Literature DB >> 26190315

Carnitine deficiency induces a short QT syndrome.

Julien Roussel1, François Labarthe2, Jerome Thireau1, Fabio Ferro3, Charlotte Farah1, Jerome Roy1, Masahisa Horiuchi4, Martine Tardieu2, Bruno Lefort2, Jean François Benoist5, Alain Lacampagne1, Sylvain Richard1, Jeremy Fauconnier1, Dominique Babuty6, Jean Yves Le Guennec1.   

Abstract

BACKGROUND: Short QT syndrome is associated with an increased risk of cardiac arrhythmias and unexpected sudden death. Until now, only mutations in genes encoding the cardiac potassium and calcium channels have been implicated in early T-wave repolarization.
OBJECTIVE: The purpose of this study was to confirm a relationship between a short QT syndrome and carnitine deficiency.
METHODS: We report 3 patients affected by primary systemic carnitine deficiency and an associated short QT syndrome. Ventricular fibrillation during early adulthood was the initial symptom in 1 case. To confirm the relationship between carnitine, short QT syndrome, and arrhythmias, we used a mouse model of carnitine deficiency induced by long-term subcutaneous perfusion of MET88.
RESULTS: MET88-treated mice developed cardiac hypertrophy associated with a remodeling of the mitochondrial network. The continuous monitoring of electrocardiograms confirmed a shortening of the QT interval, which was negatively correlated with the plasma carnitine concentration. As in humans, such alterations coincided with the genesis of ventricular premature beats and ventricular tachycardia and fibrillation.
CONCLUSION: Altogether, these results suggest that long-chain fatty acid metabolism influence the morphology and the electrical function of the heart.
Copyright © 2016 Heart Rhythm Society. Published by Elsevier Inc. All rights reserved.

Entities:  

Keywords:  Carnitine deficiency; Electrophysiological remodeling; Short QT syndrome; Sudden death; Ventricular arrhythmias

Mesh:

Substances:

Year:  2015        PMID: 26190315     DOI: 10.1016/j.hrthm.2015.07.027

Source DB:  PubMed          Journal:  Heart Rhythm        ISSN: 1547-5271            Impact factor:   6.343


  18 in total

1.  Exome sequencing identifies primary carnitine deficiency in a family with cardiomyopathy and sudden death.

Authors:  Najim Lahrouchi; Elisabeth M Lodder; Maria Mansouri; Rafik Tadros; Layla Zniber; Najlae Adadi; Sally-Ann B Clur; Karin Y van Spaendonck-Zwarts; Alex V Postma; Abdelaziz Sefiani; Ilham Ratbi; Connie R Bezzina
Journal:  Eur J Hum Genet       Date:  2017-03-15       Impact factor: 4.246

Review 2.  Short QT syndrome in pediatrics.

Authors:  Roberta Pereira; Oscar Campuzano; Georgia Sarquella-Brugada; Sergi Cesar; Anna Iglesias; Josep Brugada; Fernando E S Cruz Filho; Ramon Brugada
Journal:  Clin Res Cardiol       Date:  2017-03-16       Impact factor: 5.460

3.  European Heart Rhythm Association (EHRA)/Heart Rhythm Society (HRS)/Asia Pacific Heart Rhythm Society (APHRS)/Latin American Heart Rhythm Society (LAHRS) Expert Consensus Statement on the state of genetic testing for cardiac diseases.

Authors:  Arthur A M Wilde; Christopher Semsarian; Manlio F Márquez; Alireza Sepehri Shamloo; Michael J Ackerman; Euan A Ashley; Back Sternick Eduardo; Héctor Barajas-Martinez; Elijah R Behr; Connie R Bezzina; Jeroen Breckpot; Philippe Charron; Priya Chockalingam; Lia Crotti; Michael H Gollob; Steven Lubitz; Naomasa Makita; Seiko Ohno; Martín Ortiz-Genga; Luciana Sacilotto; Eric Schulze-Bahr; Wataru Shimizu; Nona Sotoodehnia; Rafik Tadros; James S Ware; David S Winlaw; Elizabeth S Kaufman; Takeshi Aiba; Andreas Bollmann; Jong-Il Choi; Aarti Dalal; Francisco Darrieux; John Giudicessi; Mariana Guerchicoff; Kui Hong; Andrew D Krahn; Ciorsti Mac Intyre; Judith A Mackall; Lluís Mont; Carlo Napolitano; Pablo Ochoa Juan; Petr Peichl; Alexandre C Pereira; Peter J Schwartz; Jon Skinner; Christoph Stellbrink; Jacob Tfelt-Hansen; Thomas Deneke
Journal:  J Arrhythm       Date:  2022-05-31

4.  European Heart Rhythm Association (EHRA)/Heart Rhythm Society (HRS)/Asia Pacific Heart Rhythm Society (APHRS)/Latin American Heart Rhythm Society (LAHRS) Expert Consensus Statement on the state of genetic testing for cardiac diseases.

