Literature DB >> 26416003

Dyslipidaemia: Promising new therapy for lysosomal acid lipase deficiency.

Irene Fernández Ruiz.   

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Year:  2015        PMID: 26416003     DOI: 10.1038/nrcardio.2015.154

Source DB:  PubMed          Journal:  Nat Rev Cardiol        ISSN: 1759-5002            Impact factor:   32.419


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  1 in total

1.  A Phase 3 Trial of Sebelipase Alfa in Lysosomal Acid Lipase Deficiency.

Authors:  Barbara K Burton; Manisha Balwani; François Feillet; Ivo Barić; T Andrew Burrow; Carmen Camarena Grande; Mahmut Coker; Alejandra Consuelo-Sánchez; Patrick Deegan; Maja Di Rocco; Gregory M Enns; Richard Erbe; Fatih Ezgu; Can Ficicioglu; Katryn N Furuya; John Kane; Christina Laukaitis; Eugen Mengel; Edward G Neilan; Scott Nightingale; Heidi Peters; Maurizio Scarpa; K Otfried Schwab; Vratislav Smolka; Vassili Valayannopoulos; Marnie Wood; Zachary Goodman; Yijun Yang; Stephen Eckert; Sandra Rojas-Caro; Anthony G Quinn
Journal:  N Engl J Med       Date:  2015-09-10       Impact factor: 91.245

  1 in total

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