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Review 1. Lumacaftor/Ivacaftor: A Review in Cystic Fibrosis.

Authors: Emma D Deeks
Journal: Drugs Date: 2016-08 Impact factor: 9.546

Review 2. Pharmacological analysis of CFTR variants of cystic fibrosis using stem cell-derived organoids.

Authors: Kevin G Chen; Pingyu Zhong; Wei Zheng; Jeffrey M Beekman
Journal: Drug Discov Today Date: 2019-06-04 Impact factor: 7.851

3. The CFTR Corrector, VX-809 (Lumacaftor), Rescues ABCA4 Trafficking Mutants: a Potential Treatment for Stargardt Disease.

Authors: Qiangni Liu; Inna Sabirzhanova; Emily Anne Smith Bergbower; Murali Yanda; William G Guggino; Liudmila Cebotaru
Journal: Cell Physiol Biochem Date: 2019

4. Restoration of R117H CFTR folding and function in human airway cells through combination treatment with VX-809 and VX-770.

Authors: Martina Gentzsch; Hong Y Ren; Scott A Houck; Nancy L Quinney; Deborah M Cholon; Pattarawut Sopha; Imron G Chaudhry; Jhuma Das; Nikolay V Dokholyan; Scott H Randell; Douglas M Cyr
Journal: Am J Physiol Lung Cell Mol Physiol Date: 2016-07-08 Impact factor: 5.464

5. Efficacy of lumacaftor-ivacaftor for the treatment of cystic fibrosis patients homozygous for the F508del-CFTR mutation.

Authors: Deborah M Cholon; Charles R Esther; Martina Gentzsch
Journal: Expert Rev Precis Med Drug Dev Date: 2016-04-22

Review 6. Recent Developments in mRNA-Based Protein Supplementation Therapy to Target Lung Diseases.

Authors: Itishri Sahu; A K M Ashiqul Haque; Brian Weidensee; Petra Weinmann; Michael S D Kormann
Journal: Mol Ther Date: 2019-03-06 Impact factor: 11.454

Review 7. Pharmacological targeting of endoplasmic reticulum stress in disease.

Authors: Stefan J Marciniak; Joseph E Chambers; David Ron
Journal: Nat Rev Drug Discov Date: 2021-10-26 Impact factor: 84.694

8. A computational essential dynamics approach to investigate structural influences of ligand binding on Papain like protease from SARS-CoV-2.

Authors: Ekampreet Singh; Rajat Kumar Jha; Rameez Jabeer Khan; Ankit Kumar; Monika Jain; Jayaraman Muthukumaran; Amit Kumar Singh
Journal: Comput Biol Chem Date: 2022-06-28 Impact factor: 3.737

9. Rescue of CFTR NBD2 mutants N1303K and S1235R is influenced by the functioning of the autophagosome.

Authors: Qiangni Liu; Inna Sabirzhanova; Murali K Yanda; Emily A S Bergbower; Clément Boinot; William B Guggino; Liudmila Cebotaru
Journal: J Cyst Fibros Date: 2018-06-20 Impact factor: 5.482

Review 10. A Review of Trikafta: Triple Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) Modulator Therapy.

Authors: Anas Zaher; Jude ElSaygh; Dalal Elsori; Hassan ElSaygh; Abdulsabar Sanni
Journal: Cureus Date: 2021-07-03