact factor: 5.923

8.  Identification of a leukemia-initiating stem cell in human mast cell leukemia.

Authors:  Gregor Eisenwort; Irina Sadovnik; Juliana Schwaab; Mohamad Jawhar; Alexandra Keller; Gabriele Stefanzl; Daniela Berger; Katharina Blatt; Gregor Hoermann; Martin Bilban; Michael Willmann; Christiana Winding; Wolfgang R Sperr; Michel Arock; Thomas Rülicke; Andreas Reiter; Peter Valent
Journal:  Leukemia       Date:  2019-04-05       Impact factor: 11.528

Review 9.  Updated Diagnostic Criteria and Classification of Mast Cell Disorders: A Consensus Proposal.

Authors:  Peter Valent; Cem Akin; Karin Hartmann; Ivan Alvarez-Twose; Knut Brockow; Olivier Hermine; Marek Niedoszytko; Juliana Schwaab; Jonathan J Lyons; Melody C Carter; Hanneke Oude Elberink; Joseph H Butterfield; Tracy I George; Georg Greiner; Celalettin Ustun; Patrizia Bonadonna; Karl Sotlar; Gunnar Nilsson; Mohamad Jawhar; Frank Siebenhaar; Sigurd Broesby-Olsen; Selim Yavuz; Roberta Zanotti; Magdalena Lange; Boguslaw Nedoszytko; Gregor Hoermann; Mariana Castells; Deepti H Radia; Javier I Muñoz-Gonzalez; Wolfgang R Sperr; Massimo Triggiani; Hanneke C Kluin-Nelemans; Stephen J Galli; Lawrence B Schwartz; Andreas Reiter; Alberto Orfao; Jason Gotlib; Michel Arock; Hans-Peter Horny; Dean D Metcalfe
Journal:  Hemasphere       Date:  2021-10-13

Review 10.  Recent advances in the understanding and therapeutic management of mastocytosis.

Authors:  Julien Rossignol; Laura Polivka; Leila Maouche-Chrétien; Laurent Frenzel; Patrice Dubreuil; Olivier Hermine
Journal:  F1000Res       Date:  2019-11-22
  10 in total

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