Literature DB >> 26358973

Biotinidase deficiency should be considered in individuals exhibiting myelopathy with or without and vision loss.

Barry Wolf1.   

Abstract

Multiple symptomatic children with biotinidase deficiency have exhibited spastic para- or tetraplegia due to myelopathy with and without vision loss. Although this has been a feature of what has been designated as delayed onset-biotinidase deficiency, myelopathy is likely also on the continuum of clinical features seen in younger children who have had these features attributed to dysfunction of the upper brain rather than of the spinal cord. Because many countries are still not screening their newborns for biotinidase deficiency, the disorder should be included in the differential diagnosis of individuals with myelopathic symptoms. Many of these children have gone weeks to months before they were correctly diagnosed with biotinidase deficiency. Rapid recognition that a child with myelopathy with and without vision loss has biotinidase deficiency will undoubtedly facilitate prompt treatment, increase the possibility of complete recovery and avoid potential residual permanent neurological damage. Newborn screening for biotinidase deficiency would avoid the delay in the diagnosis and treatment of individuals who otherwise may present with myelopathic or other neurological symptoms.
Copyright © 2015 Elsevier Inc. All rights reserved.

Entities:  

Keywords:  Biotin-responsive; Biotinidase; Biotinidase deficiency; Myelopathy; Scotoma; Spastic paraplegia; Spastic tetraplegia; Spinal disorder; Vision loss

Mesh:

Year:  2015        PMID: 26358973     DOI: 10.1016/j.ymgme.2015.08.012

Source DB:  PubMed          Journal:  Mol Genet Metab        ISSN: 1096-7192            Impact factor:   4.797


  14 in total

1.  "Think metabolic" in adults with diagnostic challenges: Biotinidase deficiency as a paradigm disorder.

Authors:  Barry Wolf
Journal:  Neurol Clin Pract       Date:  2017-12

2.  Irreversibility of Symptoms with Biotin Therapy in an Adult with Profound Biotinidase Deficiency.

Authors:  Patrick Ferreira; Alicia Chan; Barry Wolf
Journal:  JIMD Rep       Date:  2017-02-21

Review 3.  Treatable Genetic Metabolic Epilepsies.

Authors:  Lama Assi; Youssef Saklawi; Pascale E Karam; Makram Obeid
Journal:  Curr Treat Options Neurol       Date:  2017-09       Impact factor: 3.598

4.  High Incidence of Partial Biotinidase Deficiency in the First 3 Years of a Regional Newborn Screening Program in Italy.

Authors:  Daniela Semeraro; Sara Verrocchio; Giulia Di Dalmazi; Claudia Rossi; Damiana Pieragostino; Ilaria Cicalini; Rossella Ferrante; Silvia Di Michele; Liborio Stuppia; Cristiano Rizzo; Francesca Romana Lepri; Antonio Novelli; Carlo Dionisi-Vici; Vincenzo De Laurenzi; Ines Bucci
Journal:  Int J Environ Res Public Health       Date:  2022-07-02       Impact factor: 4.614

5.  Developmental window of sensorineural deafness in biotinidase-deficient mice.

Authors:  Kathleen June Maheras; Kirit Pindolia; Barry Wolf; Alexander Gow
Journal:  J Inherit Metab Dis       Date:  2017-05-17       Impact factor: 4.982

6.  Laboratory diagnosis of biotinidase deficiency, 2017 update: a technical standard and guideline of the American College of Medical Genetics and Genomics.

Authors:  Erin T Strovel; Tina M Cowan; Anna I Scott; Barry Wolf
Journal:  Genet Med       Date:  2017-07-05       Impact factor: 8.822

7.  Any individual with multiple sclerosis who markedly improves neurologically with high-doses of biotin should be evaluated for biotinidase deficiency.

Authors:  Barry Wolf
Journal:  Mult Scler J Exp Transl Clin       Date:  2020-04-29

8.  Subacute Myelopathy: Think Beyond Neuromyelitis Optica Spectrum Disorder.

Authors:  Ananthanarayanan Kasinathan; Renu Suthar; Sameer Vyas; Arushi Gahlot Saini; Naveen Sankhyan; Savita Attri
Journal:  Ann Indian Acad Neurol       Date:  2019-10-25       Impact factor: 1.383

Review 9.  Childhood-onset hereditary spastic paraplegia and its treatable mimics.

Authors:  Darius Ebrahimi-Fakhari; Afshin Saffari; Phillip L Pearl
Journal:  Mol Genet Metab       Date:  2021-06-24       Impact factor: 4.797

10.  Neonatal screening for biotinidase deficiency: A 30-year single center experience.

Authors:  Francesco Porta; Veronica Pagliardini; Isabella Celestino; Enza Pavanello; Severo Pagliardini; Ornella Guardamagna; Alberto Ponzone; Marco Spada
Journal:  Mol Genet Metab Rep       Date:  2017-09-20
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