Literature DB >> 26341251

Risk factors for relapse and long-term outcome in steroid-dependent nephrotic syndrome treated with rituximab.

Koichi Kamei1, Masao Ogura1, Mai Sato1, Mayumi Sako2, Kazumoto Iijima3, Shuichi Ito4,5.   

Abstract

BACKGROUND: Rituximab (RTX) is known to be effective for the treatment of refractory steroid-dependent nephrotic syndrome (SDNS). However, there are insufficient data on the risk factors for relapse and long-term outcome after RTX treatment.
METHODS: We administered a single dose of RTX to patients with refractory SDNS from November 2007 to December 2013 and continued with immunosuppressants. The risk factors for early relapse and long-term outcome were analyzed.
RESULTS: Eighty-one patients were included and the observation period was 13-90 months. Seventy-six patients (94 %) discontinued steroids. Median duration of B-cell depletion was 160 days and 50 % relapse-free survival was 482 days. In multivariate analyses, only a history of steroid-resistant nephrotic syndrome (SRNS) was a statistically significant risk factor (hazard ratio, 2.44; p = 0.048). Fifty percent relapse-free survival in patients without a history of SRNS was 615 days, longer than that of patients with a history of SRNS (393 days) (p=0.005) [corrected]. Fifty-one patients (63 %) received additional RTX treatments for relapses. At last observation, patients using calcineurin inhibitors decreased from 89 % to 23 %, and 12 patients (15 %) discontinued immunosuppressants.
CONCLUSIONS: Rituximab treatment followed by immunosuppressants is an effective option for patients with SDNS, although a history of SRNS is a risk factor for early relapse.

Entities:  

Keywords:  B-cell; Children; Rituximab; Steroid-dependent nephrotic syndrome; Steroid-resistant nephrotic syndrome

Mesh:

Substances:

Year:  2015        PMID: 26341251     DOI: 10.1007/s00467-015-3197-0

Source DB:  PubMed          Journal:  Pediatr Nephrol        ISSN: 0931-041X            Impact factor:   3.714


  23 in total

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2.  Short-term efficacy of rituximab versus tacrolimus in steroid-dependent nephrotic syndrome.

Authors:  Aditi Sinha; Arvind Bagga; Ashima Gulati; Pankaj Hari
Journal:  Pediatr Nephrol       Date:  2011-09-16       Impact factor: 3.714

3.  Rituximab efficiency in children with steroid-dependent nephrotic syndrome.

Authors:  Anne-Laure Sellier-Leclerc; Marie-Alice Macher; Chantal Loirat; Valérie Guérin; Hervé Watier; Michel Peuchmaur; Véronique Baudouin; Georges Deschênes
Journal:  Pediatr Nephrol       Date:  2010-03-18       Impact factor: 3.714

4.  Rituximab in steroid-dependent or frequently relapsing idiopathic nephrotic syndrome.

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Journal:  J Am Soc Nephrol       Date:  2014-01-30       Impact factor: 10.121

5.  Single dose of rituximab for refractory steroid-dependent nephrotic syndrome in children.

Authors:  Koichi Kamei; Shuichi Ito; Kandai Nozu; Shuichiro Fujinaga; Makiko Nakayama; Mayumi Sako; Mari Saito; Maki Yoneko; Kazumoto Iijima
Journal:  Pediatr Nephrol       Date:  2009-05-07       Impact factor: 3.714

6.  Progressive multifocal leukoencephalopathy after rituximab therapy in HIV-negative patients: a report of 57 cases from the Research on Adverse Drug Events and Reports project.

Authors:  Kenneth R Carson; Andrew M Evens; Elizabeth A Richey; Thomas M Habermann; Daniele Focosi; John F Seymour; Jacob Laubach; Susie D Bawn; Leo I Gordon; Jane N Winter; Richard R Furman; Julie M Vose; Andrew D Zelenetz; Ronac Mamtani; Dennis W Raisch; Gary W Dorshimer; Steven T Rosen; Kenji Muro; Numa R Gottardi-Littell; Robert L Talley; Oliver Sartor; David Green; Eugene O Major; Charles L Bennett
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7.  Rituximab is a safe and effective long-term treatment for children with steroid and calcineurin inhibitor-dependent idiopathic nephrotic syndrome.

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Journal:  Kidney Int       Date:  2013-06-05       Impact factor: 10.612

Review 8.  Rituximab (B-cell depleting antibody) associated lung injury (RALI): a pediatric case and systematic review of the literature.

Authors:  Martin Bitzan; Mark Anselmo; Lucy Carpineta
Journal:  Pediatr Pulmonol       Date:  2009-09

9.  Single infusion of rituximab for persistent steroid-dependent minimal-change nephrotic syndrome after long-term cyclosporine.

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10.  Atypical Pneumocystis jiroveci pneumonia with multiple nodular granulomas after rituximab for refractory nephrotic syndrome.

Authors:  Mai Sato; Shuichi Ito; Masao Ogura; Koichi Kamei; Isao Miyairi; Ippei Miyata; Masataka Higuchi; Kentaro Matsuoka
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  12 in total

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2.  Long-term outcome of childhood-onset complicated nephrotic syndrome after a multicenter, double-blind, randomized, placebo-controlled trial of rituximab.

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Journal:  Pediatr Nephrol       Date:  2017-06-29       Impact factor: 3.714

3.  Predictors of relapse and long-term outcome in children with steroid-dependent nephrotic syndrome after rituximab treatment.

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Journal:  Clin Exp Nephrol       Date:  2016-08-24       Impact factor: 2.801

4.  Efficacy of Rituximab vs Tacrolimus in Pediatric Corticosteroid-Dependent Nephrotic Syndrome: A Randomized Clinical Trial.

Authors:  Biswanath Basu; Anja Sander; Birendranath Roy; Stella Preussler; Shilpita Barua; T K S Mahapatra; Franz Schaefer
Journal:  JAMA Pediatr       Date:  2018-08-01       Impact factor: 16.193

5.  Long-Term Efficacy and Safety of Repeated Rituximab to Maintain Remission in Idiopathic Childhood Nephrotic Syndrome: An International Study.

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Journal:  J Am Soc Nephrol       Date:  2022-03-30       Impact factor: 14.978

6.  Relapse of nephrotic syndrome during post-rituximab peripheral blood B-lymphocyte depletion.

Authors:  Mai Sato; Koichi Kamei; Masao Ogura; Kenji Ishikura; Shuichi Ito
Journal:  Clin Exp Nephrol       Date:  2017-04-22       Impact factor: 2.801

7.  Ofatumumab in two pediatric nephrotic syndrome patients allergic to rituximab.

Authors:  Marina Vivarelli; Manuela Colucci; Alice Bonanni; Martina Verzani; Jessica Serafinelli; Francesco Emma; Gianmarco Ghiggeri
Journal:  Pediatr Nephrol       Date:  2016-09-29       Impact factor: 3.714

Review 8.  Rituximab in children with steroid sensitive nephrotic syndrome: in quest of the optimal regimen.

Authors:  Eugene Yu-Hin Chan; Kjell Tullus
Journal:  Pediatr Nephrol       Date:  2020-06-24       Impact factor: 3.714

Review 9.  Update on the treatment of steroid-sensitive nephrotic syndrome.

Authors:  Federica Zotta; Marina Vivarelli; Francesco Emma
Journal:  Pediatr Nephrol       Date:  2021-03-05       Impact factor: 3.714

10.  Long-term repeated rituximab treatment for childhood steroid-dependent nephrotic syndrome.

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