Literature DB >> 26464296

Preclinical Pharmacokinetics Evaluation of Anti-heparin-binding EGF-like Growth Factor (HB-EGF) Monoclonal Antibody Using Cynomolgus Monkeys via (89)Zr-immuno-PET Study and the Determination of Drug Concentrations in Serum and Cerebrospinal Fluid.

Noriyuki Kasai1, Maiko Adachi2, Kazuya Yamano3.   

Abstract

PURPOSE: Heparin-binding EGF-like growth factor (HB-EGF) is a member of the EGF family and is an important therapeutic target in some types of human cancers. KHK2866 is a humanized anti-HB-EGF monoclonal antibody IgG that neutralizes HB-EGF activity by inhibiting the binding of HB-EGF to its receptors. The phase I study of KHK2866 was discontinued because of neuropsychiatric toxicity. In this study, the pharmacokinetics of KHK2866 was evaluated by (89)Zr-immuno-PET study and the determination of drug concentrations in serum and cerebrospinal fluid using cynomolgus monkeys was performed in order to predict neurotoxicity in a reverse-translational manner.
METHODS: KHK2866 was radiolabeled with (89)Zr for preclinical evaluations in normal cynomolgus monkeys and its distribution was analyzed. Furthermore, as a separate study, KHK2866 concentrations in serum and cerebrospinal fluid were determined after administration of a single dose.
RESULTS: PET studies with monkeys revealed (89)Zr-KHK2866 accumulation in the liver, spleen and joints of multiple parts, but not in brain. In addition, the pharmacokinetic analyses in serum and CSF demonstrated a low penetration of KHK2866 into the brain.
CONCLUSIONS: These studies indicate the difficulty of prediction for neuropsychiatric toxicity of monoclonal antibodies in human by means of pharmacokinetic evaluations using cynomolgus monkeys.

Entities:  

Keywords:  89Zr-immuno-PET; HB-EGF; antibody; pharmacokinetics

Mesh:

Substances:

Year:  2015        PMID: 26464296     DOI: 10.1007/s11095-015-1803-2

Source DB:  PubMed          Journal:  Pharm Res        ISSN: 0724-8741            Impact factor:   4.200


  22 in total

1.  Immunohistochemical distribution of CD9, heparin binding epidermal growth factor-like growth factor, and integrin alpha3beta1 in normal human tissues.

Authors:  Y Nakamura; K Handa; R Iwamoto; T Tsukamoto; M Takahasi; E Mekada
Journal:  J Histochem Cytochem       Date:  2001-04       Impact factor: 2.479

2.  Biodistribution of 89Zr-trastuzumab and PET imaging of HER2-positive lesions in patients with metastatic breast cancer.

Authors:  E C Dijkers; T H Oude Munnink; J G Kosterink; A H Brouwers; P L Jager; J R de Jong; G A van Dongen; C P Schröder; M N Lub-de Hooge; E G de Vries
Journal:  Clin Pharmacol Ther       Date:  2010-03-31       Impact factor: 6.875

3.  A novel anti-human HB-EGF monoclonal antibody with multiple antitumor mechanisms against ovarian cancer cells.

Authors:  Shingo Miyamoto; Ryo Iwamoto; Akiko Furuya; Kumiko Takahashi; Yuka Sasaki; Hiroshi Ando; Fusanori Yotsumoto; Tomoko Yoneda; Miki Hamaoka; Hiroshi Yagi; Takuya Murakami; Sayaka Hori; Kenya Shitara; Eisuke Mekada
Journal:  Clin Cancer Res       Date:  2011-09-14       Impact factor: 12.531

4.  Macromolecular permeability across the blood-nerve and blood-brain barriers.

Authors:  J F Poduslo; G L Curran; C T Berg
Journal:  Proc Natl Acad Sci U S A       Date:  1994-06-07       Impact factor: 11.205

Review 5.  Membrane-anchored growth factors, the epidermal growth factor family: beyond receptor ligands.

