Literature DB >> 26122173

Effects of enzyme replacement therapy on immune function in ADA deficiency patient.

Yumiko Nakazawa1, Toshinao Kawai1, Toru Uchiyama1, Fumihiro Goto1, Nobuyuki Watanabe1, Takanobu Maekawa2, Akira Ishiguro2, Torayuki Okuyama3, Makoto Otsu4, Masafumi Yamada5, Michael S Hershfield6, Tadashi Ariga5, Masafumi Onodera7.   

Abstract

Entities:  

Keywords:  Adenosine deaminase deficiency; Enzyme replacement therapy; Immune reconstitution; PEG-ADA; Severe combined immunodeficiency; Stem cell gene therapy

Mesh:

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Year:  2015        PMID: 26122173     DOI: 10.1016/j.clim.2015.06.011

Source DB:  PubMed          Journal:  Clin Immunol        ISSN: 1521-6616            Impact factor:   3.969


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  4 in total

1.  Comparison of elapegademase and pegademase in ADA-deficient patients and mice.

Authors:  L Murguia-Favela; W Min; R Loves; M Leon-Ponte; E Grunebaum
Journal:  Clin Exp Immunol       Date:  2020-02-09       Impact factor: 4.330

2.  Long-Term Outcome of Adenosine Deaminase-Deficient Patients-a Single-Center Experience.

Authors:  Ori Scott; Vy Hong-Diep Kim; Brenda Reid; Anne Pham-Huy; Adelle R Atkinson; Alessandro Aiuti; Eyal Grunebaum
Journal:  J Clin Immunol       Date:  2017-07-26       Impact factor: 8.542

3.  Single Cell-Based Vector Tracing in Patients with ADA-SCID Treated with Stem Cell Gene Therapy.

Authors:  Yuka Igarashi; Toru Uchiyama; Tomoko Minegishi; Sirirat Takahashi; Nobuyuki Watanabe; Toshinao Kawai; Masafumi Yamada; Tadashi Ariga; Masafumi Onodera
Journal:  Mol Ther Methods Clin Dev       Date:  2017-05-25       Impact factor: 6.698

Review 4.  Adenosine Deaminase Deficiency - More Than Just an Immunodeficiency.

Authors:  Kathryn V Whitmore; Hubert B Gaspar
Journal:  Front Immunol       Date:  2016-08-16       Impact factor: 7.561

  4 in total

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