Literature DB >> 25992365

Mitochondrial dysfunction in Kennedy's disease: a new pharmacological target?

Chong Wang1, Wei Chen1, Dan Miao1, Jin-Tai Yu1, Lan Tan1.   

Abstract

BACKGROUND: Mitochondrial impairment and elevated oxidative stress have been implicated in the pathogenesis of Kennedy's disease. However, there is still no study describing the mitochondrial nutrient management in patients with Kennedy's disease.
METHODS: We assessed the clinical and electrophysiological features in a patient with Kennedy's disease. This patient was diagnosed by genetic analysis. We also measured the plasma 8-hydroxydeoxyguanosine (8-OHdG) levels of the patient and his family members using commercial enzyme-linked immunosorbent assay (ELISA). Treatment with intravenous L-carnitine (2 g/day) for the patient was started on admission, followed by two weeks.
RESULTS: Routine laboratory tests revealed a severe elevation of creatine kinase (CK) (606.5 U/L; normal value: 15-170 U/L). Sequencing of the first exon of androgen receptor (AR) revealed an increased number of CAG repeat (50; the normal range from 10-36) in the patient. Plasma 8-OHdG level in the patient was relatively elevated (34.68±1.01 ng/mL) compared with the female carriers and non-carriers. Two weeks after L-carnitine treatment, we observed a reduction of approximately 40% in CK level (391 U/L) in the patient.
CONCLUSIONS: Oxidative stress resulting from mitochondrial dysfunction could be involved in Kennedy's disease. Targeting the mitochondrial dysfunction in Kennedy's disease may have significant therapeutic potential.

Entities:  

Keywords:  Kennedy’s disease; mitochondrial dysfunction; oxidative stress; spinal and bulbar muscle atrophy

Year:  2015        PMID: 25992365      PMCID: PMC4402598          DOI: 10.3978/j.issn.2305-5839.2015.01.12

Source DB:  PubMed          Journal:  Ann Transl Med        ISSN: 2305-5839


  10 in total

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  10 in total
  1 in total

1.  Erratum to Mitochondrial dysfunction in Kennedy's disease: a new pharmacological target?

Authors: 
Journal:  Ann Transl Med       Date:  2016-05
  1 in total

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