Authors:  Shigeki Higashiyama; Hidehiko Iwabuki; Chie Morimoto; Miki Hieda; Hirofumi Inoue; Natsuki Matsushita
Journal:  Cancer Sci       Date:  2008-02       Impact factor: 6.716

6.  Validation of HB-EGF and amphiregulin as targets for human cancer therapy.

Authors:  Fusanori Yotsumoto; Hiroshi Yagi; Satoshi O Suzuki; Eiji Oki; Hiroshi Tsujioka; Touru Hachisuga; Kenzo Sonoda; Tatsuhiko Kawarabayashi; Eisuke Mekada; Shingo Miyamoto
Journal:  Biochem Biophys Res Commun       Date:  2007-11-20       Impact factor: 3.575

Review 7.  Drug targeting to the brain.

Authors:  William M Pardridge
Journal:  Pharm Res       Date:  2007-06-07       Impact factor: 4.200

8.  Rituximab levels in cerebrospinal fluid of patients with neurological autoimmune disorders.

Authors:  H F Petereit; A Rubbert-Roth
Journal:  Mult Scler       Date:  2008-10-29       Impact factor: 6.312

9.  Heparin-binding EGF-like growth factor: characterization of rat and mouse cDNA clones, protein domain conservation across species, and transcript expression in tissues.

Authors:  J A Abraham; D Damm; A Bajardi; J Miller; M Klagsbrun; R A Ezekowitz
Journal:  Biochem Biophys Res Commun       Date:  1993-01-15       Impact factor: 3.575

10.  89Zr immuno-PET: comprehensive procedures for the production of 89Zr-labeled monoclonal antibodies.

Authors:  Iris Verel; Gerard W M Visser; Ronald Boellaard; Marijke Stigter-van Walsum; Gordon B Snow; Guus A M S van Dongen
Journal:  J Nucl Med       Date:  2003-08       Impact factor: 10.057

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  3 in total

Review 1.  Role of Heparin-Binding Epidermal Growth Factor-Like Growth Factor in Oxidative Stress-Associated Metabolic Diseases.

Authors:  Seonwook Kim; Venkateswaran Subramanian; Ahmed Abdel-Latif; Sangderk Lee
Journal:  Metab Syndr Relat Disord       Date:  2020-02-20       Impact factor: 1.894

2.  BK-UM in patients with recurrent ovarian cancer or peritoneal cancer: a first-in-human phase-I study.

Authors:  Shingo Miyamoto; Fusanori Yotsumoto; Taeko Ueda; Tatsuya Fukami; Ayako Sanui; Kohei Miyata; Sung Ouk Nam; Satoshi Fukagawa; Takahiro Katsuta; Miyako Maehara; Haruhiko Kondo; Daisuke Miyahara; Kyoko Shirota; Toshiyuki Yoshizato; Masahide Kuroki; Hiroaki Nishikawa; Keijiro Saku; Yoshio Tsuboi; Kenji Ishitsuka; Yasushi Takamatsu; Kazuo Tamura; Akira Matsunaga; Toru Hachisuga; Shinsuke Nishino; Takashi Odawara; Kazuhiro Maeda; Sadao Manabe; Toyokazu Ishikawa; Yoshinobu Okuno; Minako Ohishi; Tomoya Hikita; Hiroto Mizushima; Ryo Iwamoto; Eisuke Mekada
Journal:  BMC Cancer       Date:  2017-01-31       Impact factor: 4.430

3.  Targeting hepatic heparin-binding EGF-like growth factor (HB-EGF) induces anti-hyperlipidemia leading to reduction of angiotensin II-induced aneurysm development.

Authors:  Seonwook Kim; Lihua Yang; Seongu Kim; Richard G Lee; Mark J Graham; Judith A Berliner; Aldons J Lusis; Lei Cai; Ryan E Temel; Debra L Rateri; Sangderk Lee
Journal:  PLoS One       Date:  2017-08-09       Impact factor: 3.240

  3 in total

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