Authors:  Arthur A M Wilde; Christopher Semsarian; Manlio F Márquez; Alireza Sepehri Shamloo; Michael J Ackerman; Euan A Ashley; Eduardo Back Sternick; Héctor Barajas-Martinez; Elijah R Behr; Connie R Bezzina; Jeroen Breckpot; Philippe Charron; Priya Chockalingam; Lia Crotti; Michael H Gollob; Steven Lubitz; Naomasa Makita; Seiko Ohno; Martín Ortiz-Genga; Luciana Sacilotto; Eric Schulze-Bahr; Wataru Shimizu; Nona Sotoodehnia; Rafik Tadros; James S Ware; David S Winlaw; Elizabeth S Kaufman; Takeshi Aiba; Andreas Bollmann; Jong Il Choi; Aarti Dalal; Francisco Darrieux; John Giudicessi; Mariana Guerchicoff; Kui Hong; Andrew D Krahn; Ciorsti MacIntyre; Judith A Mackall; Lluís Mont; Carlo Napolitano; Juan Pablo Ochoa; Petr Peichl; Alexandre C Pereira; Peter J Schwartz; Jon Skinner; Christoph Stellbrink; Jacob Tfelt-Hansen; Thomas Deneke
Journal:  Europace       Date:  2022-09-01       Impact factor: 5.486

Review 5.  Cardiac disease and arrhythmogenesis: Mechanistic insights from mouse models.

Authors:  Lois Choy; Jie Ming Yeo; Vivian Tse; Shing Po Chan; Gary Tse
Journal:  Int J Cardiol Heart Vasc       Date:  2016-09

Review 6.  Electrophysiological mechanisms of long and short QT syndromes.

Authors:  Gary Tse; Yin Wah Fiona Chan; Wendy Keung; Bryan P Yan
Journal:  Int J Cardiol Heart Vasc       Date:  2016-11-26

7.  Modeling Short QT Syndrome Using Human-Induced Pluripotent Stem Cell-Derived Cardiomyocytes.

Authors:  Ibrahim El-Battrawy; Huan Lan; Lukas Cyganek; Zhihan Zhao; Xin Li; Fanis Buljubasic; Siegfried Lang; Gökhan Yücel; Katherine Sattler; Wolfram-Hubertus Zimmermann; Jochen Utikal; Thomas Wieland; Ursula Ravens; Martin Borggrefe; Xiao-Bo Zhou; Ibrahim Akin
Journal:  J Am Heart Assoc       Date:  2018-03-24       Impact factor: 5.501

Review 8.  Disorders of mitochondrial long-chain fatty acid oxidation and the carnitine shuttle.

Authors:  Suzan J G Knottnerus; Jeannette C Bleeker; Rob C I Wüst; Sacha Ferdinandusse; Lodewijk IJlst; Frits A Wijburg; Ronald J A Wanders; Gepke Visser; Riekelt H Houtkooper
Journal:  Rev Endocr Metab Disord       Date:  2018-03       Impact factor: 6.514

9.  Maternal Primary Carnitine Deficiency and a Novel Solute Carrier Family 22 Member 5 (SLC22A5) Mutation.

Authors:  Michael Jakoby; Amruta Jaju; Aundrea Marsh; Andrew Wilber
Journal:  J Investig Med High Impact Case Rep       Date:  2021 Jan-Dec

Review 10.  Therapeutic Approaches to Genetic Ion Channelopathies and Perspectives in Drug Discovery.

Authors:  Paola Imbrici; Antonella Liantonio; Giulia M Camerino; Michela De Bellis; Claudia Camerino; Antonietta Mele; Arcangela Giustino; Sabata Pierno; Annamaria De Luca; Domenico Tricarico; Jean-Francois Desaphy; Diana Conte
Journal:  Front Pharmacol       Date:  2016-05-10       Impact factor: 5.810

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